JP2024532464A5 - - Google Patents

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Publication number
JP2024532464A5
JP2024532464A5 JP2024513758A JP2024513758A JP2024532464A5 JP 2024532464 A5 JP2024532464 A5 JP 2024532464A5 JP 2024513758 A JP2024513758 A JP 2024513758A JP 2024513758 A JP2024513758 A JP 2024513758A JP 2024532464 A5 JP2024532464 A5 JP 2024532464A5
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JP
Japan
Application number
JP2024513758A
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Japanese (ja)
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JP2024532464A (ja
JPWO2023034817A5 (https=
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Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/075691 external-priority patent/WO2023034817A1/en
Publication of JP2024532464A publication Critical patent/JP2024532464A/ja
Publication of JP2024532464A5 publication Critical patent/JP2024532464A5/ja
Publication of JPWO2023034817A5 publication Critical patent/JPWO2023034817A5/ja
Pending legal-status Critical Current

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JP2024513758A 2021-09-01 2022-08-30 デュシェンヌ型筋ジストロフィーにおいてエクソン44をスキッピングするための化合物及び方法 Pending JP2024532464A (ja)

Applications Claiming Priority (23)

Application Number Priority Date Filing Date Title
US202163239645P 2021-09-01 2021-09-01
US202163239671P 2021-09-01 2021-09-01
US63/239,645 2021-09-01
US63/239,671 2021-09-01
US202163290960P 2021-12-17 2021-12-17
US63/290,960 2021-12-17
US202163292685P 2021-12-22 2021-12-22
US63/292,685 2021-12-22
US202263298565P 2022-01-11 2022-01-11
US63/298,565 2022-01-11
US202263268580P 2022-02-25 2022-02-25
US202263268577P 2022-02-25 2022-02-25
US63/268,577 2022-02-25
US63/268,580 2022-02-25
US202263362294P 2022-03-31 2022-03-31
US63/362,294 2022-03-31
US202263362423P 2022-04-04 2022-04-04
US63/362,423 2022-04-04
US202263337560P 2022-05-02 2022-05-02
US63/337,560 2022-05-02
US202263354456P 2022-06-22 2022-06-22
US63/354,456 2022-06-22
PCT/US2022/075691 WO2023034817A1 (en) 2021-09-01 2022-08-30 Compounds and methods for skipping exon 44 in duchenne muscular dystrophy

Publications (3)

Publication Number Publication Date
JP2024532464A JP2024532464A (ja) 2024-09-05
JP2024532464A5 true JP2024532464A5 (https=) 2025-09-08
JPWO2023034817A5 JPWO2023034817A5 (https=) 2025-09-08

Family

ID=83448049

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024513758A Pending JP2024532464A (ja) 2021-09-01 2022-08-30 デュシェンヌ型筋ジストロフィーにおいてエクソン44をスキッピングするための化合物及び方法

Country Status (9)

Country Link
US (1) US20260098262A9 (https=)
EP (1) EP4395829A1 (https=)
JP (1) JP2024532464A (https=)
KR (1) KR20240082344A (https=)
AU (1) AU2022339769A1 (https=)
CA (1) CA3229661A1 (https=)
IL (1) IL311139A (https=)
MX (1) MX2024002640A (https=)
WO (1) WO2023034817A1 (https=)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2025038901A1 (en) * 2023-08-17 2025-02-20 Entrada Therapeutics, Inc. Cyclic peptides for delivering therapeutics
WO2025072246A1 (en) * 2023-09-26 2025-04-03 Entrada Therapeutics, Inc. Compounds and methods for skipping exon 50 in duchenne muscular dystrophy

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