JP2024529875A5 - - Google Patents
Info
- Publication number
- JP2024529875A5 JP2024529875A5 JP2024501734A JP2024501734A JP2024529875A5 JP 2024529875 A5 JP2024529875 A5 JP 2024529875A5 JP 2024501734 A JP2024501734 A JP 2024501734A JP 2024501734 A JP2024501734 A JP 2024501734A JP 2024529875 A5 JP2024529875 A5 JP 2024529875A5
- Authority
- JP
- Japan
- Prior art keywords
- rna
- dux4
- administration
- manipulated
- disease
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163221568P | 2021-07-14 | 2021-07-14 | |
| US63/221,568 | 2021-07-14 | ||
| PCT/US2022/073754 WO2023288289A2 (en) | 2021-07-14 | 2022-07-14 | Oligonucleotides and compositions thereof for neuromuscular disorders |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2024529875A JP2024529875A (ja) | 2024-08-14 |
| JP2024529875A5 true JP2024529875A5 (enExample) | 2025-07-22 |
Family
ID=83188125
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024501734A Pending JP2024529875A (ja) | 2021-07-14 | 2022-07-14 | 神経筋障害のためのオリゴヌクレオチドおよびその組成物 |
Country Status (11)
| Country | Link |
|---|---|
| US (1) | US20240271134A1 (enExample) |
| EP (1) | EP4370678A2 (enExample) |
| JP (1) | JP2024529875A (enExample) |
| KR (1) | KR20240032998A (enExample) |
| CN (1) | CN117677698A (enExample) |
| AU (1) | AU2022312501A1 (enExample) |
| CA (1) | CA3223876A1 (enExample) |
| CO (1) | CO2024000116A2 (enExample) |
| IL (1) | IL310063A (enExample) |
| MX (1) | MX2024000754A (enExample) |
| WO (1) | WO2023288289A2 (enExample) |
Families Citing this family (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| TW202144572A (zh) | 2020-03-19 | 2021-12-01 | 美商亞維代堤生物科學公司 | 治療臉肩胛肱骨肌肉失養症之組合物及方法 |
| EP4401792A4 (en) | 2021-09-16 | 2025-12-03 | Avidity Biosciences Inc | COMPOSITIONS AND METHODS OF TREATMENT OF FACIO-SCAPULO-HUMERAL MUSCULAR DYSTROPHY |
| US20260159835A1 (en) * | 2024-12-05 | 2026-06-11 | Soufflé Therapeutics, Inc. | Oligonucleotide-mediated knockdown of dux4 |
Family Cites Families (16)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US5132418A (en) | 1980-02-29 | 1992-07-21 | University Patents, Inc. | Process for preparing polynucleotides |
| US4458066A (en) | 1980-02-29 | 1984-07-03 | University Patents, Inc. | Process for preparing polynucleotides |
| US4500707A (en) | 1980-02-29 | 1985-02-19 | University Patents, Inc. | Nucleosides useful in the preparation of polynucleotides |
| US4415732A (en) | 1981-03-27 | 1983-11-15 | University Patents, Inc. | Phosphoramidite compounds and processes |
| US4973679A (en) | 1981-03-27 | 1990-11-27 | University Patents, Inc. | Process for oligonucleo tide synthesis using phosphormidite intermediates |
| US4668777A (en) | 1981-03-27 | 1987-05-26 | University Patents, Inc. | Phosphoramidite nucleoside compounds |
| US4373071A (en) | 1981-04-30 | 1983-02-08 | City Of Hope Research Institute | Solid-phase synthesis of polynucleotides |
| US4401796A (en) | 1981-04-30 | 1983-08-30 | City Of Hope Research Institute | Solid-phase synthesis of polynucleotides |
| US5153319A (en) | 1986-03-31 | 1992-10-06 | University Patents, Inc. | Process for preparing polynucleotides |
| US5047524A (en) | 1988-12-21 | 1991-09-10 | Applied Biosystems, Inc. | Automated system for polynucleotide synthesis and purification |
| US5262530A (en) | 1988-12-21 | 1993-11-16 | Applied Biosystems, Inc. | Automated system for polynucleotide synthesis and purification |
| US5700642A (en) | 1995-05-22 | 1997-12-23 | Sri International | Oligonucleotide sizing using immobilized cleavable primers |
| CA2842798C (en) * | 2011-07-25 | 2021-02-23 | Nationwide Children's Hospital, Inc. | Recombinant virus products and methods for inhibition of expression of dux4 |
| WO2017007886A2 (en) * | 2015-07-08 | 2017-01-12 | Idera Pharmaceuticals, Inc. | Compositions for inhibiting dux4 gene expression and uses thereof |
| CN116096890A (zh) | 2020-04-02 | 2023-05-09 | 米雷楚莱股份有限公司 | 使用工程化寡核苷酸的靶向抑制 |
| US20240336915A1 (en) * | 2021-01-22 | 2024-10-10 | Ionis Pharmaceuticals, Inc. | Compounds and methods for reducing dux4 expression |
-
2022
- 2022-07-14 CN CN202280049575.5A patent/CN117677698A/zh active Pending
- 2022-07-14 EP EP22764588.4A patent/EP4370678A2/en active Pending
- 2022-07-14 JP JP2024501734A patent/JP2024529875A/ja active Pending
- 2022-07-14 WO PCT/US2022/073754 patent/WO2023288289A2/en not_active Ceased
- 2022-07-14 MX MX2024000754A patent/MX2024000754A/es unknown
- 2022-07-14 KR KR1020247004600A patent/KR20240032998A/ko active Pending
- 2022-07-14 CA CA3223876A patent/CA3223876A1/en active Pending
- 2022-07-14 IL IL310063A patent/IL310063A/en unknown
- 2022-07-14 AU AU2022312501A patent/AU2022312501A1/en active Pending
-
2024
- 2024-01-10 CO CONC2024/0000116A patent/CO2024000116A2/es unknown
- 2024-01-12 US US18/411,650 patent/US20240271134A1/en active Pending
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