JPWO2022017363A5 - - Google Patents

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Publication number
JPWO2022017363A5
JPWO2022017363A5 JP2023512465A JP2023512465A JPWO2022017363A5 JP WO2022017363 A5 JPWO2022017363 A5 JP WO2022017363A5 JP 2023512465 A JP2023512465 A JP 2023512465A JP 2023512465 A JP2023512465 A JP 2023512465A JP WO2022017363 A5 JPWO2022017363 A5 JP WO2022017363A5
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JP
Japan
Prior art keywords
seq
sequence
rpe65
promoter
coding sequence
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023512465A
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English (en)
Japanese (ja)
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JP2023535232A (ja
Publication date
Priority claimed from CN202010704946.1A external-priority patent/CN113952471A/zh
Application filed filed Critical
Priority claimed from PCT/CN2021/107284 external-priority patent/WO2022017363A1/en
Publication of JP2023535232A publication Critical patent/JP2023535232A/ja
Publication of JPWO2022017363A5 publication Critical patent/JPWO2022017363A5/ja
Withdrawn legal-status Critical Current

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JP2023512465A 2020-07-21 2021-07-20 眼疾患の処置のための組成物および方法 Withdrawn JP2023535232A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
CN202010704946.1 2020-07-21
CN202010704946.1A CN113952471A (zh) 2020-07-21 2020-07-21 用于治疗眼部疾病的组合物和方法
CN202110378979.6 2021-04-08
CN202110378979 2021-04-08
PCT/CN2021/107284 WO2022017363A1 (en) 2020-07-21 2021-07-20 Compositions and methods for the treatment of ocular diseases

Publications (2)

Publication Number Publication Date
JP2023535232A JP2023535232A (ja) 2023-08-16
JPWO2022017363A5 true JPWO2022017363A5 (de) 2024-07-26

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ID=79728991

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023512465A Withdrawn JP2023535232A (ja) 2020-07-21 2021-07-20 眼疾患の処置のための組成物および方法

Country Status (7)

Country Link
US (1) US20230321280A1 (de)
EP (1) EP4185335A1 (de)
JP (1) JP2023535232A (de)
CN (1) CN116368228A (de)
AU (1) AU2021314400A1 (de)
CA (1) CA3186818A1 (de)
WO (1) WO2022017363A1 (de)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2023187822A1 (en) * 2022-03-28 2023-10-05 Indian Institute Of Technology Kanpur A system for an ocular gene therapy and a process for preparing thereof
WO2024077089A2 (en) * 2022-10-04 2024-04-11 Siren Biotechnology, Inc. Modified cpg dinucleotides for recombinant viral vector production

Family Cites Families (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
GB201502137D0 (en) * 2015-02-09 2015-03-25 Ucl Business Plc Treatment
WO2016193434A1 (en) * 2015-06-04 2016-12-08 INSERM (Institut National de la Santé et de la Recherche Médicale) Improved methods for treating ocular diseases by gene therapy
JP7448953B2 (ja) * 2017-07-31 2024-03-13 リフレクション バイオテクノロジーズ リミテッド 眼疾患のための細胞モデル及び治療関連出願への相互参照
CN111118017B (zh) * 2018-11-01 2023-10-03 上海朗昇生物科技有限公司 治疗Leber先天性黑蒙症的载体及其应用

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