JP2023526311A5 - - Google Patents
Info
- Publication number
- JP2023526311A5 JP2023526311A5 JP2022569267A JP2022569267A JP2023526311A5 JP 2023526311 A5 JP2023526311 A5 JP 2023526311A5 JP 2022569267 A JP2022569267 A JP 2022569267A JP 2022569267 A JP2022569267 A JP 2022569267A JP 2023526311 A5 JP2023526311 A5 JP 2023526311A5
- Authority
- JP
- Japan
- Prior art keywords
- pharmaceutical composition
- composition according
- patient
- brain mass
- administered
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Applications Claiming Priority (7)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202063023459P | 2020-05-12 | 2020-05-12 | |
| US63/023,459 | 2020-05-12 | ||
| US202063070653P | 2020-08-26 | 2020-08-26 | |
| US63/070,653 | 2020-08-26 | ||
| US202063073756P | 2020-09-02 | 2020-09-02 | |
| US63/073,756 | 2020-09-02 | ||
| PCT/US2021/031802 WO2021231443A1 (en) | 2020-05-12 | 2021-05-11 | Compositions useful in treatment of krabbe disease |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2023526311A JP2023526311A (ja) | 2023-06-21 |
| JP2023526311A5 true JP2023526311A5 (https=) | 2024-05-22 |
| JP7832898B2 JP7832898B2 (ja) | 2026-03-18 |
Family
ID=76284168
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022569267A Active JP7832898B2 (ja) | 2020-05-12 | 2021-05-11 | クラッベ病の治療に有用な組成物 |
Country Status (13)
| Country | Link |
|---|---|
| US (1) | US20230210941A1 (https=) |
| EP (1) | EP4149564A1 (https=) |
| JP (1) | JP7832898B2 (https=) |
| KR (1) | KR20230023637A (https=) |
| CN (1) | CN116057175A (https=) |
| AU (1) | AU2021271635A1 (https=) |
| BR (1) | BR112022021786A2 (https=) |
| CA (1) | CA3177924A1 (https=) |
| CO (1) | CO2022017953A2 (https=) |
| IL (1) | IL298137A (https=) |
| MX (1) | MX2022014245A (https=) |
| TW (1) | TW202208622A (https=) |
| WO (1) | WO2021231443A1 (https=) |
Family Cites Families (24)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US1967872A (en) | 1930-07-14 | 1934-07-24 | Gilbert E Doan | Welding electrode |
| JP2002521107A (ja) | 1998-07-23 | 2002-07-16 | コーニンクレッカ フィリップス エレクトロニクス エヌ ヴィ | 高解像度画像センサを備えたｘ線検査装置 |
| CA2379166C (en) | 1999-08-09 | 2013-03-26 | Targeted Genetics Corporation | Enhancement of expression of a single-stranded, heterologous nucleotide sequence from recombinant viral vectors by designing the sequence such that it forms instrastrand base pairs |
| MX359371B (es) | 2001-11-13 | 2018-09-25 | Univ Pennsylvania | Un metodo para detectar y/o identificar secuencias del virus adeno-asociado y aislamiento de secuencias novedosas identificadas de ese modo. |
| EP2434420A3 (en) | 2003-08-01 | 2012-07-25 | Dna Twopointo Inc. | Systems and methods for biopolymer engineering |
| US8005620B2 (en) | 2003-08-01 | 2011-08-23 | Dna Twopointo Inc. | Systems and methods for biopolymer engineering |
| EP2345731B1 (en) | 2003-09-30 | 2015-10-21 | The Trustees of the University of Pennsylvania | Adeno-associated virus (AAV) clades, sequences, vectors containing same, and uses thereof |
| ES2525067T3 (es) | 2005-04-07 | 2014-12-17 | The Trustees Of The University Of Pennsylvania | Método de incremento de la función de un vector de AAV |
| JP4495210B2 (ja) | 2005-06-09 | 2010-06-30 | パナソニック株式会社 | 振幅誤差補償装置及び直交度誤差補償装置 |
| US7588772B2 (en) | 2006-03-30 | 2009-09-15 | Board Of Trustees Of The Leland Stamford Junior University | AAV capsid library and AAV capsid proteins |
| US8734809B2 (en) | 2009-05-28 | 2014-05-27 | University Of Massachusetts | AAV's and uses thereof |
| WO2011126808A2 (en) | 2010-03-29 | 2011-10-13 | The Trustees Of The University Of Pennsylvania | Pharmacologically induced transgene ablation system |
| US8927514B2 (en) | 2010-04-30 | 2015-01-06 | City Of Hope | Recombinant adeno-associated vectors for targeted treatment |
| US20110318324A1 (en) * | 2010-06-25 | 2011-12-29 | Shire Human Genetic Therapies, Inc. | Methods and compositions for cns delivery of b-galactocerebrosidase |
| FR2977562B1 (fr) | 2011-07-06 | 2016-12-23 | Gaztransport Et Technigaz | Cuve etanche et thermiquement isolante integree dans une structure porteuse |
| WO2015012924A2 (en) * | 2013-04-29 | 2015-01-29 | The Trustees Of The University Of Pennsylvania | Tissue preferential codon modified expression cassettes, vectors containing same, and use thereof |
| AU2015320694B2 (en) | 2014-09-24 | 2021-11-11 | City Of Hope | Adeno-associated virus vector variants for high efficiency genome editing and methods thereof |
| SG11201808426XA (en) | 2016-04-15 | 2018-10-30 | Univ Pennsylvania | Compositions for treatment of wet age-related macular degeneration |
| CN118078860A (zh) | 2017-01-20 | 2024-05-28 | 联邦高等教育系统匹兹堡大学 | 用脐带血移植(ucbt)和增加的半乳糖脑苷酯酶(galc)表达治疗克拉伯病 |
| PT3589730T (pt) | 2017-02-28 | 2024-02-28 | Univ Pennsylvania | Vetor de vírus adenoassociado (aav) de clado f e suas utilizações |
| US20180250496A1 (en) | 2017-03-03 | 2018-09-06 | Cook Medical Technologies Llc | Rapid exchange multiple catheter system |
| BR112020006661A2 (pt) * | 2017-10-03 | 2020-10-13 | Prevail Therapeutics, Inc. | terapias de genes para distúrbios lipossomais |
| EP3860714B1 (en) | 2018-10-03 | 2023-09-06 | Siteone Therapeutics, Inc. | 11,13-modified saxitoxins for the treatment of pain |
| EP3931337A1 (en) * | 2019-02-26 | 2022-01-05 | The Trustees of The University of Pennsylvania | Compositions useful in treatment of krabbe disease |
-
2021
- 2021-05-11 CA CA3177924A patent/CA3177924A1/en active Pending
- 2021-05-11 JP JP2022569267A patent/JP7832898B2/ja active Active
- 2021-05-11 CN CN202180049138.9A patent/CN116057175A/zh active Pending
- 2021-05-11 KR KR1020227042731A patent/KR20230023637A/ko active Pending
- 2021-05-11 TW TW110116911A patent/TW202208622A/zh unknown
- 2021-05-11 BR BR112022021786A patent/BR112022021786A2/pt unknown
- 2021-05-11 AU AU2021271635A patent/AU2021271635A1/en active Pending
- 2021-05-11 WO PCT/US2021/031802 patent/WO2021231443A1/en not_active Ceased
- 2021-05-11 IL IL298137A patent/IL298137A/en unknown
- 2021-05-11 EP EP21730355.1A patent/EP4149564A1/en active Pending
- 2021-05-11 MX MX2022014245A patent/MX2022014245A/es unknown
- 2021-05-11 US US17/998,330 patent/US20230210941A1/en active Pending
-
2022
- 2022-12-12 CO CONC2022/0017953A patent/CO2022017953A2/es unknown
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