CN113874004A - 用于ttr基因编辑和治疗attr淀粉样变性的包括皮质类固醇的组合物和方法或其用途 - Google Patents

用于ttr基因编辑和治疗attr淀粉样变性的包括皮质类固醇的组合物和方法或其用途 Download PDF

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CN113874004A
CN113874004A CN202080039394.5A CN202080039394A CN113874004A CN 113874004 A CN113874004 A CN 113874004A CN 202080039394 A CN202080039394 A CN 202080039394A CN 113874004 A CN113874004 A CN 113874004A
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composition
seq
subject
sequence
corticosteroid
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Y·常
S·C·亚历山大
K·M·伍德
A·M·P·坎乔利亚
S·奥达特
J·L·塞泽
R·M·莱斯卡博
W·斯特雷普斯
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Intellia Therapeutics Inc
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Intellia Therapeutics Inc
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CN202080039394.5A 2019-03-28 2020-03-27 用于ttr基因编辑和治疗attr淀粉样变性的包括皮质类固醇的组合物和方法或其用途 Pending CN113874004A (zh)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201962825676P 2019-03-28 2019-03-28
US201962825637P 2019-03-28 2019-03-28
US62/825,676 2019-03-28
US62/825,637 2019-03-28
PCT/US2020/025533 WO2020198706A1 (en) 2019-03-28 2020-03-27 Compositions and methods for ttr gene editing and treating attr amyloidosis comprising a corticosteroid or use thereof

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CN113874004A true CN113874004A (zh) 2021-12-31

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CN202080039394.5A Pending CN113874004A (zh) 2019-03-28 2020-03-27 用于ttr基因编辑和治疗attr淀粉样变性的包括皮质类固醇的组合物和方法或其用途

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US (1) US20230035659A1 (https=)
EP (1) EP3946285A1 (https=)
JP (2) JP7636338B2 (https=)
KR (1) KR20220004984A (https=)
CN (1) CN113874004A (https=)
AU (1) AU2020248337A1 (https=)
CA (1) CA3134544A1 (https=)
CO (1) CO2021014562A2 (https=)
MX (1) MX2021011690A (https=)
WO (1) WO2020198706A1 (https=)

Cited By (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2025087413A1 (zh) * 2023-10-25 2025-05-01 上海津曼特生物科技有限公司 靶向ttr的基因编辑组合物

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* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
IL303195A (en) 2020-11-25 2023-07-01 Akagera Medicines Inc Lipid nanoparticles for delivery of nucleic acids and related methods of use
CR20230305A (es) * 2020-12-11 2023-11-10 Intellia Therapeutics Inc Polinucleótidos, composiciones y métodos para la edición del genoma que implican desaminación
BR112023021477A2 (pt) * 2021-04-17 2024-01-30 Intellia Therapeutics Inc Composições de nanopartículas lipídicas
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