JP2024523394A - 異常な遺伝子発現を調節するためのシステムおよび方法 - Google Patents

異常な遺伝子発現を調節するためのシステムおよび方法 Download PDF

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JP2024523394A
JP2024523394A JP2023577861A JP2023577861A JP2024523394A JP 2024523394 A JP2024523394 A JP 2024523394A JP 2023577861 A JP2023577861 A JP 2023577861A JP 2023577861 A JP2023577861 A JP 2023577861A JP 2024523394 A JP2024523394 A JP 2024523394A
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target gene
gene
heterologous
cells
krab
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JP2024523394A5 (enExample
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ドゥ ロルテ， アレクサンドラ シルヴィー コリン
ローズマリー ウェンティング ツォア，
アビナブ アディカリ，
シッダラジュ ボレゴウダ，
ダニエル オー． ハート，
トーマス ブレア ゲイナス，
ジョヴァンニ カロッソ，
シャオ ヤン，
ティモシー デイリー，
タオ グエン ヴ ルオン，
ヤンシャ リウ，
テンギュ コ，
アンバー ルース サルツマン，
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エピクリスパー バイオテクノロジーズ， インコーポレイテッド
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JP2023577861A 2021-06-17 2022-06-16 異常な遺伝子発現を調節するためのシステムおよび方法 Pending JP2024523394A (ja)

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US202163211791P 2021-06-17 2021-06-17
US63/211,791 2021-06-17
PCT/US2022/033797 WO2022266324A1 (en) 2021-06-17 2022-06-16 Systems and methods for regulating aberrant gene expressions

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KR20230076820A (ko) 2020-09-01 2023-05-31 더 보드 어브 트러스티스 어브 더 리랜드 스탠포드 주니어 유니버시티 진핵생물 유전체 공학을 위한 합성 미니어처 crispr-cas(casmini) 시스템
JP2025507822A (ja) 2022-03-01 2025-03-21 エピクリスパー バイオテクノロジーズ， インコーポレイテッド 組換えヌクレアーゼならびにその組成物および使用方法
CN121127598A (zh) * 2023-03-16 2025-12-12 埃皮克里斯皮尔生物技术公司 用于调控异常基因表达的系统和方法
CN119955797B (zh) * 2025-01-13 2026-01-23 江南大学 Kif5b基因在调控成肌细胞生理活性中的功能和应用
CN119954926B (zh) * 2025-03-11 2025-10-28 华南农业大学 Klf5转录因子在调控猪骨骼肌发育中的应用及方法

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WO2018057863A1 (en) * 2016-09-23 2018-03-29 University Of Massachusetts Silencing of dux4 by recombinant gene editing complexes
JP2019534298A (ja) * 2016-11-07 2019-11-28 ユニバーシティ オブ マサチューセッツ 顔面肩甲上腕型筋ジストロフィーのための治療標的
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EP4355357A4 (en) 2025-08-20
GB202319324D0 (en) 2024-01-31
AU2022293494A1 (en) 2024-01-04
GB2624791A (en) 2024-05-29
IL309174A (en) 2024-02-01
EP4355357A1 (en) 2024-04-24
MX2023014750A (es) 2024-03-08
WO2022266324A1 (en) 2022-12-22
CA3221874A1 (en) 2022-12-22
CN117940150A (zh) 2024-04-26
US20240216482A1 (en) 2024-07-04

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