JP2022534086A5 - - Google Patents

Info

Publication number
JP2022534086A5
JP2022534086A5 JP2021569934A JP2021569934A JP2022534086A5 JP 2022534086 A5 JP2022534086 A5 JP 2022534086A5 JP 2021569934 A JP2021569934 A JP 2021569934A JP 2021569934 A JP2021569934 A JP 2021569934A JP 2022534086 A5 JP2022534086 A5 JP 2022534086A5
Authority
JP
Japan
Prior art keywords
cnot3
expression
composition according
antisense oligomer
oligomer
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Granted
Application number
JP2021569934A
Other languages
English (en)
Japanese (ja)
Other versions
JP7652713B2 (ja
JP2022534086A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/AU2020/050516 external-priority patent/WO2020237294A1/en
Publication of JP2022534086A publication Critical patent/JP2022534086A/ja
Publication of JP2022534086A5 publication Critical patent/JP2022534086A5/ja
Priority to JP2025041378A priority Critical patent/JP2025085741A/ja
Application granted granted Critical
Publication of JP7652713B2 publication Critical patent/JP7652713B2/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

Links

JP2021569934A 2019-05-27 2020-05-25 新規の網膜色素変性処置 Active JP7652713B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2025041378A JP2025085741A (ja) 2019-05-27 2025-03-14 新規の網膜色素変性処置

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
AU2019901804A AU2019901804A0 (en) 2019-05-27 Novel Retinitis Pigmentosa Treatment
AU2019901804 2019-05-27
AU2019903812A AU2019903812A0 (en) 2019-10-10 Novel Retinitis Pigmentosa Treatment
AU2019903812 2019-10-10
PCT/AU2020/050516 WO2020237294A1 (en) 2019-05-27 2020-05-25 Novel retinitis pigmentosa treatment

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2025041378A Division JP2025085741A (ja) 2019-05-27 2025-03-14 新規の網膜色素変性処置

Publications (3)

Publication Number Publication Date
JP2022534086A JP2022534086A (ja) 2022-07-27
JP2022534086A5 true JP2022534086A5 (enExample) 2023-06-01
JP7652713B2 JP7652713B2 (ja) 2025-03-27

Family

ID=73553023

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2021569934A Active JP7652713B2 (ja) 2019-05-27 2020-05-25 新規の網膜色素変性処置
JP2025041378A Pending JP2025085741A (ja) 2019-05-27 2025-03-14 新規の網膜色素変性処置

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2025041378A Pending JP2025085741A (ja) 2019-05-27 2025-03-14 新規の網膜色素変性処置

Country Status (11)

Country Link
US (2) US12559747B2 (enExample)
EP (1) EP3976789A4 (enExample)
JP (2) JP7652713B2 (enExample)
KR (1) KR20220012276A (enExample)
CN (1) CN113891940B (enExample)
AU (1) AU2020285470B2 (enExample)
BR (1) BR112021023936A2 (enExample)
CA (1) CA3141633A1 (enExample)
IL (1) IL288442A (enExample)
SG (1) SG11202112946VA (enExample)
WO (1) WO2020237294A1 (enExample)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN115867657A (zh) 2020-05-11 2023-03-28 斯托克制药公司 用于治疗疾患和疾病的opa1反义寡聚物
WO2025043278A1 (en) * 2023-08-25 2025-03-06 PYC Therapeutics Limited Gene-mediated conditions

Family Cites Families (14)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US4458066A (en) 1980-02-29 1984-07-03 University Patents, Inc. Process for preparing polynucleotides
US5149797A (en) 1990-02-15 1992-09-22 The Worcester Foundation For Experimental Biology Method of site-specific alteration of rna and production of encoded polypeptides
US20020123476A1 (en) 1991-03-19 2002-09-05 Emanuele R. Martin Therapeutic delivery compositions and methods of use thereof
RU2034835C1 (ru) 1992-03-09 1995-05-10 Научно-исследовательский и проектный институт мономеров с опытным заводом СПОСОБ ПОЛУЧЕНИЯ β -КАРОТИНА
WO1997022371A1 (en) 1995-12-18 1997-06-26 Collagen Corporation Crosslinked polymer compositions and methods for their use
US6821724B1 (en) * 1998-09-17 2004-11-23 Affymetrix, Inc. Methods of genetic analysis using nucleic acid arrays
US6287860B1 (en) 2000-01-20 2001-09-11 Isis Pharmaceuticals, Inc. Antisense inhibition of MEKK2 expression
US6965025B2 (en) 2001-12-10 2005-11-15 Isis Pharmaceuticals, Inc. Antisense modulation of connective tissue growth factor expression
US20100016215A1 (en) 2007-06-29 2010-01-21 Avi Biopharma, Inc. Compound and method for treating myotonic dystrophy
EP2655621B1 (en) 2010-12-20 2018-05-23 The General Hospital Corporation Polycomb-associated non-coding rnas
WO2018204764A1 (en) * 2017-05-05 2018-11-08 Camp4 Therapeutics Corporation Identification and targeted modulation of gene signaling networks
EP4017979A4 (en) * 2019-08-19 2024-03-27 Stoke Therapeutics, Inc. COMPOSITIONS AND METHODS FOR MODULATING PROTEIN SPLICING AND EXPRESSION
EP4161658A4 (en) * 2020-06-01 2024-10-02 Dana-Farber Cancer Institute, Inc. Methods for modulating mhc-i expression and immunotherapy uses thereof
CN113584038B (zh) * 2021-09-09 2023-11-14 深圳雅济科技有限公司 一种治疗视网膜疾病的反义寡核苷酸组合及其应用

Similar Documents

Publication Publication Date Title
AU2021290279B2 (en) Reducing intron retention
CN111936163B (zh) 用于治疗基于无义介导的rna衰变的病况和疾病的反义寡聚体
US6727355B2 (en) Pharmaceutical composition for treatment of Duchenne muscular dystrophy
JP2020189874A (ja) 状態および疾患の処置のためのアンチセンスオリゴマー
US6365345B1 (en) Antisense nucleic acids for the prevention and treatment of disorders in which expression of c-erbB plays a role
JP2022106803A (ja) アラジール症候群の処置のためのアンチセンスオリゴマー
JP7054675B2 (ja) 網膜色素変性症18と網膜色素変性症13の処置のための組成物と方法
JPH11513889A (ja) タンパク質翻訳のアンチセンス阻害のための組成物および方法
TWI837102B (zh) 用於反義遞送之細胞穿透肽
EP1951263A1 (en) Multitargeting interfering rnas having two active strands and methods for their design and use
JP2019500346A (ja) 腎臓病の処置のための組成物と方法
JPH09503391A (ja) 多薬剤耐性関連タンパク質のオリゴヌクレオチド調整
JP2022533358A5 (enExample)
TW202019442A (zh) 用於反義遞送之三聚合肽
JP2022522205A (ja) 病態及び疾患の治療用アンチセンスオリゴマー
WO2022248879A1 (en) Composition and method for adar-mediated rna editing
JP2022534086A5 (enExample)
JP2021510512A5 (enExample)
CN119365598A (zh) 用于治疗单基因神经发育障碍的组合物和方法
CN118043461A (zh) 方法
WO2005004913A1 (ja) デコイを含む薬学的組成物およびその使用方法
CN117980479A (zh) 用于治疗基于无义介导的rna衰变的病状和疾病的反义寡聚体
WO1996023878A1 (en) Human immunodeficiency virus transcription inhibitors and methods of their use
US12163132B2 (en) Gapmer antisense oligonucleotides targeting SARS-CoV-2 for treating COVID 19
US20250136996A1 (en) Treatment of smoking with cholinergic receptor nicotinic beta 3 subunit (chrnb3) inhibitors