JP2024540470A5 - - Google Patents

Info

Publication number
JP2024540470A5
JP2024540470A5 JP2024529310A JP2024529310A JP2024540470A5 JP 2024540470 A5 JP2024540470 A5 JP 2024540470A5 JP 2024529310 A JP2024529310 A JP 2024529310A JP 2024529310 A JP2024529310 A JP 2024529310A JP 2024540470 A5 JP2024540470 A5 JP 2024540470A5
Authority
JP
Japan
Prior art keywords
pharmaceutical composition
composition according
drps
scd59
injection
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024529310A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024540470A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/IB2022/061158 external-priority patent/WO2023089564A1/en
Publication of JP2024540470A publication Critical patent/JP2024540470A/ja
Publication of JP2024540470A5 publication Critical patent/JP2024540470A5/ja
Pending legal-status Critical Current

Links

JP2024529310A 2021-11-19 2022-11-18 可溶性ｃｄ５９を発現する遺伝子療法ベクターにより地図状萎縮を治療する方法 Pending JP2024540470A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163281190P 2021-11-19 2021-11-19
US63/281,190 2021-11-19
PCT/IB2022/061158 WO2023089564A1 (en) 2021-11-19 2022-11-18 Method of treating geographic atrophy with a gene therapy vector expressing soluble cd59

Publications (2)

Publication Number Publication Date
JP2024540470A JP2024540470A (ja) 2024-10-31
JP2024540470A5 true JP2024540470A5 (https=) 2025-11-27

Family

ID=84365536

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024529310A Pending JP2024540470A (ja) 2021-11-19 2022-11-18 可溶性ｃｄ５９を発現する遺伝子療法ベクターにより地図状萎縮を治療する方法

Country Status (11)

Country Link
US (1) US20250018063A1 (https=)
EP (1) EP4433496A1 (https=)
JP (1) JP2024540470A (https=)
KR (1) KR20240107156A (https=)
CN (1) CN118369333A (https=)
AU (1) AU2022394125A1 (https=)
CA (1) CA3237907A1 (https=)
IL (1) IL312903A (https=)
JO (1) JOP20240112A1 (https=)
MX (1) MX2024006087A (https=)
WO (1) WO2023089564A1 (https=)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2025074268A1 (en) * 2023-10-02 2025-04-10 Janssen Biotech, Inc. Methods for treating macular degeneration
WO2025083169A1 (en) * 2023-10-17 2025-04-24 Tenpoint Therapeutics Limited Combination of a vegf inhibitor and a complement pathway inhibitor for treating ocular disorders

Family Cites Families (29)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US4405712A (en) 1981-07-01 1983-09-20 The United States Of America As Represented By The Department Of Health And Human Services LTR-Vectors
US4650764A (en) 1983-04-12 1987-03-17 Wisconsin Alumni Research Foundation Helper cell
AU4404785A (en) 1984-05-25 1985-12-31 Dana-Farber Cancer Institute, Inc. Ltr vectors, methods of preparation and use
US4797368A (en) 1985-03-15 1989-01-10 The United States Of America As Represented By The Department Of Health And Human Services Adeno-associated virus as eukaryotic expression vector
US5139941A (en) 1985-10-31 1992-08-18 University Of Florida Research Foundation, Inc. AAV transduction vectors
US4861719A (en) 1986-04-25 1989-08-29 Fred Hutchinson Cancer Research Center DNA constructs for retrovirus packaging cell lines
US4980289A (en) 1987-04-27 1990-12-25 Wisconsin Alumni Research Foundation Promoter deficient retroviral vector
CA1315719C (en) 1988-02-05 1993-04-06 Arthur Bank Retroviral packaging cell lines and processes of using same
US5112767A (en) 1988-03-04 1992-05-12 University Of Southern California Vectors with enhancer domains
US6677311B1 (en) 1988-07-20 2004-01-13 The Salk Institute For Biological Studies Inducible HSV-TK in transformed cell populations
WO1990002806A1 (en) 1988-09-01 1990-03-22 Whitehead Institute For Biomedical Research Recombinant retroviruses with amphotropic and ecotropic host ranges
WO1990002797A1 (en) 1988-09-15 1990-03-22 North Carolina State University Self-inactivating, replication defective, retroviral vectors and helper cells for producing the same
US5124263A (en) 1989-01-12 1992-06-23 Wisconsin Alumni Research Foundation Recombination resistant retroviral helper cell and products produced thereby
WO1990013641A1 (en) 1989-05-10 1990-11-15 Sloan-Kettering Institute For Cancer Research Stably transformed eucaryotic cells comprising a foreign transcribable dna under the control of a pol iii promoter
EP0854193A1 (en) 1990-09-21 1998-07-22 Chiron Corporation Human retroviral packaging cell line
ES2096750T3 (es) 1990-10-31 1997-03-16 Somatix Therapy Corp Vectores retroviricos utiles para la terapia genica.
US5122767A (en) 1991-01-10 1992-06-16 Northern Telecom Limited Saw device tapped delay lines
DE69131908T3 (de) 1991-02-19 2008-04-03 Oxford Biomedica (Uk) Ltd. Viruspartikel mit veraendertem wirtspektrum
AU3434393A (en) 1992-01-17 1993-08-03 Regents Of The University Of Michigan, The Targeted virus
US5627264A (en) 1994-03-03 1997-05-06 Alexion Pharmaceuticals, Inc. Chimeric complement inhibitor proteins
US5998205A (en) 1994-11-28 1999-12-07 Genetic Therapy, Inc. Vectors for tissue-specific replication
US5851826A (en) 1995-07-26 1998-12-22 Children's Medical Center Corporation Helper virus-free herpesvirus vector packaging system
US6689600B1 (en) 1998-11-16 2004-02-10 Introgen Therapeutics, Inc. Formulation of adenovirus for gene therapy
US7109029B2 (en) 2001-02-23 2006-09-19 Cell Genesys, Inc. Vector constructs
US20070196367A1 (en) 2006-02-22 2007-08-23 Valentin Dinu Methods of preventing and treating Alzheimer's disease, age related macular degeneration and other diseases involving extra-cellular debris through the inhibition of the complement system
AU2008295509A1 (en) 2007-08-29 2009-03-12 Tufts University Methods of making and using a cell penetrating peptide for enhanced delivery of nucleic acids, proteins, drugs, and adenovirus to tissues and cells, and compositions and kits
ES2478820T3 (es) 2008-02-15 2014-07-23 Tufts University Tratamiento de degeneración macular
CA2843684A1 (en) 2010-08-13 2012-02-16 Tufts University Compositions, kits and methods for treatment of macular degeneration using soluble membrane-independent cd59 protein
WO2019157447A1 (en) * 2018-02-12 2019-08-15 Trustees Of Tufts College Cd59 for inhibiting inflammasome activation

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