JPWO2021222831A5 - - Google Patents

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Publication number
JPWO2021222831A5
JPWO2021222831A5 JP2022566315A JP2022566315A JPWO2021222831A5 JP WO2021222831 A5 JPWO2021222831 A5 JP WO2021222831A5 JP 2022566315 A JP2022566315 A JP 2022566315A JP 2022566315 A JP2022566315 A JP 2022566315A JP WO2021222831 A5 JPWO2021222831 A5 JP WO2021222831A5
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JP
Japan
Prior art keywords
seq
mutation
polypeptide
viral
vector system
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2022566315A
Other languages
English (en)
Japanese (ja)
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JP2023524061A5 (https=
JP2023524061A (ja
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/030298 external-priority patent/WO2021222831A2/en
Publication of JP2023524061A publication Critical patent/JP2023524061A/ja
Publication of JP2023524061A5 publication Critical patent/JP2023524061A5/ja
Publication of JPWO2021222831A5 publication Critical patent/JPWO2021222831A5/ja
Withdrawn legal-status Critical Current

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JP2022566315A 2020-05-01 2021-04-30 操作された中枢神経系用組成物 Withdrawn JP2023524061A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202063019221P 2020-05-01 2020-05-01
US63/019,221 2020-05-01
US202063061517P 2020-08-05 2020-08-05
US63/061,517 2020-08-05
PCT/US2021/030298 WO2021222831A2 (en) 2020-05-01 2021-04-30 Engineered central nervous system compositions

Publications (3)

Publication Number Publication Date
JP2023524061A JP2023524061A (ja) 2023-06-08
JP2023524061A5 JP2023524061A5 (https=) 2024-05-13
JPWO2021222831A5 true JPWO2021222831A5 (https=) 2024-05-13

Family

ID=78373993

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2022566315A Withdrawn JP2023524061A (ja) 2020-05-01 2021-04-30 操作された中枢神経系用組成物

Country Status (7)

Country Link
US (1) US20230193316A1 (https=)
EP (1) EP4143305A4 (https=)
JP (1) JP2023524061A (https=)
CN (1) CN115867646A (https=)
AU (1) AU2021264061A1 (https=)
CA (1) CA3176506A1 (https=)
WO (1) WO2021222831A2 (https=)

Families Citing this family (17)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP3861010A1 (en) 2018-10-02 2021-08-11 Voyager Therapeutics, Inc. Redirection of tropism of aav capsids
CN116096734A (zh) 2020-05-13 2023-05-09 沃雅戈治疗公司 Aav衣壳的向性的重定向
WO2022173847A2 (en) * 2021-02-09 2022-08-18 Affinia Therapeutics Inc. Recombinant aavs with improved tropism and specificity
CA3216419A1 (en) * 2021-04-23 2022-10-27 Greg NACHTRAB Tissue-targeted modified aav capsids and methods of use thereof
WO2022226375A1 (en) * 2021-04-23 2022-10-27 Locanabio, Inc. Tissue-targeted modified aav capsids and methods of use thereof
MX2024004217A (es) 2021-10-08 2024-06-26 Dyno Therapeutics Inc Variantes de cápside y métodos de uso de estas.
MX2024004936A (es) 2021-11-02 2024-05-08 Voyager Therapeutics Inc Variantes de capsides de aav y sus usos.
US20260085284A1 (en) * 2022-08-30 2026-03-26 Shanghai Genemagic Biosciences Co., Ltd. Method for trans-differentiating non-neuronal cells into neurons and use thereof
WO2024086747A1 (en) 2022-10-19 2024-04-25 Affinia Therapeutics Inc. Recombinant aavs with improved tropism and specificity
TW202502803A (zh) 2023-03-10 2025-01-16 美商戴諾治療公司 衣殼多肽及其使用方法
WO2024238807A2 (en) 2023-05-16 2024-11-21 Affinia Therapeutics Inc. Recombinant aavs with improved tropism and specificity
AR133098A1 (es) * 2023-06-29 2025-08-27 Univ Pennsylvania Aav mutante con motivos dirigidos al sistema nervioso central y composiciones que lo contienen
TW202525832A (zh) 2023-08-31 2025-07-01 美商戴諾治療公司 衣殼多肽及其使用方法(二)
CN117165677A (zh) * 2023-11-03 2023-12-05 首都儿科研究所 检测生物标志物在制备神经管畸形疾病的产品的应用
WO2025160155A1 (en) 2024-01-22 2025-07-31 The Broad Institute, Inc. Epigenetic targeting of prion diseases
TW202545971A (zh) 2024-02-08 2025-12-01 美商戴諾治療公司 殼體多肽及其使用方法
WO2026064442A2 (en) 2024-09-18 2026-03-26 Dyno Therapeutics, Inc. Capsid polypeptides and methods of use thereof

Family Cites Families (9)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2014139182A1 (en) * 2013-03-15 2014-09-18 Shenzhen Hightide Biopharmaceutical, Ltd. Compositions and methods of using islet neogenesis peptides and analogs thereof
WO2016081811A1 (en) * 2014-11-21 2016-05-26 The University Of North Carolina At Chapel Hill Aav vectors targeted to the central nervous system
CA2988388C (en) * 2015-04-23 2022-11-22 Nantomics, Llc Cancer neoepitopes
KR102423442B1 (ko) * 2015-12-11 2022-07-20 캘리포니아 인스티튜트 오브 테크놀로지 아데노-관련 바이러스를 지시하기 위한 타겟팅 펩타이드
NZ763617A (en) * 2017-10-16 2026-01-30 Vigeneron Gmbh Aav vectors
IL278598B2 (en) * 2018-05-11 2025-11-01 Massachusetts Eye & Ear Infirmary Altering tissue tropism of adeno-associated viruses
US20210277418A1 (en) * 2018-08-03 2021-09-09 Voyager Therapeutics, Inc. Aav variants with enhanced tropism
EP3861010A1 (en) * 2018-10-02 2021-08-11 Voyager Therapeutics, Inc. Redirection of tropism of aav capsids
WO2023039480A2 (en) * 2021-09-08 2023-03-16 The Broad Institute, Inc. Engineered central nervous system compositions

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