JP7253379B2 - 組織特異的発現のための改変ｕ６プロモーターシステム - Google Patents

組織特異的発現のための改変ｕ６プロモーターシステム Download PDF

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JP7253379B2
JP7253379B2 JP2018551837A JP2018551837A JP7253379B2 JP 7253379 B2 JP7253379 B2 JP 7253379B2 JP 2018551837 A JP2018551837 A JP 2018551837A JP 2018551837 A JP2018551837 A JP 2018551837A JP 7253379 B2 JP7253379 B2 JP 7253379B2
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mirna
nucleic acid
aav
sequence
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スコット クエントン ハーパー，
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リサーチ インスティチュート アット ネイションワイド チルドレンズ ホスピタル
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JP2018551837A 2016-04-02 2017-03-31 組織特異的発現のための改変ｕ６プロモーターシステム Active JP7253379B2 (ja)

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Ｇｅｎｅ Ｔｈｅｒａｐｙ，２０１１年，Ｖｏｌ．１８，ｐ．１９９－２０９
Ｍｏｌｅｃｕｌａｒ Ｔｈｅｒａｐｙ，２０１２年，Ｖｏｌ．２０，Ｎｏ．９，ｐ．１７３７－１７４９
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AU2017240236B2 (en) 2023-07-27
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AU2017240236A1 (en) 2018-10-18
JP2019515663A (ja) 2019-06-13
EP4335502A3 (en) 2024-07-03
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IL262056B2 (en) 2023-10-01
EP3435755B1 (en) 2023-11-01
CA3019832A1 (en) 2017-10-05
MA44528A (fr) 2019-02-06
BR112018070249A2 (pt) 2019-01-29
US20250019697A1 (en) 2025-01-16
RU2018137677A3 (enExample) 2020-07-23
AU2017240236C1 (en) 2024-03-07
CA3019832C (en) 2023-05-09
WO2017173411A1 (en) 2017-10-05
CN109714954A (zh) 2019-05-03
EP3435755A1 (en) 2019-02-06
IL262056B1 (en) 2023-06-01
KR20180130550A (ko) 2018-12-07
RU2018137677A (ru) 2020-05-12
RU2768289C2 (ru) 2022-03-23
EP4335502A2 (en) 2024-03-13
JP2022046792A (ja) 2022-03-23
IL262056A (en) 2018-11-29
US11345913B2 (en) 2022-05-31
US11939579B2 (en) 2024-03-26

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