JP2024529425A5 - - Google Patents

Info

Publication number
JP2024529425A5
JP2024529425A5 JP2024504461A JP2024504461A JP2024529425A5 JP 2024529425 A5 JP2024529425 A5 JP 2024529425A5 JP 2024504461 A JP2024504461 A JP 2024504461A JP 2024504461 A JP2024504461 A JP 2024504461A JP 2024529425 A5 JP2024529425 A5 JP 2024529425A5
Authority
JP
Japan
Prior art keywords
grna
amino acid
cas9
adenosine deaminase
sequence
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024504461A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024529425A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/074041 external-priority patent/WO2023004409A1/en
Publication of JP2024529425A publication Critical patent/JP2024529425A/ja
Publication of JP2024529425A5 publication Critical patent/JP2024529425A5/ja
Pending legal-status Critical Current

Links

JP2024504461A 2021-07-23 2022-07-22 CRISPR/Cas編集系のためのガイドRNA Pending JP2024529425A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202163225322P 2021-07-23 2021-07-23
US63/225,322 2021-07-23
US202163255927P 2021-10-14 2021-10-14
US63/255,927 2021-10-14
PCT/US2022/074041 WO2023004409A1 (en) 2021-07-23 2022-07-22 Guide rnas for crispr/cas editing systems

Publications (2)

Publication Number Publication Date
JP2024529425A JP2024529425A (ja) 2024-08-06
JP2024529425A5 true JP2024529425A5 (enExample) 2025-07-18

Family

ID=83149172

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024504461A Pending JP2024529425A (ja) 2021-07-23 2022-07-22 CRISPR/Cas編集系のためのガイドRNA

Country Status (7)

Country Link
US (1) US20240301405A1 (enExample)
EP (1) EP4373931A1 (enExample)
JP (1) JP2024529425A (enExample)
KR (1) KR20240037299A (enExample)
AU (1) AU2022313315A1 (enExample)
CA (1) CA3226664A1 (enExample)
WO (1) WO2023004409A1 (enExample)

Families Citing this family (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20230383277A1 (en) * 2020-10-14 2023-11-30 Beam Therapeutics Inc. Compositions and methods for treating glycogen storage disease type 1a
WO2024220980A2 (en) * 2023-04-20 2024-10-24 The Schepens Eye Research Institute, Inc. Dscam inhibitory nucleic acids and methods of use thereof
JP2026523341A (ja) 2023-05-15 2026-07-14 エヌクロマ・バイオ,インコーポレーテッド Hbv遺伝子発現のエピジェネティック調節のための組成物および方法
CN122161928A (zh) * 2023-10-25 2026-06-05 上海尧唐生物科技股份有限公司 一种脱氨酶、包含其的碱基编辑器及其应用

Family Cites Families (18)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US4880635B1 (en) 1984-08-08 1996-07-02 Liposome Company Dehydrated liposomes
US4921757A (en) 1985-04-26 1990-05-01 Massachusetts Institute Of Technology System for delayed and pulsed release of biologically active substances
US4920016A (en) 1986-12-24 1990-04-24 Linear Technology, Inc. Liposomes with enhanced circulation time
JPH0825869B2 (ja) 1987-02-09 1996-03-13 株式会社ビタミン研究所 抗腫瘍剤包埋リポソ−ム製剤
US4917951A (en) 1987-07-28 1990-04-17 Micro-Pak, Inc. Lipid vesicles formed of surfactants and steroids
US4911928A (en) 1987-03-13 1990-03-27 Micro-Pak, Inc. Paucilamellar lipid vesicles
US5846946A (en) 1996-06-14 1998-12-08 Pasteur Merieux Serums Et Vaccins Compositions and methods for administering Borrelia DNA
EP2397490B1 (en) 2004-07-16 2013-09-04 THE UNITED STATES OF AMERICA, represented by THE SECRETARY, DEPARTMENT OF HEALTH AND HUMAN SERVICES Vaccine constructs and combinations of vaccines designed to improve the breadth of the immune response to diverse strains and clades of HIV
JP2011512326A (ja) 2007-12-31 2011-04-21 ナノコア セラピューティクス,インコーポレイテッド 心不全の治療用のrna干渉
ES2728782T3 (es) 2012-05-25 2019-10-28 Univ California Métodos y composiciones para la modificación de ADN objetivo dirigida por ARN y para la modulación de la transcripción dirigida por ARN
CN105139759B (zh) 2015-09-18 2017-10-10 京东方科技集团股份有限公司 一种拼接屏
US11286480B2 (en) * 2015-09-28 2022-03-29 North Carolina State University Methods and compositions for sequence specific antimicrobials
WO2017070632A2 (en) 2015-10-23 2017-04-27 President And Fellows Of Harvard College Nucleobase editors and uses thereof
WO2018027078A1 (en) 2016-08-03 2018-02-08 President And Fellows Of Harard College Adenosine nucleobase editors and uses thereof
EP3829597A4 (en) * 2018-07-30 2022-05-18 Sarepta Therapeutics, Inc. TRIMER PEPTIDES FOR ANTISENSE ADMINISTRATION
JP2020038883A (ja) 2018-09-03 2020-03-12 株式会社オートネットワーク技術研究所 回路構造体及び回路構造体の製造方法
EP4034658A4 (en) * 2019-09-23 2023-11-29 Flagship Pioneering Innovations V, Inc. MODULATION OF GENOMIC COMPLEXES
EP4058032A4 (en) * 2019-12-19 2024-01-10 Entrada Therapeutics, Inc. Compositions for delivery of antisense compounds

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