JP2024095680A5 - - Google Patents
Download PDFInfo
- Publication number
- JP2024095680A5 JP2024095680A5 JP2024040767A JP2024040767A JP2024095680A5 JP 2024095680 A5 JP2024095680 A5 JP 2024095680A5 JP 2024040767 A JP2024040767 A JP 2024040767A JP 2024040767 A JP2024040767 A JP 2024040767A JP 2024095680 A5 JP2024095680 A5 JP 2024095680A5
- Authority
- JP
- Japan
- Prior art keywords
- pharmaceutical composition
- human
- human subject
- months
- brain mass
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (4)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201862699923P | 2018-07-18 | 2018-07-18 | |
| US62/699,923 | 2018-07-18 | ||
| PCT/US2019/042205 WO2020018665A1 (en) | 2018-07-18 | 2019-07-17 | Treatment of mucopolysaccharidosis i with fully-human glycosylated human alpha-l-iduronidase (idus) |
| JP2021502545A JP2021531276A (ja) | 2018-07-18 | 2019-07-17 | 完全ヒトグリコシル化ヒトα−Ｌ−イズロニダーゼ（ＩＤＵＡ）を用いたムコ多糖症Ｉ型の治療 |
Related Parent Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021502545A Division JP2021531276A (ja) | 2018-07-18 | 2019-07-17 | 完全ヒトグリコシル化ヒトα−Ｌ−イズロニダーゼ（ＩＤＵＡ）を用いたムコ多糖症Ｉ型の治療 |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2024095680A JP2024095680A (ja) | 2024-07-10 |
| JP2024095680A5 true JP2024095680A5 (https=) | 2024-09-18 |
Family
ID=69164759
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021502545A Pending JP2021531276A (ja) | 2018-07-18 | 2019-07-17 | 完全ヒトグリコシル化ヒトα−Ｌ−イズロニダーゼ（ＩＤＵＡ）を用いたムコ多糖症Ｉ型の治療 |
| JP2024040767A Pending JP2024095680A (ja) | 2018-07-18 | 2024-03-15 | 完全ヒトグリコシル化ヒトα－Ｌ－イズロニダーゼ（ＩＤＵＡ）を用いたムコ多糖症Ｉ型の治療 |
Family Applications Before (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021502545A Pending JP2021531276A (ja) | 2018-07-18 | 2019-07-17 | 完全ヒトグリコシル化ヒトα−Ｌ−イズロニダーゼ（ＩＤＵＡ）を用いたムコ多糖症Ｉ型の治療 |
Country Status (10)
| Country | Link |
|---|---|
| US (1) | US20210275647A1 (https=) |
| EP (1) | EP3823590A4 (https=) |
| JP (2) | JP2021531276A (https=) |
| KR (1) | KR20210034037A (https=) |
| AU (1) | AU2019306236A1 (https=) |
| BR (1) | BR112021000830A2 (https=) |
| CA (1) | CA3106651A1 (https=) |
| IL (1) | IL280198B2 (https=) |
| SG (1) | SG11202100423YA (https=) |
| WO (1) | WO2020018665A1 (https=) |
Families Citing this family (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| MA50016A (fr) | 2017-07-06 | 2020-07-08 | Univ Pennsylvania | Thérapie génique médiée par aav9 pour traiter la mucopolysaccharidose de type i |
| TWI835747B (zh) | 2017-09-22 | 2024-03-21 | 賓州大學委員會 | 用於治療黏多醣病 ii 型之基因治療 |
| US20190114858A1 (en) * | 2017-10-16 | 2019-04-18 | Raritan Americas, Inc. | System for controlling access to an equipment rack and intelligent power distribution unit and control unit used therein |
Family Cites Families (9)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2001097829A2 (en) * | 2000-06-19 | 2001-12-27 | Genzyme Corporation | Combination enzyme replacement, gene therapy and small molecule therapy for lysosomal storage diseases |
| US7560425B2 (en) * | 2002-06-07 | 2009-07-14 | Waratah Pharmaceuticals Inc. | Pharmaceutical composition consisting of rapamycine and gastrin 17(LEU15) and a method for treating diabetes |
| EP2052083B1 (en) * | 2006-09-21 | 2014-01-08 | The Scripps Research Institute | Genetically programmed expression of selectively sulfated proteins in eubacteria |
| EP3230438B1 (en) * | 2014-12-12 | 2024-12-04 | University of Copenhagen | N-glycosylation |
| HK1256341A1 (zh) * | 2015-05-15 | 2019-09-20 | 明尼苏达大学董事会 | 用於治疗性递送到中枢神经系统的腺相关物 |
| EP3411488A1 (en) * | 2016-02-03 | 2018-12-12 | The Trustees Of The University Of Pennsylvania | Gene therapy for treating mucopolysaccharidosis type i |
| PL3411484T3 (pl) * | 2016-02-05 | 2024-02-19 | Emory University | Wstrzykiwanie jednoniciowego lub samokomplementarnego wirusa adenosatelitarnego 9 do płynu mózgowego |
| EP3541946A1 (en) * | 2016-11-15 | 2019-09-25 | Regents Of The University Of Minnesota | Method for improving neurological function in mpsi and mpsii and other neurological disorders |
| CA3049915A1 (en) * | 2017-01-31 | 2018-08-09 | Stephen YOO | Treatment of mucopolysaccharidosis i with fully-human glycosylated human alpha-l-iduronidase (idua) |
-
2019
- 2019-07-16 IL IL280198A patent/IL280198B2/en unknown
- 2019-07-17 JP JP2021502545A patent/JP2021531276A/ja active Pending
- 2019-07-17 KR KR1020217004709A patent/KR20210034037A/ko active Pending
- 2019-07-17 EP EP19837268.2A patent/EP3823590A4/en active Pending
- 2019-07-17 WO PCT/US2019/042205 patent/WO2020018665A1/en not_active Ceased
- 2019-07-17 CA CA3106651A patent/CA3106651A1/en active Pending
- 2019-07-17 US US17/260,732 patent/US20210275647A1/en active Pending
- 2019-07-17 BR BR112021000830-6A patent/BR112021000830A2/pt not_active Application Discontinuation
- 2019-07-17 AU AU2019306236A patent/AU2019306236A1/en not_active Abandoned
- 2019-07-17 SG SG11202100423YA patent/SG11202100423YA/en unknown
-
2024
- 2024-03-15 JP JP2024040767A patent/JP2024095680A/ja active Pending
Similar Documents
| Publication | Publication Date | Title |
|---|---|---|
| JP2024095680A5 (https=) | ||
| JP2024112876A5 (https=) | ||
| CN100389820C (zh) | 含肉毒神经毒素的治疗剂 | |
| JP2007314575A (ja) | 治療剤としてのプロサポシンおよびサイトカイン由来ペプチド | |
| JP2005516949A (ja) | Ｇｄｎｆの骨格筋へのアデノ随伴ウイルス媒介性のデリバリー | |
| CA3134523A1 (en) | Compositions useful for treatment of pompe disease | |
| CN111954537A (zh) | 生长分化因子15融合蛋白 | |
| US20240002462A1 (en) | Treatment of neuropathy with igf-1-encoding dna constructs and hgf-encoding dna constructs | |
| JP2020508289A5 (https=) | ||
| JP2021512095A (ja) | 脳損傷を処置するための方法及び材料 | |
| US20240261364A1 (en) | Peptides and methods of using the same | |
| AU2019312301A1 (en) | Treatment of mucopolysaccharidosis IVA | |
| JP2024511024A (ja) | ２１－ヒドロキシラーゼ欠損症の遺伝子治療 | |
| WO2015001352A1 (en) | Novel regenerative therapy | |
| US11510999B2 (en) | Treatment of neuropathy with DNA constructs expressing IGF-1 isoforms | |
| US20210207168A1 (en) | Aav-compatible laminin-linker polymerization proteins | |
| US20210130429A1 (en) | Recombinant adeno-associated virus-mediated expression of fractalkine for treatment of neuroinflammatory and neurodegenerative diseases | |
| KR20230003569A (ko) | Cdkl5 결핍 장애 (cdd)의 치료에 유용한 조성물 | |
| CA3190597A1 (en) | Compositions and methods for the treatment of ocular neuroinflammation | |
| CN119497719A (zh) | Serpin肽衍生物及其使用方法 | |
| WO2024216080A1 (en) | Immunosuppressive regimens and methods thereof | |
| CN118252953A (zh) | 一种用于神经退行性疾病治疗的基因序列构建体及其应用 | |
| CN121909039A (zh) | 分裂内含肽用于治疗scn1a相关疾病的用途 | |
| EA049495B1 (ru) | Гены ube3a и кассеты экспрессии и их использование | |
| HK40063258B (zh) | 腺相关病毒对cln6多核苷酸的递送 |