JP2022534086A5 - - Google Patents

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Publication number
JP2022534086A5
JP2022534086A5 JP2021569934A JP2021569934A JP2022534086A5 JP 2022534086 A5 JP2022534086 A5 JP 2022534086A5 JP 2021569934 A JP2021569934 A JP 2021569934A JP 2021569934 A JP2021569934 A JP 2021569934A JP 2022534086 A5 JP2022534086 A5 JP 2022534086A5
Authority
JP
Japan
Prior art keywords
cnot3
expression
composition according
antisense oligomer
oligomer
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Granted
Application number
JP2021569934A
Other languages
English (en)
Japanese (ja)
Other versions
JP7652713B2 (ja
JP2022534086A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/AU2020/050516 external-priority patent/WO2020237294A1/en
Publication of JP2022534086A publication Critical patent/JP2022534086A/ja
Publication of JP2022534086A5 publication Critical patent/JP2022534086A5/ja
Priority to JP2025041378A priority Critical patent/JP2025085741A/ja
Application granted granted Critical
Publication of JP7652713B2 publication Critical patent/JP7652713B2/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

Links

JP2021569934A 2019-05-27 2020-05-25 新規の網膜色素変性処置 Active JP7652713B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2025041378A JP2025085741A (ja) 2019-05-27 2025-03-14 新規の網膜色素変性処置

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
AU2019901804A AU2019901804A0 (en) 2019-05-27 Novel Retinitis Pigmentosa Treatment
AU2019901804 2019-05-27
AU2019903812 2019-10-10
AU2019903812A AU2019903812A0 (en) 2019-10-10 Novel Retinitis Pigmentosa Treatment
PCT/AU2020/050516 WO2020237294A1 (en) 2019-05-27 2020-05-25 Novel retinitis pigmentosa treatment

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2025041378A Division JP2025085741A (ja) 2019-05-27 2025-03-14 新規の網膜色素変性処置

Publications (3)

Publication Number Publication Date
JP2022534086A JP2022534086A (ja) 2022-07-27
JP2022534086A5 true JP2022534086A5 (enExample) 2023-06-01
JP7652713B2 JP7652713B2 (ja) 2025-03-27

Family

ID=73553023

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2021569934A Active JP7652713B2 (ja) 2019-05-27 2020-05-25 新規の網膜色素変性処置
JP2025041378A Pending JP2025085741A (ja) 2019-05-27 2025-03-14 新規の網膜色素変性処置

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2025041378A Pending JP2025085741A (ja) 2019-05-27 2025-03-14 新規の網膜色素変性処置

Country Status (11)

Country Link
US (2) US12559747B2 (enExample)
EP (1) EP3976789A4 (enExample)
JP (2) JP7652713B2 (enExample)
KR (1) KR20220012276A (enExample)
CN (1) CN113891940B (enExample)
AU (1) AU2020285470B2 (enExample)
BR (1) BR112021023936A2 (enExample)
CA (1) CA3141633A1 (enExample)
IL (1) IL288442A (enExample)
SG (1) SG11202112946VA (enExample)
WO (1) WO2020237294A1 (enExample)

Families Citing this family (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US12559747B2 (en) * 2019-05-27 2026-02-24 Vision Pharma Pty Ltd Retinitis pigmentosa treatment
US12338437B2 (en) 2020-05-11 2025-06-24 Stoke Therapeutics, Inc. OPA1 antisense oligomers for treatment of conditions and diseases
WO2025043278A1 (en) * 2023-08-25 2025-03-06 PYC Therapeutics Limited Gene-mediated conditions
WO2026090034A1 (en) * 2024-10-21 2026-04-30 Vision Pharma Pty Ltd Agents for treatment of optic conditions

Family Cites Families (17)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US4458066A (en) 1980-02-29 1984-07-03 University Patents, Inc. Process for preparing polynucleotides
US5149797A (en) 1990-02-15 1992-09-22 The Worcester Foundation For Experimental Biology Method of site-specific alteration of rna and production of encoded polypeptides
US20020123476A1 (en) 1991-03-19 2002-09-05 Emanuele R. Martin Therapeutic delivery compositions and methods of use thereof
RU2034835C1 (ru) 1992-03-09 1995-05-10 Научно-исследовательский и проектный институт мономеров с опытным заводом СПОСОБ ПОЛУЧЕНИЯ β -КАРОТИНА
US6806084B1 (en) 1992-06-04 2004-10-19 The Regents Of The University Of California Methods for compositions for in vivo gene delivery
WO1997022371A1 (en) 1995-12-18 1997-06-26 Collagen Corporation Crosslinked polymer compositions and methods for their use
US6821724B1 (en) * 1998-09-17 2004-11-23 Affymetrix, Inc. Methods of genetic analysis using nucleic acid arrays
US6287860B1 (en) 2000-01-20 2001-09-11 Isis Pharmaceuticals, Inc. Antisense inhibition of MEKK2 expression
US6965025B2 (en) 2001-12-10 2005-11-15 Isis Pharmaceuticals, Inc. Antisense modulation of connective tissue growth factor expression
US20100016215A1 (en) 2007-06-29 2010-01-21 Avi Biopharma, Inc. Compound and method for treating myotonic dystrophy
AU2011349464B2 (en) 2010-12-20 2016-07-07 The General Hospital Corporation Polycomb-associated non-coding RNAS
WO2013027104A1 (en) 2011-08-25 2013-02-28 Db Equipment As Accessory bag having reinforced sidewalls and variable length
US20210254056A1 (en) * 2017-05-05 2021-08-19 Camp4 Therapeutics Corporation Identification and targeted modulation of gene signaling networks
US12559747B2 (en) * 2019-05-27 2026-02-24 Vision Pharma Pty Ltd Retinitis pigmentosa treatment
KR20220104677A (ko) * 2019-08-19 2022-07-26 스톡 테라퓨틱스, 인크. 스플라이싱 및 단백질 발현을 조절하기 위한 조성물 및 방법
JP2023529026A (ja) * 2020-06-01 2023-07-06 デイナ ファーバー キャンサー インスティチュート,インコーポレイテッド Mhc-i発現を調節するための方法及びその免疫療法の使用
CN113584038B (zh) * 2021-09-09 2023-11-14 深圳雅济科技有限公司 一种治疗视网膜疾病的反义寡核苷酸组合及其应用

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