JP2024524332A5 - - Google Patents

Info

Publication number
JP2024524332A5
JP2024524332A5 JP2023579741A JP2023579741A JP2024524332A5 JP 2024524332 A5 JP2024524332 A5 JP 2024524332A5 JP 2023579741 A JP2023579741 A JP 2023579741A JP 2023579741 A JP2023579741 A JP 2023579741A JP 2024524332 A5 JP2024524332 A5 JP 2024524332A5
Authority
JP
Japan
Prior art keywords
exon
seq
aso
oligonucleotide
sequence
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023579741A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024524332A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/EP2022/068313 external-priority patent/WO2023275376A1/en
Publication of JP2024524332A publication Critical patent/JP2024524332A/ja
Publication of JP2024524332A5 publication Critical patent/JP2024524332A5/ja
Pending legal-status Critical Current

Links

JP2023579741A 2021-07-02 2022-07-01 アルツハイマー病の治療方法 Pending JP2024524332A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
EP21183395 2021-07-02
EP21183395.9 2021-07-02
PCT/EP2022/068313 WO2023275376A1 (en) 2021-07-02 2022-07-01 Methods of treating alzheimer's disease

Publications (2)

Publication Number Publication Date
JP2024524332A JP2024524332A (ja) 2024-07-05
JP2024524332A5 true JP2024524332A5 (https=) 2025-07-08

Family

ID=76764882

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023579741A Pending JP2024524332A (ja) 2021-07-02 2022-07-01 アルツハイマー病の治療方法

Country Status (4)

Country Link
US (1) US20240279666A1 (https=)
EP (1) EP4363578A1 (https=)
JP (1) JP2024524332A (https=)
WO (1) WO2023275376A1 (https=)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2024178386A1 (en) 2023-02-24 2024-08-29 Aarhus Universitet Methods of treating endosomal trafficking diseases
WO2025262002A2 (en) * 2024-06-17 2025-12-26 Aarhus Universitet Antisense oligonucleotides for treating alzheimer's disease

Family Cites Families (9)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2008052016A2 (en) * 2006-10-23 2008-05-02 Columbia University The sortilin-related receptor sorl1 is functionally and genetically associated with alzheimer's disease
BR122020021379B1 (pt) * 2008-10-24 2021-05-11 Sarepta Therapeutics, Inc. oligômero morfolino fosforodiamidato, composição que compreende o mesmo e uso do dito oligômero para tratar distrofia muscular
US9994893B2 (en) * 2011-12-13 2018-06-12 Rutgers, The State University Of New Jersey Compositions and methods for functional quality control for human blood-based gene expression products
KR102040364B1 (ko) * 2017-05-26 2019-11-05 가천대학교 산학협력단 알츠하이머병 관련 30개 유전자를 이용한 유전적 진단방법
WO2019012542A1 (en) * 2017-07-13 2019-01-17 Yissum Research Development Company Of The Hebrew University Of Jerusalem Ltd. DETECTION OF SPECIFIC DNA FROM A FABRIC
KR102318434B1 (ko) * 2017-08-25 2021-11-01 스톡 테라퓨틱스, 인크. 병태 및 질환 치료용 안티센스 올리고머
GB201803010D0 (en) * 2018-02-26 2018-04-11 Royal Holloway & Bedford New College Neurodegenerative disorders
EP3819378A4 (en) * 2018-07-04 2022-09-14 Aichi Medical University OLIGONUCLEOTIDES FOR CONTROL OF TAU SPLICING AND THEIR USES
IL293997A (en) * 2019-12-19 2022-08-01 Nippon Shinyaku Co Ltd Antistrand nucleic acids that allow exon skipping

Similar Documents

Publication Publication Date Title
JP6425775B2 (ja) 真核細胞におけるエキソンスキッピングの誘導
ES2837437T3 (es) Usos diagnósticos, pronósticos y terapéuticos de ARN largos no codificantes para cardiopatías y medicina regenerativa
JP7531514B2 (ja) 操作されたmRNA配列及びその使用
US8962582B2 (en) PKR activation via hybridization chain reaction
AU2014337506B2 (en) Methods for modulating expression of C9ORF72 antisense transcript
US20050064449A1 (en) Single copy genomic hybridization probes and method of generating same
JP2019500346A (ja) 腎臓病の処置のための組成物と方法
US20160024575A1 (en) Circulating small noncoding rna markers
JP2019500350A (ja) 結節性硬化症の処置のためのアンチセンスオリゴマー
EP3371328A2 (en) Compositions for inhibiting nlrp3 gene expression and uses thereof
TW201143780A (en) Treatment of Colony-stimulating factor 3 (CSF3) related diseases by inhibition of natural antisense transcript to CSF3
JP2024524332A5 (https=)
JP2004501211A5 (https=)
CN118647722A (zh) Fgg相关疾病和病症的治疗
US12421552B2 (en) MicroRNA-134 biomarker
JPH10513052A (ja) ヒト・ヒスタミンh▲下2▼ レセプターの新規対立遺伝子およびh▲下2▼ レセプター変異種の検出方法
EP4133110A1 (en) Floating barcodes
CN104099349B (zh) 枫糖尿病相关基因突变、其检测方法及其用途
US11674180B2 (en) Method and kit for determining hyperexcitability in subject
US20250092396A1 (en) Treatment Of Osteoarthritis With Cartilage Intermediate Layer Protein 2 (CILP2) Inhibitors
WO2014169294A1 (en) Mutations in dstyk cause dominant urinary tract malformations
CN117940565A (zh) 用Wnt家族成员5B(WNT5B)抑制剂治疗骨矿物质密度降低
HK40119876A (zh) 跨膜受体基因编辑
CN118265529A (zh) 使用camp应答元件结合蛋白3样3(creb3l3)抑制剂的肝病治疗
CN118891050A (zh) 用Rho鸟嘌呤核苷酸交换因子12(ARHGEF12)抑制剂治疗青光眼