JP2024521767A5 - - Google Patents

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Publication number
JP2024521767A5
JP2024521767A5 JP2023572717A JP2023572717A JP2024521767A5 JP 2024521767 A5 JP2024521767 A5 JP 2024521767A5 JP 2023572717 A JP2023572717 A JP 2023572717A JP 2023572717 A JP2023572717 A JP 2023572717A JP 2024521767 A5 JP2024521767 A5 JP 2024521767A5
Authority
JP
Japan
Prior art keywords
nucleic acid
composition according
disease
complement
amd
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023572717A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024521767A (ja
Filing date
Publication date
Priority claimed from GBGB2107586.6A external-priority patent/GB202107586D0/en
Application filed filed Critical
Publication of JP2024521767A publication Critical patent/JP2024521767A/ja
Publication of JP2024521767A5 publication Critical patent/JP2024521767A5/ja
Pending legal-status Critical Current

Links

JP2023572717A 2021-05-27 2022-05-26 H因子ファミリータンパク質のための阻害性核酸 Pending JP2024521767A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
GBGB2107586.6A GB202107586D0 (en) 2021-05-27 2021-05-27 Inhibitory nucleic acids for Factor H family proteins
GB2107586.6 2021-05-27
PCT/EP2022/064376 WO2022248651A2 (en) 2021-05-27 2022-05-26 Inhibitory nucleic acids for factor h family proteins

Publications (2)

Publication Number Publication Date
JP2024521767A JP2024521767A (ja) 2024-06-04
JP2024521767A5 true JP2024521767A5 (cg-RX-API-DMAC10.html) 2025-06-03

Family

ID=76741290

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023572717A Pending JP2024521767A (ja) 2021-05-27 2022-05-26 H因子ファミリータンパク質のための阻害性核酸

Country Status (8)

Country Link
US (1) US20240209367A1 (cg-RX-API-DMAC10.html)
EP (1) EP4347030A2 (cg-RX-API-DMAC10.html)
JP (1) JP2024521767A (cg-RX-API-DMAC10.html)
CN (1) CN118632711A (cg-RX-API-DMAC10.html)
AU (1) AU2022279580A1 (cg-RX-API-DMAC10.html)
CA (1) CA3219247A1 (cg-RX-API-DMAC10.html)
GB (1) GB202107586D0 (cg-RX-API-DMAC10.html)
WO (1) WO2022248651A2 (cg-RX-API-DMAC10.html)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
AU2024218976A1 (en) * 2023-02-06 2025-09-11 E-Therapeutics Plc Inhibitors of expression and/or function
WO2026101913A1 (en) * 2024-11-05 2026-05-15 Alnylam Pharmaceuticals, Inc. Sirnas targeting complement factor h-related (cfhr) gene transcripts and methods of use

Family Cites Families (17)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US7217807B2 (en) * 2002-11-26 2007-05-15 Rosetta Genomics Ltd Bioinformatically detectable group of novel HIV regulatory genes and uses thereof
US20050118625A1 (en) * 2003-10-02 2005-06-02 Mounts William M. Nucleic acid arrays for detecting gene expression associated with human osteoarthritis and human proteases
CA2566286A1 (en) * 2004-05-11 2005-12-08 Rnai Co., Ltd. Polynucleotide causing rna interfere and method of regulating gene expression with the use of the same
US7745389B2 (en) 2005-02-14 2010-06-29 University Of Iowa Research Foundation Methods for treatment of age-related macular degeneration
GB0611606D0 (en) * 2006-06-13 2006-07-19 Univ Belfast Protection against and treatment of age related macular degeneration
DK2447275T3 (en) * 2006-07-13 2015-06-29 Univ Iowa Res Found Methods and reagents for the treatment of age-related macular degeneration
WO2009059317A2 (en) 2007-11-01 2009-05-07 University Of Iowa Research Foundation Predicting amd with snps within or near c2, factor b, plekha1, htra1, prelp, or loc387715
US9598733B2 (en) 2011-02-17 2017-03-21 The Trustees Of Columbia University In The City Of New York Methods for identifying subjects with a genetic risk for developing IgA nephropathy
WO2013151192A1 (ko) 2012-04-02 2013-10-10 주식회사 성균바이오텍 등골나물속 추출물을 유효성분으로 하는 비만 및 골대사질환 예방 및 치료용 조성물
EA201492055A1 (ru) 2012-06-08 2015-11-30 Шир Хьюман Дженетик Терапис, Инк. ИНГАЛЯЦИОННАЯ ДОСТАВКА мРНК В НЕЛЕГОЧНЫЕ КЛЕТКИ-МИШЕНИ
GB201301632D0 (en) * 2013-01-30 2013-03-13 Imp Innovations Complement System
WO2017070632A2 (en) 2015-10-23 2017-04-27 President And Fellows Of Harvard College Nucleobase editors and uses thereof
GB201709222D0 (en) 2017-06-09 2017-07-26 Univ Manchester C3b Inactivating Polypeptide
JP2020533414A (ja) * 2017-09-11 2020-11-19 インサイドアウトバイオ インコーポレイテッド 腫瘍の免疫原性を増強する方法および組成物
GB201800620D0 (en) 2018-01-15 2018-02-28 Univ Manchester C3b Binding Polypeptide
JP7467355B2 (ja) 2018-05-10 2024-04-15 コンプリメント・セラピューティクス・リミテッド 黄斑変性症を評価するための方法
EP4214515A1 (en) 2020-09-16 2023-07-26 Complement Therapeutics Limited Complementome assay

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