JP7498665B2 - 新規アデノ随伴ウイルス（ａａｖ）ベクター、低減されたカプシド脱アミド化を有するａａｖベクター、およびその使用 - Google Patents

新規アデノ随伴ウイルス（ａａｖ）ベクター、低減されたカプシド脱アミド化を有するａａｖベクター、およびその使用 Download PDF

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JP7498665B2
JP7498665B2 JP2020545159A JP2020545159A JP7498665B2 JP 7498665 B2 JP7498665 B2 JP 7498665B2 JP 2020545159 A JP2020545159 A JP 2020545159A JP 2020545159 A JP2020545159 A JP 2020545159A JP 7498665 B2 JP7498665 B2 JP 7498665B2
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ウイルソン，ジェームス・エム
テペ，エイプリル
ターナー，ケビン
シムス，ジョシュア・ジョイナー
ワン，チャン
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ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア
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    • C12N2750/14011—Parvoviridae
    • C12N2750/14111—Dependovirus, e.g. adenoassociated viruses
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    • C12N2750/00011—Details
    • C12N2750/14011—Parvoviridae
    • C12N2750/14111—Dependovirus, e.g. adenoassociated viruses
    • C12N2750/14141—Use of virus, viral particle or viral elements as a vector
    • C12N2750/14143—Use of virus, viral particle or viral elements as a vector viral genome or elements thereof as genetic vector

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JP2020545159A 2018-02-27 2019-02-27 新規アデノ随伴ウイルス（ａａｖ）ベクター、低減されたカプシド脱アミド化を有するａａｖベクター、およびその使用 Active JP7498665B2 (ja)

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JP2024088641A JP7860169B2 (ja) 2018-02-27 2024-05-31 新規アデノ随伴ウイルス（ａａｖ）ベクター、低減されたカプシド脱アミド化を有するａａｖベクター、およびその使用

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US201862635968P 2018-02-27 2018-02-27
US201862635964P 2018-02-27 2018-02-27
US62/635,964 2018-02-27
US62/635,968 2018-02-27
US201862663797P 2018-04-27 2018-04-27
US201862663788P 2018-04-27 2018-04-27
US62/663,788 2018-04-27
US62/663,797 2018-04-27
US201862667587P 2018-05-06 2018-05-06
US62/667,587 2018-05-06
US201862667881P 2018-05-07 2018-05-07
US201862667888P 2018-05-07 2018-05-07
US62/667,881 2018-05-07
US62/667,888 2018-05-07
US201862677474P 2018-05-29 2018-05-29
US201862667585P 2018-05-29 2018-05-29
US201862677471P 2018-05-29 2018-05-29
US62/677,471 2018-05-29
US62/667,585 2018-05-29
US62/677,474 2018-05-29
US201862703670P 2018-07-26 2018-07-26
US201862703673P 2018-07-26 2018-07-26
US62/703,670 2018-07-26
US62/703,673 2018-07-26
US201862722382P 2018-08-24 2018-08-24
US201862722388P 2018-08-24 2018-08-24
US62/722,388 2018-08-24
US62/722,382 2018-08-24
PCT/US2019/019861 WO2019169004A1 (en) 2018-02-27 2019-02-27 Novel adeno-associated virus (aav) vectors, aav vectors having reduced capsid deamidation and uses therefor

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JP2024088641A Active JP7860169B2 (ja) 2018-02-27 2024-05-31 新規アデノ随伴ウイルス（ａａｖ）ベクター、低減されたカプシド脱アミド化を有するａａｖベクター、およびその使用

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CN114787180A (zh) 2019-10-17 2022-07-22 斯特里迪比奥公司 用于治疗c型尼曼-匹克病的腺相关病毒载体
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JP7860169B2 (ja) 2018-02-27 2026-05-15 ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア 新規アデノ随伴ウイルス（ａａｖ）ベクター、低減されたカプシド脱アミド化を有するａａｖベクター、およびその使用

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US20210123073A1 (en) 2021-04-29
KR20210006327A (ko) 2021-01-18
MX2020008932A (es) 2020-10-01
CN112236443B (zh) 2025-02-07
US20260049334A1 (en) 2026-02-19
CN120519403A (zh) 2025-08-22
CA3091795A1 (en) 2019-09-06
AU2019228504B2 (en) 2025-06-26
US12416016B2 (en) 2025-09-16
CN112236443A (zh) 2021-01-15
BR112020017278A2 (pt) 2020-12-22
KR102848518B1 (ko) 2025-08-22
MA52087A (fr) 2021-06-02
WO2019169004A1 (en) 2019-09-06
AU2019228504A1 (en) 2020-09-10
JP7860169B2 (ja) 2026-05-15
SG11202007942YA (en) 2020-09-29
JP2021515548A (ja) 2021-06-24
JP2024115558A (ja) 2024-08-26
CL2020002201A1 (es) 2020-12-18
IL276860A (en) 2020-10-29
EP3768695A1 (en) 2021-01-27
EP3768695A4 (en) 2022-04-06
WO2019169004A8 (en) 2019-12-05

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