JP2022549834A5 - - Google Patents

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Publication number
JP2022549834A5
JP2022549834A5 JP2022518780A JP2022518780A JP2022549834A5 JP 2022549834 A5 JP2022549834 A5 JP 2022549834A5 JP 2022518780 A JP2022518780 A JP 2022518780A JP 2022518780 A JP2022518780 A JP 2022518780A JP 2022549834 A5 JP2022549834 A5 JP 2022549834A5
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JP
Japan
Prior art keywords
pharmaceutical composition
composition according
subject
pharmaceutically acceptable
acceptable salt
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Granted
Application number
JP2022518780A
Other languages
English (en)
Japanese (ja)
Other versions
JP2022549834A (ja
JP7661315B2 (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2020/052871 external-priority patent/WO2021062264A1/en
Publication of JP2022549834A publication Critical patent/JP2022549834A/ja
Publication of JP2022549834A5 publication Critical patent/JP2022549834A5/ja
Priority to JP2025061214A priority Critical patent/JP2025111476A/ja
Application granted granted Critical
Publication of JP7661315B2 publication Critical patent/JP7661315B2/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

Links

JP2022518780A 2019-09-25 2020-09-25 高フェニルアラニン血症の治療方法 Active JP7661315B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2025061214A JP2025111476A (ja) 2019-09-25 2025-04-02 高フェニルアラニン血症の治療方法

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201962905720P 2019-09-25 2019-09-25
US62/905,720 2019-09-25
PCT/US2020/052871 WO2021062264A1 (en) 2019-09-25 2020-09-25 Methods for treating hyperphenylalaninemia

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2025061214A Division JP2025111476A (ja) 2019-09-25 2025-04-02 高フェニルアラニン血症の治療方法

Publications (3)

Publication Number Publication Date
JP2022549834A JP2022549834A (ja) 2022-11-29
JP2022549834A5 true JP2022549834A5 (https=) 2023-10-02
JP7661315B2 JP7661315B2 (ja) 2025-04-14

Family

ID=72827023

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2022518780A Active JP7661315B2 (ja) 2019-09-25 2020-09-25 高フェニルアラニン血症の治療方法
JP2025061214A Pending JP2025111476A (ja) 2019-09-25 2025-04-02 高フェニルアラニン血症の治療方法

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2025061214A Pending JP2025111476A (ja) 2019-09-25 2025-04-02 高フェニルアラニン血症の治療方法

Country Status (22)

Country Link
US (1) US20220362249A1 (https=)
EP (1) EP4034122B1 (https=)
JP (2) JP7661315B2 (https=)
KR (1) KR20220070477A (https=)
CN (1) CN114650825A (https=)
BR (1) BR112022003719A2 (https=)
CA (1) CA3150003A1 (https=)
DK (1) DK4034122T3 (https=)
ES (1) ES3041002T3 (https=)
FI (1) FI4034122T3 (https=)
HR (1) HRP20251268T1 (https=)
HU (1) HUE073483T2 (https=)
IL (1) IL291565B1 (https=)
JO (1) JOP20220042A1 (https=)
LT (1) LT4034122T (https=)
MX (1) MX2022003585A (https=)
PL (1) PL4034122T3 (https=)
PT (1) PT4034122T (https=)
RS (1) RS67295B1 (https=)
SI (1) SI4034122T1 (https=)
SM (1) SMT202500493T1 (https=)
WO (1) WO2021062264A1 (https=)

Families Citing this family (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
MA46973A (fr) 2016-11-29 2019-10-09 Censa Pharmaceuticals Inc Polymorphes de sépiaptérine et leurs sels
MA46972A (fr) 2016-11-29 2019-10-09 Censa Pharmaceuticals Inc Forme polymorphe de sépiaptérine
JP7811085B2 (ja) 2017-09-01 2026-02-04 ピーティーシー セラピューティクス エムピー,インコーポレイテッド セピアプテリンを含む医薬組成物及びその使用
FI3801536T3 (fi) 2018-05-30 2024-08-29 Ptc Therapeutics Mp Inc Sepiapteriinin antaminen ilman ruokaa käytettäväksi menetelmässä sepiapteriinin plasma-altistuksen lisäämiseksi
EP3801534B1 (en) * 2018-05-30 2026-02-18 PTC Therapeutics MP, Inc. Treatment of phenylketonuria with sepiapterin

Family Cites Families (8)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US5910304A (en) 1982-12-13 1999-06-08 Texas A&M University System Low-dose oral administration of interferons
CA1320905C (en) 1986-11-06 1993-08-03 Joseph M. Cummins Treatment of immuno-resistant disease
US6036949A (en) 1998-03-05 2000-03-14 Amarillo Biosciences, Inc. Treatment of fibromyalgia with low doses of interferon
ES2586945T3 (es) * 2014-03-31 2016-10-19 Vasopharm Gmbh Composiciones farmacéuticas sólidas que comprenden derivados de biopterina y usos de dichas composiciones
MA46973A (fr) 2016-11-29 2019-10-09 Censa Pharmaceuticals Inc Polymorphes de sépiaptérine et leurs sels
MA46972A (fr) 2016-11-29 2019-10-09 Censa Pharmaceuticals Inc Forme polymorphe de sépiaptérine
JP7811085B2 (ja) * 2017-09-01 2026-02-04 ピーティーシー セラピューティクス エムピー,インコーポレイテッド セピアプテリンを含む医薬組成物及びその使用
AU2019277372B2 (en) 2018-05-30 2024-12-19 Ptc Therapeutics Mp, Inc. Pharmaceutically acceptable salts of sepiapterin

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