JP7636338B2 - コルチコステロイドを含む、ｔｔｒ遺伝子編集およびａｔｔｒアミロイドーシスを治療するための組成物および方法、またはその使用 - Google Patents

コルチコステロイドを含む、ｔｔｒ遺伝子編集およびａｔｔｒアミロイドーシスを治療するための組成物および方法、またはその使用 Download PDF

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JP7636338B2
JP7636338B2 JP2021557650A JP2021557650A JP7636338B2 JP 7636338 B2 JP7636338 B2 JP 7636338B2 JP 2021557650 A JP2021557650 A JP 2021557650A JP 2021557650 A JP2021557650 A JP 2021557650A JP 7636338 B2 JP7636338 B2 JP 7636338B2
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administered
sequence
corticosteroid
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JP2022525429A5 (https=
JP2022525429A (ja
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チャン，ヨン
シー． アレクサンダー，セス
エム． ウッド，クリスティ
マヘンドラ プラカーシュ カンジョリア，アルティ
オダテ，ショブ
リン サイツァー，ジェシカ
マイケル レスカルボー，レイナード
ストラップス，ワルター
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インテリア セラピューティクス，インコーポレイテッド
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JP2021557650A 2019-03-28 2020-03-27 コルチコステロイドを含む、ｔｔｒ遺伝子編集およびａｔｔｒアミロイドーシスを治療するための組成物および方法、またはその使用 Active JP7636338B2 (ja)

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JP2025021006A JP2025081416A (ja) 2019-03-28 2025-02-12 コルチコステロイドを含む、ｔｔｒ遺伝子編集およびａｔｔｒアミロイドーシスを治療するための組成物および方法、またはその使用

Applications Claiming Priority (5)

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US201962825676P 2019-03-28 2019-03-28
US201962825637P 2019-03-28 2019-03-28
US62/825,676 2019-03-28
US62/825,637 2019-03-28
PCT/US2020/025533 WO2020198706A1 (en) 2019-03-28 2020-03-27 Compositions and methods for ttr gene editing and treating attr amyloidosis comprising a corticosteroid or use thereof

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JP2022525429A JP2022525429A (ja) 2022-05-13
JP2022525429A5 JP2022525429A5 (https=) 2023-12-15
JP7636338B2 true JP7636338B2 (ja) 2025-02-26

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