JP2025501646A5 - - Google Patents

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Publication number
JP2025501646A5
JP2025501646A5 JP2024539849A JP2024539849A JP2025501646A5 JP 2025501646 A5 JP2025501646 A5 JP 2025501646A5 JP 2024539849 A JP2024539849 A JP 2024539849A JP 2024539849 A JP2024539849 A JP 2024539849A JP 2025501646 A5 JP2025501646 A5 JP 2025501646A5
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JP
Japan
Prior art keywords
composition
use according
subject
improved
administered
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024539849A
Other languages
English (en)
Japanese (ja)
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JP2025501646A (ja
Filing date
Publication date
Priority claimed from EP22150783.3A external-priority patent/EP4209215A1/en
Application filed filed Critical
Priority claimed from PCT/EP2023/050459 external-priority patent/WO2023131720A1/en
Publication of JP2025501646A publication Critical patent/JP2025501646A/ja
Publication of JP2025501646A5 publication Critical patent/JP2025501646A5/ja
Pending legal-status Critical Current

Links

JP2024539849A 2022-01-10 2023-01-10 Gm2ガングリオシドーシスの処置 Pending JP2025501646A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
EP22150783.3 2022-01-10
EP22150783.3A EP4209215A1 (en) 2022-01-10 2022-01-10 Treatment of gm2 gangliosidosis
EP22193136 2022-08-31
EP22193136.3 2022-08-31
PCT/EP2023/050459 WO2023131720A1 (en) 2022-01-10 2023-01-10 Treatment of gm2 gangliosidosis

Publications (2)

Publication Number Publication Date
JP2025501646A JP2025501646A (ja) 2025-01-22
JP2025501646A5 true JP2025501646A5 (https=) 2026-01-20

Family

ID=84982296

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024539849A Pending JP2025501646A (ja) 2022-01-10 2023-01-10 Gm2ガングリオシドーシスの処置

Country Status (9)

Country Link
US (1) US20250120958A1 (https=)
EP (2) EP4714497A2 (https=)
JP (1) JP2025501646A (https=)
AU (1) AU2023205441A1 (https=)
CA (1) CA3242701A1 (https=)
IL (1) IL314212A (https=)
MX (1) MX2024008583A (https=)
TW (1) TW202337456A (https=)
WO (1) WO2023131720A1 (https=)

Families Citing this family (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
TW202539666A (zh) * 2024-02-01 2025-10-16 荷蘭商雅捷法羅斯公司 Gm1神經節苷脂儲積症之治療
EP4595964A1 (en) * 2024-02-01 2025-08-06 Azafaros B.V. Treatment of gm1 gangliosidosis
WO2026013261A1 (en) 2024-07-11 2026-01-15 Azafaros B.V. Nizubaglustat for use in the treatment of lysosomal storage disorders
EP4678174A1 (en) 2024-07-11 2026-01-14 Azafaros B.V. Nizubaglustat for use in the treatment of lysosomal storage disorders

Family Cites Families (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP3461812B1 (en) 2014-03-27 2021-10-13 Academisch Medisch Centrum N-(5-(biphen-4-ylmethyloxy)pentyl)-substituted iminosugars as inhibitors of glucosylceramide synthase
EP3978474A1 (en) * 2020-10-02 2022-04-06 Azafaros B.V. Crystalline forms of a pharmaceutical compound

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