KR20210034037A - 완전-인간 글리코실화된 인간 알파-l-이두로니다아제 (idua)를 사용한 점액다당류증 i의 치료 - Google Patents

완전-인간 글리코실화된 인간 알파-l-이두로니다아제 (idua)를 사용한 점액다당류증 i의 치료 Download PDF

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KR20210034037A
KR20210034037A KR1020217004709A KR20217004709A KR20210034037A KR 20210034037 A KR20210034037 A KR 20210034037A KR 1020217004709 A KR1020217004709 A KR 1020217004709A KR 20217004709 A KR20217004709 A KR 20217004709A KR 20210034037 A KR20210034037 A KR 20210034037A
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human
idua
leu
expression vector
gly
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Korean (ko)
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스테판 유
리키 로버트 라인하르트
큐랜 매튜 심슨
주춘 우
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리젠엑스바이오 인크.
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    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
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    • C12Y302/01076—L-Iduronidase (3.2.1.76)
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    • C12N2750/14011—Parvoviridae
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  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
  • Medicines Containing Material From Animals Or Micro-Organisms (AREA)
  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
KR1020217004709A 2018-07-18 2019-07-17 완전-인간 글리코실화된 인간 알파-l-이두로니다아제 (idua)를 사용한 점액다당류증 i의 치료 Pending KR20210034037A (ko)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201862699923P 2018-07-18 2018-07-18
US62/699,923 2018-07-18
PCT/US2019/042205 WO2020018665A1 (en) 2018-07-18 2019-07-17 Treatment of mucopolysaccharidosis i with fully-human glycosylated human alpha-l-iduronidase (idus)

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KR20210034037A true KR20210034037A (ko) 2021-03-29

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KR1020217004709A Pending KR20210034037A (ko) 2018-07-18 2019-07-17 완전-인간 글리코실화된 인간 알파-l-이두로니다아제 (idua)를 사용한 점액다당류증 i의 치료

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Country Link
US (1) US20210275647A1 (https=)
EP (1) EP3823590A4 (https=)
JP (2) JP2021531276A (https=)
KR (1) KR20210034037A (https=)
AU (1) AU2019306236A1 (https=)
BR (1) BR112021000830A2 (https=)
CA (1) CA3106651A1 (https=)
IL (1) IL280198B2 (https=)
SG (1) SG11202100423YA (https=)
WO (1) WO2020018665A1 (https=)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
MA50016A (fr) 2017-07-06 2020-07-08 Univ Pennsylvania Thérapie génique médiée par aav9 pour traiter la mucopolysaccharidose de type i
TWI835747B (zh) 2017-09-22 2024-03-21 賓州大學委員會 用於治療黏多醣病 ii 型之基因治療
US20190114858A1 (en) * 2017-10-16 2019-04-18 Raritan Americas, Inc. System for controlling access to an equipment rack and intelligent power distribution unit and control unit used therein

Family Cites Families (9)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2001097829A2 (en) * 2000-06-19 2001-12-27 Genzyme Corporation Combination enzyme replacement, gene therapy and small molecule therapy for lysosomal storage diseases
US7560425B2 (en) * 2002-06-07 2009-07-14 Waratah Pharmaceuticals Inc. Pharmaceutical composition consisting of rapamycine and gastrin 17(LEU15) and a method for treating diabetes
EP2052083B1 (en) * 2006-09-21 2014-01-08 The Scripps Research Institute Genetically programmed expression of selectively sulfated proteins in eubacteria
EP3230438B1 (en) * 2014-12-12 2024-12-04 University of Copenhagen N-glycosylation
HK1256341A1 (zh) * 2015-05-15 2019-09-20 明尼苏达大学董事会 用於治疗性递送到中枢神经系统的腺相关物
EP3411488A1 (en) * 2016-02-03 2018-12-12 The Trustees Of The University Of Pennsylvania Gene therapy for treating mucopolysaccharidosis type i
PL3411484T3 (pl) * 2016-02-05 2024-02-19 Emory University Wstrzykiwanie jednoniciowego lub samokomplementarnego wirusa adenosatelitarnego 9 do płynu mózgowego
EP3541946A1 (en) * 2016-11-15 2019-09-25 Regents Of The University Of Minnesota Method for improving neurological function in mpsi and mpsii and other neurological disorders
CA3049915A1 (en) * 2017-01-31 2018-08-09 Stephen YOO Treatment of mucopolysaccharidosis i with fully-human glycosylated human alpha-l-iduronidase (idua)

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Publication number Publication date
IL280198B1 (en) 2025-09-01
AU2019306236A1 (en) 2021-03-11
WO2020018665A1 (en) 2020-01-23
BR112021000830A2 (pt) 2021-04-13
IL280198A (en) 2021-03-01
US20210275647A1 (en) 2021-09-09
JP2024095680A (ja) 2024-07-10
EP3823590A1 (en) 2021-05-26
CA3106651A1 (en) 2020-01-23
EP3823590A4 (en) 2022-04-20
JP2021531276A (ja) 2021-11-18
SG11202100423YA (en) 2021-02-25
IL280198B2 (en) 2026-01-01

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