JP2024511954A5 - - Google Patents

Info

Publication number
JP2024511954A5
JP2024511954A5 JP2023555737A JP2023555737A JP2024511954A5 JP 2024511954 A5 JP2024511954 A5 JP 2024511954A5 JP 2023555737 A JP2023555737 A JP 2023555737A JP 2023555737 A JP2023555737 A JP 2023555737A JP 2024511954 A5 JP2024511954 A5 JP 2024511954A5
Authority
JP
Japan
Prior art keywords
pharmaceutical composition
composition according
seq
oligonucleotide
alkyl
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023555737A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024511954A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/020070 external-priority patent/WO2022192754A2/en
Publication of JP2024511954A publication Critical patent/JP2024511954A/ja
Publication of JP2024511954A5 publication Critical patent/JP2024511954A5/ja
Pending legal-status Critical Current

Links

JP2023555737A 2021-03-12 2022-03-11 ペプチド-オリゴヌクレオチド複合体を用いる筋強直性ジストロフィー1型の治療法 Pending JP2024511954A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163160710P 2021-03-12 2021-03-12
US63/160,710 2021-03-12
PCT/US2022/020070 WO2022192754A2 (en) 2021-03-12 2022-03-11 Methods of treating myotonic dystrophy type 1 using peptide-oligonucleotide conjugates

Publications (2)

Publication Number Publication Date
JP2024511954A JP2024511954A (ja) 2024-03-18
JP2024511954A5 true JP2024511954A5 (https=) 2025-04-03

Family

ID=83228538

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023555737A Pending JP2024511954A (ja) 2021-03-12 2022-03-11 ペプチド-オリゴヌクレオチド複合体を用いる筋強直性ジストロフィー1型の治療法

Country Status (6)

Country Link
US (1) US20240189434A1 (https=)
EP (1) EP4304657A4 (https=)
JP (1) JP2024511954A (https=)
CN (1) CN117425499A (https=)
CA (1) CA3212994A1 (https=)
WO (1) WO2022192754A2 (https=)

Families Citing this family (7)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20200131231A1 (en) 2017-02-17 2020-04-30 Oxford University Innovation Limited Cell penetrating peptides
GB201812980D0 (en) 2018-08-09 2018-09-26 Univ Oxford Innovation Ltd Cell-penetrating peptides
GB201812972D0 (en) 2018-08-09 2018-09-26 Univ Oxford Innovation Ltd Cell-penetrating peptides
US12465646B2 (en) 2018-12-07 2025-11-11 Oxford University Innovation Limited Linkers
WO2024097310A2 (en) * 2022-11-01 2024-05-10 Impilo Therapeutics, Inc. Targeted non-charged-nucleic acid (ncna) delivery and related tumor penetrating nanocomplexes
WO2025264554A1 (en) 2024-06-17 2025-12-26 Pepgen Inc. Antisense oligonucleotide conjugates targeting peripheral myelin protein 22 (pmp22) and methods of use thereof
WO2026080471A2 (en) 2024-10-07 2026-04-16 Flagship Pioneering Innovations Vi, Llc Compositions of trem conjugates and uses thereof

Family Cites Families (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US9740817B1 (en) * 2002-10-18 2017-08-22 Dennis Sunga Fernandez Apparatus for biological sensing and alerting of pharmaco-genomic mutation
EP2595663A4 (en) * 2010-07-19 2014-03-05 Isis Pharmaceuticals Inc MODULATION OF DYSTROPHIA MYOTONICA PROTEIN KINASE (DMPK) EXPRESSION
EP3034074A1 (en) * 2014-12-18 2016-06-22 Universitat De València, Estudi General Compound for treatment of myotonic dystrophy type 1
US12465646B2 (en) * 2018-12-07 2025-11-11 Oxford University Innovation Limited Linkers
GB201911403D0 (en) * 2019-08-09 2019-09-25 Univ Oxford Innovation Ltd Conjugate and uses thereof
WO2022171972A1 (en) * 2021-02-12 2022-08-18 Oxford University Innovation Limited Cell-penetrating peptide conjugates and methods of their use

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