JP2023504195A5 - - Google Patents

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Publication number
JP2023504195A5
JP2023504195A5 JP2022534221A JP2022534221A JP2023504195A5 JP 2023504195 A5 JP2023504195 A5 JP 2023504195A5 JP 2022534221 A JP2022534221 A JP 2022534221A JP 2022534221 A JP2022534221 A JP 2022534221A JP 2023504195 A5 JP2023504195 A5 JP 2023504195A5
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JP
Japan
Prior art keywords
pharmaceutical composition
composition according
aso
aspects
administered
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2022534221A
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English (en)
Japanese (ja)
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JP2023504195A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2020/063157 external-priority patent/WO2021113541A1/en
Publication of JP2023504195A publication Critical patent/JP2023504195A/ja
Publication of JP2023504195A5 publication Critical patent/JP2023504195A5/ja
Priority to JP2025264280A priority Critical patent/JP2026048892A/ja
Pending legal-status Critical Current

Links

JP2022534221A 2019-12-06 2020-12-03 状態および疾患の処置のためのアンチセンスオリゴマー Pending JP2023504195A (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2025264280A JP2026048892A (ja) 2019-12-06 2025-12-18 状態および疾患の処置のためのアンチセンスオリゴマー

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201962945048P 2019-12-06 2019-12-06
US62/945,048 2019-12-06
US202062993971P 2020-03-24 2020-03-24
US62/993,971 2020-03-24
PCT/US2020/063157 WO2021113541A1 (en) 2019-12-06 2020-12-03 Antisense oligomers for treatment of conditions and diseases

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2025264280A Division JP2026048892A (ja) 2019-12-06 2025-12-18 状態および疾患の処置のためのアンチセンスオリゴマー

Publications (2)

Publication Number Publication Date
JP2023504195A JP2023504195A (ja) 2023-02-01
JP2023504195A5 true JP2023504195A5 (https=) 2023-12-07

Family

ID=76222665

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2022534221A Pending JP2023504195A (ja) 2019-12-06 2020-12-03 状態および疾患の処置のためのアンチセンスオリゴマー
JP2025264280A Pending JP2026048892A (ja) 2019-12-06 2025-12-18 状態および疾患の処置のためのアンチセンスオリゴマー

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2025264280A Pending JP2026048892A (ja) 2019-12-06 2025-12-18 状態および疾患の処置のためのアンチセンスオリゴマー

Country Status (11)

Country Link
US (1) US20230116704A1 (https=)
EP (1) EP4069256A4 (https=)
JP (2) JP2023504195A (https=)
KR (1) KR20220113743A (https=)
CN (1) CN115087452A (https=)
AU (1) AU2020395835A1 (https=)
BR (1) BR112022010882A2 (https=)
CA (1) CA3159162A1 (https=)
IL (1) IL293531A (https=)
MX (1) MX2022006858A (https=)
WO (1) WO2021113541A1 (https=)

Families Citing this family (10)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
AU2020227825B2 (en) 2019-02-27 2026-03-26 Stoke Therapeutics, Inc. Antisense oligomers for treatment of conditions and diseases
EP4110919A4 (en) * 2020-02-28 2024-06-05 Ionis Pharmaceuticals, Inc. COMPOUNDS AND METHODS FOR MODULATING SCN1A EXPRESSION
CN115867657A (zh) 2020-05-11 2023-03-28 斯托克制药公司 用于治疗疾患和疾病的opa1反义寡聚物
JP2024534157A (ja) * 2021-08-27 2024-09-18 アイオーニス ファーマシューティカルズ, インコーポレーテッド Scn1a発現を調節するための化合物及び方法
KR20250087733A (ko) * 2022-07-29 2025-06-16 스톡 테라퓨틱스, 인크. 병태 및 질환의 치료를 위한 화합물
AU2023321711A1 (en) * 2022-08-11 2025-02-20 Wave Life Sciences Ltd. Oligonucleotide compositions and methods thereof
CN121194802A (zh) * 2023-02-14 2025-12-23 斯托克制药公司 反义寡聚物调配物
MX2025013084A (es) * 2023-05-03 2026-02-03 Stoke Therapeutics Inc Compuestos y métodos para tratar sujetos humanos
WO2026036032A1 (en) * 2024-08-09 2026-02-12 Amylyx Pharmaceuticals, Inc. Formulations containing antisense oligonucleotides targeting calpain-2
WO2026052819A1 (en) * 2024-09-06 2026-03-12 Ospedale San Raffaele S.R.L. Gene therapy

Family Cites Families (7)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6503756B1 (en) * 2000-09-22 2003-01-07 Isis Pharmaceuticals, Inc. Antisense modulation of syntaxin 4 interacting protein expression
CN109112126B (zh) * 2010-06-23 2024-06-14 库尔纳公司 通过抑制电压门控钠通道α亚基(SCNA)的天然反义转录物而治疗SCNA相关疾病
WO2017106377A1 (en) * 2015-12-14 2017-06-22 Cold Spring Harbor Laboratory Antisense oligomers for treatment of autosomal dominant mental retardation-5 and dravet syndrome
KR102318434B1 (ko) * 2017-08-25 2021-11-01 스톡 테라퓨틱스, 인크. 병태 및 질환 치료용 안티센스 올리고머
HUE070436T2 (hu) * 2017-10-23 2025-06-28 Stoke Therapeutics Inc Antiszensz oligomerek nonszensz-mediált RNS-lebomláson alapuló állapotok és betegségek kezelésére
WO2019224864A1 (ja) * 2018-05-21 2019-11-28 国立研究開発法人理化学研究所 Scn1a遺伝子の発現増強法とそれによるドラベ症候群の治療法
AU2020227825B2 (en) * 2019-02-27 2026-03-26 Stoke Therapeutics, Inc. Antisense oligomers for treatment of conditions and diseases

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