JP2023543154A5 - - Google Patents

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Publication number
JP2023543154A5
JP2023543154A5 JP2023516514A JP2023516514A JP2023543154A5 JP 2023543154 A5 JP2023543154 A5 JP 2023543154A5 JP 2023516514 A JP2023516514 A JP 2023516514A JP 2023516514 A JP2023516514 A JP 2023516514A JP 2023543154 A5 JP2023543154 A5 JP 2023543154A5
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JP
Japan
Prior art keywords
nucleic acid
acid sequence
mammalian
seq
specific regulatory
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JP2023516514A
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English (en)
Japanese (ja)
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JP7846677B2 (ja
JP2023543154A (ja
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Priority claimed from PCT/US2021/049914 external-priority patent/WO2022056291A1/en
Publication of JP2023543154A publication Critical patent/JP2023543154A/ja
Publication of JP2023543154A5 publication Critical patent/JP2023543154A5/ja
Application granted granted Critical
Publication of JP7846677B2 publication Critical patent/JP7846677B2/ja
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JP2023516514A 2020-09-11 2021-09-10 筋特異的ハイブリッドプロモーター Active JP7846677B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063077339P 2020-09-11 2020-09-11
US63/077,339 2020-09-11
PCT/US2021/049914 WO2022056291A1 (en) 2020-09-11 2021-09-10 Muscle-specific hybrid promoter

Publications (3)

Publication Number Publication Date
JP2023543154A JP2023543154A (ja) 2023-10-13
JP2023543154A5 true JP2023543154A5 (enExample) 2024-09-04
JP7846677B2 JP7846677B2 (ja) 2026-04-15

Family

ID=80629936

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023516514A Active JP7846677B2 (ja) 2020-09-11 2021-09-10 筋特異的ハイブリッドプロモーター

Country Status (6)

Country Link
US (1) US20230346976A1 (enExample)
EP (1) EP4211251A4 (enExample)
JP (1) JP7846677B2 (enExample)
AU (1) AU2021342165A1 (enExample)
CA (1) CA3192120A1 (enExample)
WO (1) WO2022056291A1 (enExample)

Families Citing this family (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JP2026506177A (ja) 2023-02-21 2026-02-20 イリューコン セラピューティクス, インコーポレイテッド 改変インターロイキン2(il2)ポリペプチドをコードするポリヌクレオチド、ならびにその作製方法および使用方法
WO2024211480A2 (en) * 2023-04-05 2024-10-10 Genzyme Corporation Targeted gene therapy for dm-1 myotonic dystrophy
CN121311497A (zh) 2023-04-14 2026-01-09 精密生物科学公司 肌肉特异性表达盒
WO2025157259A1 (en) * 2024-01-25 2025-07-31 Sichuan Real & Best Biotech Co., Ltd. Novel muscle-specific promoters
WO2025235807A1 (en) * 2024-05-10 2025-11-13 Solid Biosciences, Inc. Compositions and methods to improve graft survival

Family Cites Families (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP1390490B1 (en) * 2001-05-24 2009-04-15 Genzyme Corporation Muscle-specific expression vectors
AU2015208247B2 (en) * 2014-01-21 2021-05-27 Universiteit Gent Muscle-specific nucleic acid regulatory elements and methods and use thereof
WO2018178067A1 (en) 2017-03-27 2018-10-04 Vrije Universiteit Brussel Diaphragm-specific nucleic acid regulatory elements and methods and use thereof
AU2020232790A1 (en) 2019-03-06 2021-09-16 Generation Bio Co. Non-active lipid nanoparticles with non-viral, capsid free DNA

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