JP2024529425A5 - - Google Patents

Info

Publication number
JP2024529425A5
JP2024529425A5 JP2024504461A JP2024504461A JP2024529425A5 JP 2024529425 A5 JP2024529425 A5 JP 2024529425A5 JP 2024504461 A JP2024504461 A JP 2024504461A JP 2024504461 A JP2024504461 A JP 2024504461A JP 2024529425 A5 JP2024529425 A5 JP 2024529425A5
Authority
JP
Japan
Prior art keywords
grna
amino acid
cas9
adenosine deaminase
sequence
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024504461A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024529425A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/074041 external-priority patent/WO2023004409A1/en
Publication of JP2024529425A publication Critical patent/JP2024529425A/ja
Publication of JP2024529425A5 publication Critical patent/JP2024529425A5/ja
Pending legal-status Critical Current

Links

JP2024504461A 2021-07-23 2022-07-22 CRISPR/Cas編集系のためのガイドRNA Pending JP2024529425A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202163225322P 2021-07-23 2021-07-23
US63/225,322 2021-07-23
US202163255927P 2021-10-14 2021-10-14
US63/255,927 2021-10-14
PCT/US2022/074041 WO2023004409A1 (en) 2021-07-23 2022-07-22 Guide rnas for crispr/cas editing systems

Publications (2)

Publication Number Publication Date
JP2024529425A JP2024529425A (ja) 2024-08-06
JP2024529425A5 true JP2024529425A5 (enExample) 2025-07-18

Family

ID=83149172

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024504461A Pending JP2024529425A (ja) 2021-07-23 2022-07-22 CRISPR/Cas編集系のためのガイドRNA

Country Status (7)

Country Link
US (1) US20240301405A1 (enExample)
EP (1) EP4373931A1 (enExample)
JP (1) JP2024529425A (enExample)
KR (1) KR20240037299A (enExample)
AU (1) AU2022313315A1 (enExample)
CA (1) CA3226664A1 (enExample)
WO (1) WO2023004409A1 (enExample)

Families Citing this family (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CA3198671A1 (en) * 2020-10-14 2022-04-21 Beam Therapeutics Inc. Compositions and methods for treating glycogen storage disease type 1a
WO2024220980A2 (en) * 2023-04-20 2024-10-24 The Schepens Eye Research Institute, Inc. Dscam inhibitory nucleic acids and methods of use thereof
AU2024270764A1 (en) 2023-05-15 2025-12-04 Nchroma Bio, Inc. Compositions and methods for epigenetic regulation of hbv gene expression
WO2025087411A1 (zh) * 2023-10-25 2025-05-01 尧唐(上海)生物科技有限公司 一种脱氨酶、包含其的碱基编辑器及其应用

Family Cites Families (18)

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US4880635B1 (en) 1984-08-08 1996-07-02 Liposome Company Dehydrated liposomes
US4921757A (en) 1985-04-26 1990-05-01 Massachusetts Institute Of Technology System for delayed and pulsed release of biologically active substances
US4920016A (en) 1986-12-24 1990-04-24 Linear Technology, Inc. Liposomes with enhanced circulation time
JPH0825869B2 (ja) 1987-02-09 1996-03-13 株式会社ビタミン研究所 抗腫瘍剤包埋リポソ−ム製剤
US4917951A (en) 1987-07-28 1990-04-17 Micro-Pak, Inc. Lipid vesicles formed of surfactants and steroids
US4911928A (en) 1987-03-13 1990-03-27 Micro-Pak, Inc. Paucilamellar lipid vesicles
US5846946A (en) 1996-06-14 1998-12-08 Pasteur Merieux Serums Et Vaccins Compositions and methods for administering Borrelia DNA
AU2005274948B2 (en) 2004-07-16 2011-09-22 Genvec, Inc. Vaccines against aids comprising CMV/R-nucleic acid constructs
US8404658B2 (en) 2007-12-31 2013-03-26 Nanocor Therapeutics, Inc. RNA interference for the treatment of heart failure
AU2013266968B2 (en) 2012-05-25 2017-06-29 Emmanuelle CHARPENTIER Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription
CN105139759B (zh) 2015-09-18 2017-10-10 京东方科技集团股份有限公司 一种拼接屏
EP3356533A1 (en) * 2015-09-28 2018-08-08 North Carolina State University Methods and compositions for sequence specific antimicrobials
IL310721B2 (en) 2015-10-23 2025-11-01 Harvard College Nucleobase editors and uses thereof
CN110214183A (zh) 2016-08-03 2019-09-06 哈佛大学的校长及成员们 腺苷核碱基编辑器及其用途
JP7564087B2 (ja) * 2018-07-30 2024-10-08 サレプタ セラピューティクス, インコーポレイテッド アンチセンス送達のための三量体ペプチド
JP2020038883A (ja) 2018-09-03 2020-03-12 株式会社オートネットワーク技術研究所 回路構造体及び回路構造体の製造方法
CA3154759A1 (en) * 2019-09-23 2021-04-01 Flagship Pioneering Innovations V, Inc. Modulating genomic complexes
EP4058032A4 (en) * 2019-12-19 2024-01-10 Entrada Therapeutics, Inc. Compositions for delivery of antisense compounds

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