HRP20251268T1 - Postupci za liječenje hiperfenilalaninemije - Google Patents

Postupci za liječenje hiperfenilalaninemije

Info

Publication number
HRP20251268T1
HRP20251268T1 HRP20251268TT HRP20251268T HRP20251268T1 HR P20251268 T1 HRP20251268 T1 HR P20251268T1 HR P20251268T T HRP20251268T T HR P20251268TT HR P20251268 T HRP20251268 T HR P20251268T HR P20251268 T1 HRP20251268 T1 HR P20251268T1
Authority
HR
Croatia
Prior art keywords
sepiapterin
individual
pharmaceutically acceptable
salt
acceptable salt
Prior art date
Application number
HRP20251268TT
Other languages
English (en)
Croatian (hr)
Inventor
Niel SMITH
Original Assignee
Ptc Therapeutics Mp, Inc.
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Ptc Therapeutics Mp, Inc. filed Critical Ptc Therapeutics Mp, Inc.
Publication of HRP20251268T1 publication Critical patent/HRP20251268T1/hr

Links

Classifications

    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K31/00Medicinal preparations containing organic active ingredients
    • A61K31/33Heterocyclic compounds
    • A61K31/395Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins
    • A61K31/495Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having six-membered rings with two or more nitrogen atoms as the only ring heteroatoms, e.g. piperazine or tetrazines
    • A61K31/505Pyrimidines; Hydrogenated pyrimidines, e.g. trimethoprim
    • A61K31/519Pyrimidines; Hydrogenated pyrimidines, e.g. trimethoprim ortho- or peri-condensed with heterocyclic rings
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P3/00Drugs for disorders of the metabolism
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K9/00Medicinal preparations characterised by special physical form
    • A61K9/0087Galenical forms not covered by A61K9/02 - A61K9/7023
    • A61K9/0095Drinks; Beverages; Syrups; Compositions for reconstitution thereof, e.g. powders or tablets to be dispersed in a glass of water; Veterinary drenches

Landscapes

  • Health & Medical Sciences (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Veterinary Medicine (AREA)
  • Public Health (AREA)
  • General Health & Medical Sciences (AREA)
  • Chemical & Material Sciences (AREA)
  • Animal Behavior & Ethology (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • Medicinal Chemistry (AREA)
  • Epidemiology (AREA)
  • Obesity (AREA)
  • Organic Chemistry (AREA)
  • Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
  • General Chemical & Material Sciences (AREA)
  • Chemical Kinetics & Catalysis (AREA)
  • Hematology (AREA)
  • Diabetes (AREA)
  • Bioinformatics & Cheminformatics (AREA)
  • Engineering & Computer Science (AREA)
  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
  • Acyclic And Carbocyclic Compounds In Medicinal Compositions (AREA)
  • Medicinal Preparation (AREA)
HRP20251268TT 2019-09-25 2020-09-25 Postupci za liječenje hiperfenilalaninemije HRP20251268T1 (hr)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201962905720P 2019-09-25 2019-09-25
EP20789788.5A EP4034122B1 (en) 2019-09-25 2020-09-25 Methods for treating hyperphenylalaninemia
PCT/US2020/052871 WO2021062264A1 (en) 2019-09-25 2020-09-25 Methods for treating hyperphenylalaninemia

Publications (1)

Publication Number Publication Date
HRP20251268T1 true HRP20251268T1 (hr) 2025-12-05

Family

ID=72827023

Family Applications (1)

Application Number Title Priority Date Filing Date
HRP20251268TT HRP20251268T1 (hr) 2019-09-25 2020-09-25 Postupci za liječenje hiperfenilalaninemije

Country Status (22)

Country Link
US (1) US20220362249A1 (https=)
EP (1) EP4034122B1 (https=)
JP (2) JP7661315B2 (https=)
KR (1) KR20220070477A (https=)
CN (1) CN114650825A (https=)
BR (1) BR112022003719A2 (https=)
CA (1) CA3150003A1 (https=)
DK (1) DK4034122T3 (https=)
ES (1) ES3041002T3 (https=)
FI (1) FI4034122T3 (https=)
HR (1) HRP20251268T1 (https=)
HU (1) HUE073483T2 (https=)
IL (1) IL291565B1 (https=)
JO (1) JOP20220042A1 (https=)
LT (1) LT4034122T (https=)
MX (1) MX2022003585A (https=)
PL (1) PL4034122T3 (https=)
PT (1) PT4034122T (https=)
RS (1) RS67295B1 (https=)
SI (1) SI4034122T1 (https=)
SM (1) SMT202500493T1 (https=)
WO (1) WO2021062264A1 (https=)

Families Citing this family (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
MA46973A (fr) 2016-11-29 2019-10-09 Censa Pharmaceuticals Inc Polymorphes de sépiaptérine et leurs sels
MA46972A (fr) 2016-11-29 2019-10-09 Censa Pharmaceuticals Inc Forme polymorphe de sépiaptérine
JP7811085B2 (ja) 2017-09-01 2026-02-04 ピーティーシー セラピューティクス エムピー,インコーポレイテッド セピアプテリンを含む医薬組成物及びその使用
FI3801536T3 (fi) 2018-05-30 2024-08-29 Ptc Therapeutics Mp Inc Sepiapteriinin antaminen ilman ruokaa käytettäväksi menetelmässä sepiapteriinin plasma-altistuksen lisäämiseksi
EP3801534B1 (en) * 2018-05-30 2026-02-18 PTC Therapeutics MP, Inc. Treatment of phenylketonuria with sepiapterin

Family Cites Families (8)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US5910304A (en) 1982-12-13 1999-06-08 Texas A&M University System Low-dose oral administration of interferons
CA1320905C (en) 1986-11-06 1993-08-03 Joseph M. Cummins Treatment of immuno-resistant disease
US6036949A (en) 1998-03-05 2000-03-14 Amarillo Biosciences, Inc. Treatment of fibromyalgia with low doses of interferon
ES2586945T3 (es) * 2014-03-31 2016-10-19 Vasopharm Gmbh Composiciones farmacéuticas sólidas que comprenden derivados de biopterina y usos de dichas composiciones
MA46973A (fr) 2016-11-29 2019-10-09 Censa Pharmaceuticals Inc Polymorphes de sépiaptérine et leurs sels
MA46972A (fr) 2016-11-29 2019-10-09 Censa Pharmaceuticals Inc Forme polymorphe de sépiaptérine
JP7811085B2 (ja) * 2017-09-01 2026-02-04 ピーティーシー セラピューティクス エムピー,インコーポレイテッド セピアプテリンを含む医薬組成物及びその使用
AU2019277372B2 (en) 2018-05-30 2024-12-19 Ptc Therapeutics Mp, Inc. Pharmaceutically acceptable salts of sepiapterin

Also Published As

Publication number Publication date
SMT202500493T1 (it) 2026-01-12
SI4034122T1 (sl) 2025-12-31
IL291565B1 (en) 2026-04-01
AU2020353676A1 (en) 2022-04-14
HUE073483T2 (hu) 2026-01-28
FI4034122T3 (fi) 2025-10-08
IL291565A (en) 2022-05-01
CA3150003A1 (en) 2021-04-01
DK4034122T3 (da) 2025-09-15
LT4034122T (lt) 2025-11-10
JP2025111476A (ja) 2025-07-30
JP2022549834A (ja) 2022-11-29
JOP20220042A1 (ar) 2023-01-30
PT4034122T (pt) 2025-09-18
WO2021062264A1 (en) 2021-04-01
MX2022003585A (es) 2022-04-19
CN114650825A (zh) 2022-06-21
EP4034122A1 (en) 2022-08-03
ES3041002T3 (en) 2025-11-06
JP7661315B2 (ja) 2025-04-14
US20220362249A1 (en) 2022-11-17
EP4034122B1 (en) 2025-08-13
RS67295B1 (sr) 2025-11-28
BR112022003719A2 (pt) 2022-05-31
KR20220070477A (ko) 2022-05-31
PL4034122T3 (pl) 2026-01-26

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