JP2023513189A - 筋萎縮性側索硬化症（ａｌｓ）を治療するためのｍｉｒｎａ－４８５阻害剤の使用 - Google Patents

筋萎縮性側索硬化症（ａｌｓ）を治療するためのｍｉｒｎａ－４８５阻害剤の使用 Download PDF

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JP2023513189A
JP2023513189A JP2022547888A JP2022547888A JP2023513189A JP 2023513189 A JP2023513189 A JP 2023513189A JP 2022547888 A JP2022547888 A JP 2022547888A JP 2022547888 A JP2022547888 A JP 2022547888A JP 2023513189 A JP2023513189 A JP 2023513189A
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seq
mir
nucleotides
aspects
protein
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JP2023513189A5 (https=
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ジン－ヒョブ リュ，
ハン ソク コ，
デ フン キム，
ヒュン ス ミン，
ユ ナ リム，
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バイオーケストラ カンパニー， リミテッド
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JP2022547888A 2020-02-07 2021-02-06 筋萎縮性側索硬化症（ａｌｓ）を治療するためのｍｉｒｎａ－４８５阻害剤の使用 Pending JP2023513189A (ja)

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US202062971771P 2020-02-07 2020-02-07
US62/971,771 2020-02-07
US202062989487P 2020-03-13 2020-03-13
US62/989,487 2020-03-13
US202063047147P 2020-07-01 2020-07-01
US63/047,147 2020-07-01
PCT/IB2021/050975 WO2021156832A1 (en) 2020-02-07 2021-02-06 Use of mirna-485 inhibitors for treating amyotrophic lateral sclerosis (als)

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JP2023513189A true JP2023513189A (ja) 2023-03-30
JP2023513189A5 JP2023513189A5 (https=) 2024-02-14

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US (1) US20230131083A1 (https=)
EP (1) EP4100068A4 (https=)
JP (1) JP2023513189A (https=)
KR (1) KR20220154105A (https=)
CN (1) CN115461086A (https=)
AU (1) AU2021215407A1 (https=)
CA (1) CA3166603A1 (https=)
MX (1) MX2022009451A (https=)
WO (1) WO2021156832A1 (https=)

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EP4720313A1 (en) * 2023-05-26 2026-04-08 Shanghai Vitalgen Biopharma Co., Ltd. Recombinant aav vectors for treating proteinopathies in central nervous system

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JP2016523980A (ja) * 2013-07-11 2016-08-12 ザ トラスティーズ オブ コロンビア ユニバーシティ イン ザ シティ オブ ニューヨーク タウ発現を抑制するマイクロｒｎａ
WO2018139819A1 (ko) * 2017-01-26 2018-08-02 주식회사 바이오오케스트라 마이크로 rna를 이용한 뇌 질환 예방 또는 치료 용도

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WO2016030899A1 (en) * 2014-08-28 2016-03-03 Yeda Research And Development Co. Ltd. Methods of treating amyotrophic lateral scleroses
DE102016103562A1 (de) * 2015-09-17 2017-03-23 Topos Nomos Ltd. Pharmazeutische Wirkstoffe zur Verwendung in der Behandlung von Amyotropher Lateralsklerose (ALS) und Diagnoseverfahren
DK3378482T5 (da) * 2015-11-19 2024-09-30 Univ Nagoya City Public Univ Corp Formulering til administration af antitumorlægemiddel
WO2018139759A1 (ko) * 2017-01-26 2018-08-02 주식회사 바이오오케스트라 마이크로 rna를 이용한 알츠하이머병 진단방법
JPWO2019240223A1 (ja) * 2018-06-13 2021-07-01 公益財団法人川崎市産業振興財団 数平均分子量が３ｋＤａ〜１０ｋＤａであるＰＥＧブロックとカチオン性ポリマーとのブロックコポリマーと、アンチセンスオリゴヌクレオチドとを含む、ポリイオンコンプレックスミセル
US10844380B1 (en) * 2019-06-17 2020-11-24 Biorchestra Co., Ltd. Uses for prevention or treatment of brain diseases using microrna

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JP2016523980A (ja) * 2013-07-11 2016-08-12 ザ トラスティーズ オブ コロンビア ユニバーシティ イン ザ シティ オブ ニューヨーク タウ発現を抑制するマイクロｒｎａ
WO2018139819A1 (ko) * 2017-01-26 2018-08-02 주식회사 바이오오케스트라 마이크로 rna를 이용한 뇌 질환 예방 또는 치료 용도

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WO2021156832A1 (en) 2021-08-12
US20230131083A1 (en) 2023-04-27
AU2021215407A1 (en) 2022-08-25
CN115461086A (zh) 2022-12-09
EP4100068A4 (en) 2024-03-20
EP4100068A1 (en) 2022-12-14
MX2022009451A (es) 2022-10-31
CA3166603A1 (en) 2021-08-12
KR20220154105A (ko) 2022-11-21

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