JP2022553307A5 - - Google Patents
Info
- Publication number
- JP2022553307A5 JP2022553307A5 JP2022523408A JP2022523408A JP2022553307A5 JP 2022553307 A5 JP2022553307 A5 JP 2022553307A5 JP 2022523408 A JP2022523408 A JP 2022523408A JP 2022523408 A JP2022523408 A JP 2022523408A JP 2022553307 A5 JP2022553307 A5 JP 2022553307A5
- Authority
- JP
- Japan
- Prior art keywords
- aav
- seq
- functionally linked
- nucleic acid
- polynucleotide
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962924340P | 2019-10-22 | 2019-10-22 | |
| US62/924,340 | 2019-10-22 | ||
| PCT/US2020/056860 WO2021081201A1 (en) | 2019-10-22 | 2020-10-22 | Adeno-associated virus (aav) systems for treatment of progranulin associated neurodegeneative diseases or disorders |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2022553307A JP2022553307A (ja) | 2022-12-22 |
| JP2022553307A5 true JP2022553307A5 (enExample) | 2023-10-30 |
Family
ID=75620215
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022523408A Pending JP2022553307A (ja) | 2019-10-22 | 2020-10-22 | プログラニュリン関連神経変性疾患または障害の治療のためのアデノ随伴ウイルス（ａａｖ）システム |
Country Status (10)
| Country | Link |
|---|---|
| US (2) | US20210147872A1 (enExample) |
| EP (1) | EP4048799A4 (enExample) |
| JP (1) | JP2022553307A (enExample) |
| KR (1) | KR20230019402A (enExample) |
| CN (1) | CN115715327A (enExample) |
| AU (1) | AU2020371662A1 (enExample) |
| CA (1) | CA3158516A1 (enExample) |
| IL (1) | IL292382A (enExample) |
| MX (1) | MX2022004812A (enExample) |
| WO (1) | WO2021081201A1 (enExample) |
Families Citing this family (7)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| BR112021001878A2 (pt) * | 2018-07-31 | 2021-04-27 | Cornell University | métodos de terapia genética para o controle da função do órgão |
| WO2022119890A1 (en) * | 2020-12-01 | 2022-06-09 | The Trustees Of The University Of Pennsylvania | Compositions and uses thereof for treatment of angelman syndrome |
| JPWO2022131322A1 (enExample) * | 2020-12-17 | 2022-06-23 | ||
| CN119343455A (zh) * | 2022-01-31 | 2025-01-21 | 特拉梅斯生物股份有限公司 | 用于治疗癫痫和神经性疼痛的表达盒 |
| WO2024035649A1 (en) * | 2022-08-08 | 2024-02-15 | Shape Therapeutics Inc. | Compositions for progranulin expression and methods of use thereof |
| AU2023378899A1 (en) * | 2022-11-13 | 2025-06-26 | Alexion Pharma International Operations Limited | Gene therapy for frontotemporal dementia |
| WO2025251041A1 (en) * | 2024-05-31 | 2025-12-04 | Bluerock Therapeutics Lp | METHODS AND COMPOSITIONS FOR TREATING PROGRANULIN DEFICIENCIES USING iPSC-DERIVED CELLS |
Family Cites Families (10)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2009089635A1 (en) * | 2008-01-16 | 2009-07-23 | Neurodyn, Inc. | Treating neurodegenerative diseases with progranulin (pgrn) |
| SI3988660T1 (sl) * | 2009-05-02 | 2025-09-30 | Genzyme Corporation | Genska terapija za nevrodegenerativne motnje |
| WO2013151664A1 (en) * | 2012-04-02 | 2013-10-10 | modeRNA Therapeutics | Modified polynucleotides for the production of proteins |
| WO2016125330A1 (ja) * | 2015-02-02 | 2016-08-11 | 原 英彰 | 網膜再生促進薬 |
| CA3016314A1 (en) * | 2016-03-02 | 2017-09-08 | Julianne REIDERS | Therapy for frontotemporal dementia |
| US20190388508A1 (en) * | 2017-01-19 | 2019-12-26 | New York University | Progranulin and progranulin derivatives in treating impaired fracture healing |
| EP3692158A4 (en) * | 2017-10-03 | 2021-08-04 | Prevail Therapeutics, Inc. | GENE THERAPIES FOR LYSOSOMAL DISEASES |
| CN111542549A (zh) * | 2017-10-03 | 2020-08-14 | 普利维尔治疗公司 | 用于溶酶体障碍的基因疗法 |
| EP3917539A4 (en) * | 2019-02-01 | 2022-11-23 | Avrobio, Inc. | COMPOSITIONS AND METHODS FOR THE TREATMENT OF NEUROCOGNITIVE DISORDERS |
| MX2021010134A (es) * | 2019-02-22 | 2021-09-23 | Univ Pennsylvania | Virus adenoasociado recombinante para el tratamiento de la neurodegeneracion de inicio en adultos asociada a grn. |
-
2020
- 2020-10-22 IL IL292382A patent/IL292382A/en unknown
- 2020-10-22 WO PCT/US2020/056860 patent/WO2021081201A1/en not_active Ceased
- 2020-10-22 JP JP2022523408A patent/JP2022553307A/ja active Pending
- 2020-10-22 AU AU2020371662A patent/AU2020371662A1/en not_active Abandoned
- 2020-10-22 EP EP20880235.5A patent/EP4048799A4/en active Pending
- 2020-10-22 CA CA3158516A patent/CA3158516A1/en active Pending
- 2020-10-22 CN CN202080089386.1A patent/CN115715327A/zh active Pending
- 2020-10-22 MX MX2022004812A patent/MX2022004812A/es unknown
- 2020-10-22 KR KR1020227017064A patent/KR20230019402A/ko not_active Ceased
- 2020-10-22 US US17/077,680 patent/US20210147872A1/en not_active Abandoned
-
2023
- 2023-09-26 US US18/372,868 patent/US20240318199A1/en not_active Abandoned