JP2022528416A5 - - Google Patents
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- Publication number
- JP2022528416A5 JP2022528416A5 JP2021559079A JP2021559079A JP2022528416A5 JP 2022528416 A5 JP2022528416 A5 JP 2022528416A5 JP 2021559079 A JP2021559079 A JP 2021559079A JP 2021559079 A JP2021559079 A JP 2021559079A JP 2022528416 A5 JP2022528416 A5 JP 2022528416A5
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Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2025003555A JP2025069170A (ja) | 2019-04-04 | 2025-01-09 | 組換えアデノ随伴ウイルス及びその使用 |
Applications Claiming Priority (11)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962829608P | 2019-04-04 | 2019-04-04 | |
| US62/829,608 | 2019-04-04 | ||
| US201962833516P | 2019-04-12 | 2019-04-12 | |
| US62/833,516 | 2019-04-12 | ||
| US201962839368P | 2019-04-26 | 2019-04-26 | |
| US62/839,368 | 2019-04-26 | ||
| US201962924107P | 2019-10-21 | 2019-10-21 | |
| US62/924,107 | 2019-10-21 | ||
| US202062963512P | 2020-01-20 | 2020-01-20 | |
| US62/963,512 | 2020-01-20 | ||
| PCT/US2020/026485 WO2020206189A1 (en) | 2019-04-04 | 2020-04-02 | Recombinant adeno-associated viruses and uses thereof |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025003555A Division JP2025069170A (ja) | 2019-04-04 | 2025-01-09 | 組換えアデノ随伴ウイルス及びその使用 |
Publications (4)
| Publication Number | Publication Date |
|---|---|
| JP2022528416A JP2022528416A (ja) | 2022-06-10 |
| JP2022528416A5 true JP2022528416A5 (https=) | 2023-04-11 |
| JPWO2020206189A5 JPWO2020206189A5 (https=) | 2023-04-11 |
| JP7619958B2 JP7619958B2 (ja) | 2025-01-22 |
Family
ID=70416587
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021559079A Active JP7619958B2 (ja) | 2019-04-04 | 2020-04-02 | 組換えアデノ随伴ウイルス及びその使用 |
| JP2025003555A Pending JP2025069170A (ja) | 2019-04-04 | 2025-01-09 | 組換えアデノ随伴ウイルス及びその使用 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025003555A Pending JP2025069170A (ja) | 2019-04-04 | 2025-01-09 | 組換えアデノ随伴ウイルス及びその使用 |
Country Status (9)
| Country | Link |
|---|---|
| US (1) | US20220186256A1 (https=) |
| EP (1) | EP3947420A1 (https=) |
| JP (2) | JP7619958B2 (https=) |
| CN (1) | CN114127089A (https=) |
| CA (1) | CA3135798A1 (https=) |
| IL (1) | IL286911A (https=) |
| MX (1) | MX2021011963A (https=) |
| TW (1) | TW202102526A (https=) |
| WO (1) | WO2020206189A1 (https=) |
Families Citing this family (59)
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| EP4591708A3 (en) | 2020-07-08 | 2026-01-14 | Baylor College of Medicine | Gene therapy for stxbp1 encephalopathy |
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| EP4185608A4 (en) * | 2020-07-23 | 2024-08-21 | University of Florida Research Foundation, Inc. | INSULIN RECEPTOR-MEDIATED ENHANCEMENT OF GENE TRANSFER |
| US20230381341A1 (en) * | 2020-10-07 | 2023-11-30 | Regenxbio Inc. | Adeno-associated viruses for ocular delivery of gene therapy |
| WO2022076750A2 (en) * | 2020-10-07 | 2022-04-14 | Regenxbio Inc. | Recombinant adeno-associated viruses for cns or muscle delivery |
| EP4243848A4 (en) * | 2020-11-10 | 2025-07-23 | Avirmax Biopharma Inc | MODIFIED VIRAL CAPSIDS AND METHODS OF USE |
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| WO2022156531A1 (zh) * | 2021-01-19 | 2022-07-28 | 中国人民解放军军事科学院军事医学研究院 | 一种能够透过生物屏障的动力蛋白结合肽及其应用 |
| CN114805594B (zh) * | 2021-01-19 | 2024-01-26 | 中国人民解放军军事科学院军事医学研究院 | 一种能够透过生物屏障且聚集核周的动力蛋白结合肽及其应用 |
| CN114805595B (zh) * | 2021-01-19 | 2024-01-26 | 中国人民解放军军事科学院军事医学研究院 | 具有生物屏障透过性和核内聚集特性的动力蛋白结合肽及其应用 |
| WO2022173847A2 (en) * | 2021-02-09 | 2022-08-18 | Affinia Therapeutics Inc. | Recombinant aavs with improved tropism and specificity |
| CN113121651B (zh) * | 2021-04-19 | 2023-11-17 | 信念医药科技(上海)有限公司 | 低中和抗体腺相关病毒衣壳蛋白 |
| CN113121653B (zh) * | 2021-04-19 | 2021-11-19 | 上海信致医药科技有限公司 | 肌肉和视网膜特异性的新型腺相关病毒衣壳蛋白 |
| CA3220800A1 (en) * | 2021-06-03 | 2022-12-08 | Sylvain LAPAN | Capsid variants and methods of using the same |
| WO2023283962A1 (en) * | 2021-07-16 | 2023-01-19 | Huigene Therapeutics Co., Ltd. | Modified aav capsid for gene therapy and methods thereof |
| EP4359551A4 (en) * | 2021-07-23 | 2025-09-24 | Univ Duke | ADENO-ASSOCIATED VIRUS COMPOSITIONS AND METHODS OF USE THEREOF |
| CN118202060A (zh) | 2021-10-05 | 2024-06-14 | 再生生物股份有限公司 | 用于重组aav生产的组合物和方法 |
| WO2023060113A1 (en) | 2021-10-05 | 2023-04-13 | Regenxbio Inc. | Compositions and methods for recombinant aav production |
| WO2023060272A2 (en) * | 2021-10-07 | 2023-04-13 | Regenxbio Inc. | Recombinant adeno-associated viruses for cns tropic delivery |
| WO2023060269A1 (en) * | 2021-10-07 | 2023-04-13 | Regenxbio Inc. | Recombinant adeno-associated viruses for targeted delivery |
| MX2024004217A (es) | 2021-10-08 | 2024-06-26 | Dyno Therapeutics Inc | Variantes de cápside y métodos de uso de estas. |
| MX2024004936A (es) | 2021-11-02 | 2024-05-08 | Voyager Therapeutics Inc | Variantes de capsides de aav y sus usos. |
| WO2023108507A1 (en) * | 2021-12-15 | 2023-06-22 | National Institute Of Biological Sciences, Beijing | Recombinant aav vectors and use thereof |
| US20250382634A1 (en) * | 2021-12-21 | 2025-12-18 | Curigin Co., Ltd. | Immune-cloaking antitumor adenovirus |
| WO2023183623A1 (en) | 2022-03-25 | 2023-09-28 | Regenxbio Inc. | Dominant-negative tumor necrosis factor alpha adeno-associated virus gene therapy |
| WO2023201277A1 (en) * | 2022-04-14 | 2023-10-19 | Regenxbio Inc. | Recombinant adeno-associated viruses for cns tropic delivery |
| US20250277004A1 (en) | 2022-04-18 | 2025-09-04 | Regenxbio Inc. | Hybrid aav capsids |
| AU2023282121A1 (en) * | 2022-05-31 | 2025-01-09 | Mount Spec Investments Pty Ltd | Modified adeno-associated virus capsid proteins and methods thereof |
| WO2023242633A2 (en) * | 2022-06-14 | 2023-12-21 | Vectory B.V. | Recombinant aav capsid proteins |
| JP2025524656A (ja) * | 2022-07-14 | 2025-07-30 | ザ・ブロード・インスティテュート・インコーポレイテッド | トランスフェリン受容体との相互作用を通じてｃｎｓ全体への遺伝子送達を可能にするａａｖキャプシド |
| JP2025525792A (ja) * | 2022-07-29 | 2025-08-07 | リジェネロン・ファーマシューティカルズ・インコーポレイテッド | トランスフェリン受容体１に対して再標的化されるウイルス粒子 |
| WO2024040193A2 (en) * | 2022-08-17 | 2024-02-22 | Affinia Therapeutics Inc. | Recombinant aavs with improved tropism and specificity |
| JP2025527658A (ja) | 2022-08-24 | 2025-08-22 | リジェネックスバイオ インコーポレイテッド | 組換えアデノ随伴ウイルス及びその使用 |
| EP4410987A1 (en) * | 2023-01-31 | 2024-08-07 | Universitätsklinikum Hamburg-Eppendorf | An aav9 capsid variant for targeted gene transfer |
| EP4410988A1 (en) * | 2023-01-31 | 2024-08-07 | Universitätsklinikum Hamburg-Eppendorf | An aav2-vector variant for targeted transfer of genes |
| CN116693633B (zh) * | 2023-02-21 | 2023-12-22 | 广州派真生物技术有限公司 | 腺相关病毒突变体及其应用 |
| TW202502803A (zh) | 2023-03-10 | 2025-01-16 | 美商戴諾治療公司 | 衣殼多肽及其使用方法 |
| EP4680741A2 (en) | 2023-03-15 | 2026-01-21 | RegenxBio Inc. | Exon skipping gene therapy constructs, vectors and uses thereof |
| AU2024242380A1 (en) * | 2023-03-31 | 2025-11-06 | Exegenesis Bio Singapore Pte. Ltd. | Variant aav9 capsid proteins and uses thereof |
| WO2024229389A1 (en) * | 2023-05-03 | 2024-11-07 | Voyager Therapeutics, Inc. | Compositions and methods for the treatment of tau-related disorders |
| EP4705488A1 (en) * | 2023-05-04 | 2026-03-11 | Voyager Therapeutics, Inc. | Aav capsid variants and uses thereof |
| WO2024238807A2 (en) * | 2023-05-16 | 2024-11-21 | Affinia Therapeutics Inc. | Recombinant aavs with improved tropism and specificity |
| WO2025018388A1 (ja) * | 2023-07-20 | 2025-01-23 | 学校法人自治医科大学 | 抗菌カプシド、治療用組成物、殺菌剤、細菌除去方法、殺菌方法、動物治療方法、遺伝子導入方法、細菌機能追加方法、抗菌カプシドの製造方法、抗菌カプシドの標識方法、及び抗菌カプシドの細胞内送達方法 |
| WO2025137290A1 (en) * | 2023-12-19 | 2025-06-26 | The Broad Institute, Inc. | Methods and systems directed to therapeutic delivery of the human gba1 gene |
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| TW202545971A (zh) | 2024-02-08 | 2025-12-01 | 美商戴諾治療公司 | 殼體多肽及其使用方法 |
| WO2025207954A1 (en) * | 2024-03-27 | 2025-10-02 | General Medicines Llc | Compositions and methods for improved adeno-associated viral gene therapy |
| WO2025217214A2 (en) | 2024-04-08 | 2025-10-16 | Regenxbio Inc. | Recombinant adeno-associated viruses and uses thereof |
| US20260042803A1 (en) * | 2024-08-09 | 2026-02-12 | Revvity Gene Delivery Gmbh | Variant aav capsid polypeptides targeting the eye |
| WO2026037757A1 (en) | 2024-08-13 | 2026-02-19 | F. Hoffmann-La Roche Ag | Modified aav particles |
| CN119039401B (zh) * | 2024-08-19 | 2025-04-11 | 广州派真生物技术有限公司 | 腺相关病毒突变体及其应用 |
| WO2026042009A1 (en) | 2024-08-19 | 2026-02-26 | Theriva Biologics S.L. | Modified adenovirus by hexon hypervariable region 7 (hvr7) gene insertion |
| WO2026041788A1 (en) * | 2024-08-22 | 2026-02-26 | Uniqure Biopharma B.V | Novel bbb interacting capsids |
| WO2026064428A2 (en) | 2024-09-18 | 2026-03-26 | Dyno Therapeutics, Inc. | Capsid polypeptides and methods of use thereof |
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| WO2026064444A1 (en) | 2024-09-18 | 2026-03-26 | Dyno Therapeutics, Inc. | Capsid polypeptides and methods of use thereof |
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-
2020
- 2020-04-01 TW TW109111391A patent/TW202102526A/zh unknown
- 2020-04-02 US US17/600,418 patent/US20220186256A1/en active Pending
- 2020-04-02 MX MX2021011963A patent/MX2021011963A/es unknown
- 2020-04-02 JP JP2021559079A patent/JP7619958B2/ja active Active
- 2020-04-02 WO PCT/US2020/026485 patent/WO2020206189A1/en not_active Ceased
- 2020-04-02 CN CN202080031981.XA patent/CN114127089A/zh active Pending
- 2020-04-02 CA CA3135798A patent/CA3135798A1/en active Pending
- 2020-04-02 EP EP20721074.1A patent/EP3947420A1/en active Pending
-
2021
- 2021-10-03 IL IL286911A patent/IL286911A/en unknown
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2025
- 2025-01-09 JP JP2025003555A patent/JP2025069170A/ja active Pending