JP2024529899A5 - - Google Patents

Info

Publication number
JP2024529899A5
JP2024529899A5 JP2024502462A JP2024502462A JP2024529899A5 JP 2024529899 A5 JP2024529899 A5 JP 2024529899A5 JP 2024502462 A JP2024502462 A JP 2024502462A JP 2024502462 A JP2024502462 A JP 2024502462A JP 2024529899 A5 JP2024529899 A5 JP 2024529899A5
Authority
JP
Japan
Prior art keywords
glycero
rna
guide
guide rna
phosphocholine
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024502462A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024529899A (ja
Filing date
Publication date
Priority claimed from PCT/US2021/042100 external-priority patent/WO2022016121A2/en
Application filed filed Critical
Priority claimed from PCT/US2022/037490 external-priority patent/WO2023288135A2/en
Publication of JP2024529899A publication Critical patent/JP2024529899A/ja
Publication of JP2024529899A5 publication Critical patent/JP2024529899A5/ja
Pending legal-status Critical Current

Links

JP2024502462A 2021-07-16 2022-07-18 関節機能を改善する遺伝子編集 Pending JP2024529899A (ja)

Applications Claiming Priority (9)

Application Number Priority Date Filing Date Title
USPCT/US2021/042100 2021-07-16
PCT/US2021/042100 WO2022016121A2 (en) 2020-07-16 2021-07-16 Gene editing to improve joint function
US202163222972P 2021-07-17 2021-07-17
US63/222,972 2021-07-17
US202263300822P 2022-01-19 2022-01-19
US63/300,822 2022-01-19
US202263326571P 2022-04-01 2022-04-01
US63/326,571 2022-04-01
PCT/US2022/037490 WO2023288135A2 (en) 2021-07-16 2022-07-18 Gene editing to improve joint function

Publications (2)

Publication Number Publication Date
JP2024529899A JP2024529899A (ja) 2024-08-14
JP2024529899A5 true JP2024529899A5 (https=) 2025-07-24

Family

ID=84919676

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024502462A Pending JP2024529899A (ja) 2021-07-16 2022-07-18 関節機能を改善する遺伝子編集

Country Status (10)

Country Link
US (1) US20230235321A1 (https=)
EP (1) EP4370165A4 (https=)
JP (1) JP2024529899A (https=)
KR (1) KR20240095529A (https=)
CN (1) CN119110732A (https=)
AU (1) AU2022311936A1 (https=)
CA (1) CA3226089A1 (https=)
IL (1) IL310118A (https=)
MX (1) MX2024000821A (https=)
WO (1) WO2023288135A2 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP4694913A2 (en) * 2023-04-11 2026-02-18 Orthobio Therapeutics, Inc. Lipid nanoparticles for gene editing systems

Family Cites Families (8)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20050282198A1 (en) * 1997-05-29 2005-12-22 Interleukin Genetics, Inc. Diagnostics and therapeutics for diseases associated with an IL-1 inflammatory haplotype
WO2016094872A1 (en) * 2014-12-12 2016-06-16 The Broad Institute Inc. Dead guides for crispr transcription factors
WO2017083722A1 (en) * 2015-11-11 2017-05-18 Greenberg Kenneth P Crispr compositions and methods of using the same for gene therapy
LT3436077T (lt) * 2016-03-30 2025-06-25 Intellia Therapeutics, Inc. Lipidų nanodalelių vaisto formos, skirtos crispr/cas komponentams
WO2019113061A1 (en) * 2017-12-06 2019-06-13 Klogene Therapeutics, Inc. Compositions and methods for modulating gene expression
EP3802578A4 (en) * 2018-06-01 2022-03-23 Washington University SUPPRESSION OF CYTOKINE RELEASE SYNDROME IN CHIMERIC ANTIGEN RECEPTOR CELL THERAPY
CN113557036A (zh) * 2019-01-18 2021-10-26 奥泽生物疗法公司 基因编辑以改善关节功能
EP3987087A4 (en) * 2019-06-21 2023-11-15 Function Oncology, Inc. GENETIC PHARMACEOPIA FOR COMPREHENSIVE FUNCTIONAL PROFILING OF HUMAN CANCERS

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