JP2023515466A5 - - Google Patents

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Publication number
JP2023515466A5
JP2023515466A5 JP2022549789A JP2022549789A JP2023515466A5 JP 2023515466 A5 JP2023515466 A5 JP 2023515466A5 JP 2022549789 A JP2022549789 A JP 2022549789A JP 2022549789 A JP2022549789 A JP 2022549789A JP 2023515466 A5 JP2023515466 A5 JP 2023515466A5
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JP
Japan
Prior art keywords
pharmaceutical composition
composition according
eeg
administration
decreased
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2022549789A
Other languages
English (en)
Japanese (ja)
Other versions
JP2023515466A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/018681 external-priority patent/WO2021168183A1/en
Publication of JP2023515466A publication Critical patent/JP2023515466A/ja
Publication of JP2023515466A5 publication Critical patent/JP2023515466A5/ja
Pending legal-status Critical Current

Links

JP2022549789A 2020-02-21 2021-02-19 Httの発現を低下させる方法 Pending JP2023515466A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202062980010P 2020-02-21 2020-02-21
US62/980,010 2020-02-21
PCT/US2021/018681 WO2021168183A1 (en) 2020-02-21 2021-02-19 Methods for reducing htt expression

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2025281702A Division JP2026075094A (ja) 2020-02-21 2025-12-25 Httの発現を低下させる方法

Publications (2)

Publication Number Publication Date
JP2023515466A JP2023515466A (ja) 2023-04-13
JP2023515466A5 true JP2023515466A5 (enExample) 2024-02-28

Family

ID=77391689

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2022549789A Pending JP2023515466A (ja) 2020-02-21 2021-02-19 Httの発現を低下させる方法

Country Status (12)

Country Link
US (1) US20230108340A1 (enExample)
EP (1) EP4107269A4 (enExample)
JP (1) JP2023515466A (enExample)
KR (1) KR20220144837A (enExample)
CN (1) CN115279903A (enExample)
AU (1) AU2021224729A1 (enExample)
BR (1) BR112022016370A2 (enExample)
CA (1) CA3172336A1 (enExample)
IL (1) IL295625A (enExample)
MX (1) MX2022010204A (enExample)
WO (1) WO2021168183A1 (enExample)
ZA (1) ZA202209112B (enExample)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2025265013A2 (en) 2024-06-20 2025-12-26 Arrowhead Pharmaceuticals, Inc. Rnai agents for inhibiting expression of huntingtin (htt), compositions thereof, and methods of use

Family Cites Families (7)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP1991677A2 (en) * 2006-01-26 2008-11-19 Isis Pharmaceuticals, Inc. Compositions and their uses directed to huntingtin
NZ714887A (en) * 2009-09-11 2019-07-26 Ionis Pharmaceuticals Inc Modulation of huntingtin expression
LT3052628T (lt) * 2013-10-04 2020-09-10 Alnylam Pharmaceuticals, Inc. Kompozicijos ir būdai alas1 geno raiškai nuslopinti
EP3797780B1 (en) * 2014-04-17 2022-09-14 Biogen MA Inc. Compositions and methods for modulation of smn2 splicing in a subject
IL320434A (en) * 2015-07-22 2025-06-01 Wave Life Sciences Ltd Oligonucleotide preparations and methods
US11268093B2 (en) * 2017-01-03 2022-03-08 Rula Zain-Luqman Therapeutic method for huntington's disease
CN114286710A (zh) * 2019-06-28 2022-04-05 宾州研究基金会 治疗亨廷顿病的方法和材料

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