JP2024524291A5 - - Google Patents

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Publication number
JP2024524291A5
JP2024524291A5 JP2023579457A JP2023579457A JP2024524291A5 JP 2024524291 A5 JP2024524291 A5 JP 2024524291A5 JP 2023579457 A JP2023579457 A JP 2023579457A JP 2023579457 A JP2023579457 A JP 2023579457A JP 2024524291 A5 JP2024524291 A5 JP 2024524291A5
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JP
Japan
Prior art keywords
cag cag
compound according
peptide
extracyclic
compound
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023579457A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024524291A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/034517 external-priority patent/WO2022271818A1/en
Publication of JP2024524291A publication Critical patent/JP2024524291A/ja
Publication of JP2024524291A5 publication Critical patent/JP2024524291A5/ja
Pending legal-status Critical Current

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JP2023579457A 2021-06-23 2022-06-22 Cugリピートを標的とするためのアンチセンス化合物及び方法 Pending JP2024524291A (ja)

Applications Claiming Priority (31)

Application Number Priority Date Filing Date Title
US202163213900P 2021-06-23 2021-06-23
US63/213,900 2021-06-23
US202163239847P 2021-09-01 2021-09-01
US202163239671P 2021-09-01 2021-09-01
US63/239,671 2021-09-01
US63/239,847 2021-09-01
US202163290960P 2021-12-17 2021-12-17
US202163290892P 2021-12-17 2021-12-17
US63/290,892 2021-12-17
US63/290,960 2021-12-17
US202263298565P 2022-01-11 2022-01-11
US63/298,565 2022-01-11
US202263305071P 2022-01-31 2022-01-31
US63/305,071 2022-01-31
US202263268577P 2022-02-25 2022-02-25
US63/268,577 2022-02-25
US202263314369P 2022-02-26 2022-02-26
US63/314,369 2022-02-26
US202263316634P 2022-03-04 2022-03-04
US63/316,634 2022-03-04
US202263317856P 2022-03-08 2022-03-08
US63/317,856 2022-03-08
US202263326201P 2022-03-31 2022-03-31
US202263362295P 2022-03-31 2022-03-31
US63/362,295 2022-03-31
US63/326,201 2022-03-31
US202263327179P 2022-04-04 2022-04-04
US63/327,179 2022-04-04
US202263339250P 2022-05-06 2022-05-06
US63/339,250 2022-05-06
PCT/US2022/034517 WO2022271818A1 (en) 2021-06-23 2022-06-22 Antisense compounds and methods for targeting cug repeats

Publications (2)

Publication Number Publication Date
JP2024524291A JP2024524291A (ja) 2024-07-05
JP2024524291A5 true JP2024524291A5 (enExample) 2025-07-01

Family

ID=82608300

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023579457A Pending JP2024524291A (ja) 2021-06-23 2022-06-22 Cugリピートを標的とするためのアンチセンス化合物及び方法

Country Status (15)

Country Link
EP (1) EP4359006A1 (enExample)
JP (1) JP2024524291A (enExample)
KR (1) KR20240038967A (enExample)
AU (1) AU2022298774A1 (enExample)
CA (1) CA3222824A1 (enExample)
CL (1) CL2023003840A1 (enExample)
CO (1) CO2023018002A2 (enExample)
DO (1) DOP2023000279A (enExample)
EC (1) ECSP23096162A (enExample)
GE (1) GEAP202416440A (enExample)
IL (1) IL309001A (enExample)
JO (1) JOP20230327A1 (enExample)
MX (1) MX2023015509A (enExample)
PE (1) PE20242357A1 (enExample)
WO (1) WO2022271818A1 (enExample)

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WO2025038901A1 (en) * 2023-08-17 2025-02-20 Entrada Therapeutics, Inc. Cyclic peptides for delivering therapeutics
WO2025072246A1 (en) * 2023-09-26 2025-04-03 Entrada Therapeutics, Inc. Compounds and methods for skipping exon 50 in duchenne muscular dystrophy
WO2025137623A1 (en) * 2023-12-22 2025-06-26 Iris Medicine, Inc. Methods and compositions for treating ctg repeat expansion diseases
EP4692348A1 (en) * 2024-08-07 2026-02-11 Nocturna Therapeutics SL Artificial rnas for treating repeat expansion disorders

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