JP2022531347A5 - - Google Patents

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Publication number
JP2022531347A5
JP2022531347A5 JP2021564834A JP2021564834A JP2022531347A5 JP 2022531347 A5 JP2022531347 A5 JP 2022531347A5 JP 2021564834 A JP2021564834 A JP 2021564834A JP 2021564834 A JP2021564834 A JP 2021564834A JP 2022531347 A5 JP2022531347 A5 JP 2022531347A5
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JP
Japan
Application number
JP2021564834A
Other languages
Japanese (ja)
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JPWO2020223514A5 (https=
JP2022531347A (ja
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Publication date
Application filed filed Critical
Priority claimed from PCT/US2020/030782 external-priority patent/WO2020223514A2/en
Publication of JP2022531347A publication Critical patent/JP2022531347A/ja
Publication of JPWO2020223514A5 publication Critical patent/JPWO2020223514A5/ja
Publication of JP2022531347A5 publication Critical patent/JP2022531347A5/ja
Priority to JP2024000768A priority Critical patent/JP2024050582A/ja
Pending legal-status Critical Current

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JP2021564834A 2019-04-30 2020-04-30 新規のomni-50crisprヌクレアーゼ Pending JP2022531347A (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2024000768A JP2024050582A (ja) 2019-04-30 2024-01-05 新規のomni-50crisprヌクレアーゼ

Applications Claiming Priority (11)

Application Number Priority Date Filing Date Title
US201962841046P 2019-04-30 2019-04-30
US62/841,046 2019-04-30
US201962897806P 2019-09-09 2019-09-09
US62/897,806 2019-09-09
US201962931630P 2019-11-06 2019-11-06
US62/931,630 2019-11-06
US202062959672P 2020-01-10 2020-01-10
US62/959,672 2020-01-10
US202062991285P 2020-03-18 2020-03-18
US62/991,285 2020-03-18
PCT/US2020/030782 WO2020223514A2 (en) 2019-04-30 2020-04-30 Novel omni-50 crispr nuclease

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2024000768A Division JP2024050582A (ja) 2019-04-30 2024-01-05 新規のomni-50crisprヌクレアーゼ

Publications (3)

Publication Number Publication Date
JP2022531347A JP2022531347A (ja) 2022-07-06
JPWO2020223514A5 JPWO2020223514A5 (https=) 2023-05-11
JP2022531347A5 true JP2022531347A5 (https=) 2023-05-11

Family

ID=73029467

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2021564834A Pending JP2022531347A (ja) 2019-04-30 2020-04-30 新規のomni-50crisprヌクレアーゼ
JP2024000768A Pending JP2024050582A (ja) 2019-04-30 2024-01-05 新規のomni-50crisprヌクレアーゼ

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2024000768A Pending JP2024050582A (ja) 2019-04-30 2024-01-05 新規のomni-50crisprヌクレアーゼ

Country Status (10)

Country Link
US (2) US11666641B2 (https=)
EP (1) EP3963061A4 (https=)
JP (2) JP2022531347A (https=)
KR (2) KR20250060327A (https=)
CN (1) CN114127274A (https=)
AU (2) AU2020266587B2 (https=)
BR (1) BR112021021912A2 (https=)
CA (1) CA3135759A1 (https=)
IL (1) IL287693A (https=)
WO (1) WO2020223514A2 (https=)

Families Citing this family (15)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP3204496A1 (en) 2014-10-10 2017-08-16 Editas Medicine, Inc. Compositions and methods for promoting homology directed repair
EP3823633A4 (en) 2018-06-29 2023-05-03 Editas Medicine, Inc. SYNTHETIC LEAD MOLECULES, COMPOSITIONS AND METHODS RELATED THERETO
US11946077B2 (en) 2020-06-04 2024-04-02 Emendobio Inc. OMNI-59, 61, 67, 76, 79, 80, 81, and 82 CRISPR nucleases
WO2022098693A1 (en) * 2020-11-04 2022-05-12 Emendobio Inc. Novel omni-50 crispr nuclease-rna complexes
US20240175013A1 (en) * 2020-12-14 2024-05-30 Emendobio Inc. Biallelic knockout of trac
WO2022132765A1 (en) * 2020-12-14 2022-06-23 Emendobio Inc. Biallelic knockout of b2m
US12091688B2 (en) 2021-02-08 2024-09-17 Emendobio Inc. OMNI-103 CRISPR nuclease
KR20230142740A (ko) 2021-02-08 2023-10-11 에멘도바이오 인코포레이티드 Omni-103 crispr 뉴클레아제
IL307855A (en) * 2021-04-22 2023-12-01 Emendobio Inc OMNI CRISPR Nucleases 117, 140, 150-158, 160-165, 167-177, 180-188, 191-198, 200, 201, 203, 205-209, 211-217, 219, 220, 222, 223, 226 , 227, 229, 231-236, 238-245, 247, 250, 254, 256, 257, 260 and 262 news
IL310730A (en) * 2021-08-12 2024-04-01 Emendobio Inc Engineered high fidelity omni-50 nuclease variants
JP2024540558A (ja) * 2021-11-19 2024-10-31 エメンドバイオ・インコーポレイテッド 新規なomni crisprヌクレアーゼ
US20250043260A1 (en) * 2021-12-01 2025-02-06 Emendobio Inc. Engineered High Activity Omni-79 Nuclease Variants
US20260021141A1 (en) * 2022-07-15 2026-01-22 Emendobio Inc. Strategies For Knock-Ins At APLP2 Safe Harbor Sites
WO2024042165A2 (en) * 2022-08-26 2024-02-29 UCB Biopharma SRL Novel rna-guided nucleases and nucleic acid targeting systems comprising such rna-guided nucleases
WO2025043140A1 (en) * 2023-08-23 2025-02-27 Emendobio Inc. Methods and compositions for modifying expression of a mutant transforming growth factor beta induced (tgfbi) allele

Family Cites Families (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP2334794B8 (en) 2008-09-15 2017-04-19 The Children's Medical Center Corporation Modulation of bcl11a for treatment of hemoglobinopathies
EP3241902B1 (en) 2012-05-25 2018-02-28 The Regents of The University of California Methods and compositions for rna-directed target dna modification and for rna-directed modulation of transcription
WO2015134812A1 (en) * 2014-03-05 2015-09-11 Editas Medicine, Inc. Crispr/cas-related methods and compositions for treating usher syndrome and retinitis pigmentosa
WO2017024047A1 (en) 2015-08-03 2017-02-09 Emendobio Inc. Compositions and methods for increasing nuclease induced recombination rate in cells
ES2942309T3 (es) 2015-11-04 2023-05-31 Vertex Pharma Materiales y métodos para el tratamiento de hemoglobinopatías
CN105567735A (zh) * 2016-01-05 2016-05-11 华东师范大学 一种凝血因子基因突变的定点修复载体系统及方法

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