JP2022518354A5 - - Google Patents
Info
- Publication number
- JP2022518354A5 JP2022518354A5 JP2021535753A JP2021535753A JP2022518354A5 JP 2022518354 A5 JP2022518354 A5 JP 2022518354A5 JP 2021535753 A JP2021535753 A JP 2021535753A JP 2021535753 A JP2021535753 A JP 2021535753A JP 2022518354 A5 JP2022518354 A5 JP 2022518354A5
- Authority
- JP
- Japan
- Prior art keywords
- suspension
- patient
- regimen
- raav
- dose
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201862782627P | 2018-12-20 | 2018-12-20 | |
| US62/782,627 | 2018-12-20 | ||
| PCT/US2019/067316 WO2020132155A1 (en) | 2018-12-20 | 2019-12-19 | Gene therapy for treating familial hypercholesterolemia |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2022518354A JP2022518354A (ja) | 2022-03-15 |
| JP2022518354A5 true JP2022518354A5 (https=) | 2022-12-23 |
Family
ID=71101865
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021535753A Pending JP2022518354A (ja) | 2018-12-20 | 2019-12-19 | 家族性高コレステロール血症を治療するための遺伝子療法 |
Country Status (9)
| Country | Link |
|---|---|
| US (1) | US20220040332A1 (https=) |
| EP (1) | EP3902918A4 (https=) |
| JP (1) | JP2022518354A (https=) |
| KR (1) | KR20210106489A (https=) |
| CN (1) | CN113710808A (https=) |
| AU (1) | AU2019401638A1 (https=) |
| CA (1) | CA3123844A1 (https=) |
| IL (1) | IL284121A (https=) |
| WO (1) | WO2020132155A1 (https=) |
Families Citing this family (1)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CN117887723A (zh) * | 2024-01-08 | 2024-04-16 | 苏州诺洁贝生物技术有限公司 | 密码子优化的ldlr基因及其应用 |
Family Cites Families (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| HK1224186A1 (zh) * | 2013-11-20 | 2017-08-18 | Cymabay Therapeutics, Inc. | 纯阖家族型高胆固醇血症的治疗 |
| EP3134431B1 (en) * | 2014-04-25 | 2021-04-07 | The Trustees Of The University Of Pennsylvania | Ldlr variants and their use in compositions for reducing cholesterol levels |
| AU2016366560A1 (en) * | 2015-12-11 | 2018-06-28 | The Trustees Of The University Of Pennsylvania | Gene therapy for treating familial hypercholesterolemia |
-
2019
- 2019-12-19 CN CN201980092776.1A patent/CN113710808A/zh active Pending
- 2019-12-19 KR KR1020217022265A patent/KR20210106489A/ko not_active Withdrawn
- 2019-12-19 EP EP19898384.3A patent/EP3902918A4/en not_active Withdrawn
- 2019-12-19 WO PCT/US2019/067316 patent/WO2020132155A1/en not_active Ceased
- 2019-12-19 AU AU2019401638A patent/AU2019401638A1/en not_active Abandoned
- 2019-12-19 US US17/414,263 patent/US20220040332A1/en not_active Abandoned
- 2019-12-19 CA CA3123844A patent/CA3123844A1/en active Pending
- 2019-12-19 JP JP2021535753A patent/JP2022518354A/ja active Pending
-
2021
- 2021-06-17 IL IL284121A patent/IL284121A/en unknown
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