JPWO2021041885A5 - - Google Patents

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Publication number
JPWO2021041885A5
JPWO2021041885A5 JP2022513443A JP2022513443A JPWO2021041885A5 JP WO2021041885 A5 JPWO2021041885 A5 JP WO2021041885A5 JP 2022513443 A JP2022513443 A JP 2022513443A JP 2022513443 A JP2022513443 A JP 2022513443A JP WO2021041885 A5 JPWO2021041885 A5 JP WO2021041885A5
Authority
JP
Japan
Prior art keywords
tada
spcas9
deaminase
sequence
variant
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2022513443A
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English (en)
Japanese (ja)
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JP2022545950A (ja
Publication date
Application filed filed Critical
Priority claimed from PCT/US2020/048510 external-priority patent/WO2021041885A2/en
Publication of JP2022545950A publication Critical patent/JP2022545950A/ja
Publication of JPWO2021041885A5 publication Critical patent/JPWO2021041885A5/ja
Pending legal-status Critical Current

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JP2022513443A 2019-08-29 2020-08-28 転写または発現を可能にするように変異を編集するための組成物および方法 Pending JP2022545950A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201962893638P 2019-08-29 2019-08-29
US62/893,638 2019-08-29
PCT/US2020/048510 WO2021041885A2 (en) 2019-08-29 2020-08-28 Compositions and methods for editing a mutation to permit transcription or expression

Publications (2)

Publication Number Publication Date
JP2022545950A JP2022545950A (ja) 2022-11-01
JPWO2021041885A5 true JPWO2021041885A5 (de) 2023-09-05

Family

ID=74684607

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2022513443A Pending JP2022545950A (ja) 2019-08-29 2020-08-28 転写または発現を可能にするように変異を編集するための組成物および方法

Country Status (8)

Country Link
US (1) US20220313799A1 (de)
EP (1) EP4022050A2 (de)
JP (1) JP2022545950A (de)
KR (1) KR20220066289A (de)
CN (1) CN114641567A (de)
AU (1) AU2020336953A1 (de)
CA (1) CA3152861A1 (de)
WO (1) WO2021041885A2 (de)

Families Citing this family (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2021222318A1 (en) 2020-04-28 2021-11-04 The Broad Institute, Inc. Targeted base editing of the ush2a gene
CN115348870B (zh) * 2021-03-16 2023-06-13 上海驯鹿生物技术有限公司 通用型嵌合抗原受体t细胞及其应用
WO2023102550A2 (en) 2021-12-03 2023-06-08 The Broad Institute, Inc. Compositions and methods for efficient in vivo delivery
KR20230166378A (ko) 2022-05-30 2023-12-07 현대자동차주식회사 차량의 제동 방법 및 장치

Family Cites Families (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CA2502636C (en) * 2002-08-30 2013-11-19 The Hospital For Sick Children Diagnosis of shwachman-diamond syndrome
US20110151447A1 (en) * 2007-11-06 2011-06-23 Children's Medical Center Corporation Method to produce induced pluripotent stem (ips) cells from non-embryonic human cells
IL258821B (en) * 2015-10-23 2022-07-01 Harvard College Nucleobase editors and their uses
KR20200006054A (ko) * 2017-04-12 2020-01-17 더 브로드 인스티튜트, 인코퍼레이티드 신규 타입 vi crispr 오르소로그 및 시스템
CN109306361B (zh) * 2018-02-11 2022-06-28 华东师范大学 一种新的a/t到g/c碱基定点转换的基因编辑系统

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