JP2024511955A5 - - Google Patents

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Publication number
JP2024511955A5
JP2024511955A5 JP2023555748A JP2023555748A JP2024511955A5 JP 2024511955 A5 JP2024511955 A5 JP 2024511955A5 JP 2023555748 A JP2023555748 A JP 2023555748A JP 2023555748 A JP2023555748 A JP 2023555748A JP 2024511955 A5 JP2024511955 A5 JP 2024511955A5
Authority
JP
Japan
Prior art keywords
seq
pharmaceutical composition
composition according
peptide
terminus
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023555748A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024511955A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/020061 external-priority patent/WO2022192749A2/en
Publication of JP2024511955A publication Critical patent/JP2024511955A/ja
Publication of JP2024511955A5 publication Critical patent/JP2024511955A5/ja
Pending legal-status Critical Current

Links

JP2023555748A 2021-03-12 2022-03-11 ペプチド-オリゴヌクレオチド複合体を用いるデュシェンヌ型筋ジストロフィーの治療法 Pending JP2024511955A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202163160705P 2021-03-12 2021-03-12
US63/160,705 2021-03-12
US202163194039P 2021-05-27 2021-05-27
US63/194,039 2021-05-27
PCT/US2022/020061 WO2022192749A2 (en) 2021-03-12 2022-03-11 Methods of treating duchenne muscular dystrophy using peptide-oligonucleotide conjugates

Publications (2)

Publication Number Publication Date
JP2024511955A JP2024511955A (ja) 2024-03-18
JP2024511955A5 true JP2024511955A5 (https=) 2025-04-03

Family

ID=83228540

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023555748A Pending JP2024511955A (ja) 2021-03-12 2022-03-11 ペプチド-オリゴヌクレオチド複合体を用いるデュシェンヌ型筋ジストロフィーの治療法

Country Status (4)

Country Link
US (1) US20240200062A1 (https=)
EP (1) EP4304628A4 (https=)
JP (1) JP2024511955A (https=)
WO (1) WO2022192749A2 (https=)

Families Citing this family (7)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20200131231A1 (en) 2017-02-17 2020-04-30 Oxford University Innovation Limited Cell penetrating peptides
GB201812980D0 (en) 2018-08-09 2018-09-26 Univ Oxford Innovation Ltd Cell-penetrating peptides
GB201812972D0 (en) 2018-08-09 2018-09-26 Univ Oxford Innovation Ltd Cell-penetrating peptides
US12465646B2 (en) 2018-12-07 2025-11-11 Oxford University Innovation Limited Linkers
EP4702143A2 (en) 2023-04-24 2026-03-04 BioMarin Pharmaceutical Inc. Compositions and methods for treating stxbp1 disorders
WO2025264554A1 (en) 2024-06-17 2025-12-26 Pepgen Inc. Antisense oligonucleotide conjugates targeting peripheral myelin protein 22 (pmp22) and methods of use thereof
WO2026080471A2 (en) 2024-10-07 2026-04-16 Flagship Pioneering Innovations Vi, Llc Compositions of trem conjugates and uses thereof

Family Cites Families (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN103998458B (zh) * 2011-08-30 2018-10-09 医学研究理事会 具有中央疏水域的细胞穿透肽
WO2015161255A1 (en) * 2014-04-18 2015-10-22 Board Of Regents Of The Nevada System Of Higher Education, On Behalf Of The University Of Nevada, Reno Methods for enhancing or decreasing the levels of mir124 and mir29 in subjects with muscular dystrophy
EP3858993A1 (en) * 2015-10-09 2021-08-04 Sarepta Therapeutics, Inc. Compositions and methods for treating duchenne muscular dystrophy and related disorders
GB201812972D0 (en) * 2018-08-09 2018-09-26 Univ Oxford Innovation Ltd Cell-penetrating peptides
US12465646B2 (en) * 2018-12-07 2025-11-11 Oxford University Innovation Limited Linkers
WO2022171972A1 (en) * 2021-02-12 2022-08-18 Oxford University Innovation Limited Cell-penetrating peptide conjugates and methods of their use

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