JP2022522166A5 - - Google Patents
Info
- Publication number
- JP2022522166A5 JP2022522166A5 JP2021549908A JP2021549908A JP2022522166A5 JP 2022522166 A5 JP2022522166 A5 JP 2022522166A5 JP 2021549908 A JP2021549908 A JP 2021549908A JP 2021549908 A JP2021549908 A JP 2021549908A JP 2022522166 A5 JP2022522166 A5 JP 2022522166A5
- Authority
- JP
- Japan
- Prior art keywords
- sequence
- effector
- seq
- sequence described
- shmir
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962812187P | 2019-02-28 | 2019-02-28 | |
| US62/812,187 | 2019-02-28 | ||
| PCT/AU2020/050182 WO2020172720A1 (en) | 2019-02-28 | 2020-02-28 | Compositions and methods for treating oculopharyngeal muscular dystrophy (opmd) |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2022522166A JP2022522166A (ja) | 2022-04-14 |
| JP2022522166A5 true JP2022522166A5 (enExample) | 2023-03-03 |
Family
ID=72238736
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021549908A Pending JP2022522166A (ja) | 2019-02-28 | 2020-02-28 | 眼咽頭型筋ジストロフィー（ｏｐｍｄ）を治療するための組成物及び方法 |
Country Status (12)
| Country | Link |
|---|---|
| US (1) | US20220098614A1 (enExample) |
| EP (1) | EP3931317A4 (enExample) |
| JP (1) | JP2022522166A (enExample) |
| KR (1) | KR102959609B1 (enExample) |
| CN (2) | CN121160804A (enExample) |
| AU (1) | AU2020229886B2 (enExample) |
| BR (1) | BR112021017054A2 (enExample) |
| CA (1) | CA3130221A1 (enExample) |
| IL (1) | IL285841A (enExample) |
| MX (1) | MX2021010412A (enExample) |
| SG (1) | SG11202108469XA (enExample) |
| WO (1) | WO2020172720A1 (enExample) |
Families Citing this family (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| SG11202102185RA (en) * | 2018-10-17 | 2021-05-28 | Benitec Biopharma Ltd | Methods for treating oculopharyngeal muscular dystrophy (opmd) |
| KR20260030147A (ko) * | 2023-06-28 | 2026-03-05 | 베니텍 아이피 홀딩스 아이엔씨. | 인두 근육에 치료 조성물을 투여하기 위한 장치 및 방법 |
| WO2026011009A1 (en) * | 2024-07-02 | 2026-01-08 | Kate Therapeutics, Inc. | Compositions and methods for muscle disorders |
Family Cites Families (21)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US4745051A (en) | 1983-05-27 | 1988-05-17 | The Texas A&M University System | Method for producing a recombinant baculovirus expression vector |
| EP1983057A3 (en) | 1995-09-08 | 2009-01-07 | Genzyme Corporation | Improved AAV vectors for gene therapy |
| WO2001049829A1 (en) | 2000-01-05 | 2001-07-12 | Fred Hutchinson Cancer Research Center | Compositions and methods for efficient aav vector production |
| CA2448120A1 (en) | 2001-05-24 | 2002-11-28 | Genzyme Corporation | Muscle-specific expression vectors |
| AU2002360355B2 (en) | 2001-11-09 | 2005-07-07 | Government Of The United States Of America, Department Of Health And Human Services | Production of adeno-associated virus in insect cells |
| US6723551B2 (en) | 2001-11-09 | 2004-04-20 | The United States Of America As Represented By The Department Of Health And Human Services | Production of adeno-associated virus in insect cells |
| WO2003074714A1 (en) | 2002-03-05 | 2003-09-12 | Stichting Voor De Technische Wetenschappen | Baculovirus expression system |
| US20060166363A1 (en) | 2004-01-27 | 2006-07-27 | Sergei Zolotukhin | Modified baculovirus expression system for production of pseudotyped rAAV vector |
| US8008468B2 (en) | 2005-02-16 | 2011-08-30 | Benitec, Inc. | RNAi expression constructs with liver-specific enhancer/promoter |
| AU2006304997B2 (en) | 2005-10-20 | 2012-03-01 | Uniqure Ip B.V. | Improved AAV vectors produced in insect cells |
| US8129510B2 (en) | 2006-03-30 | 2012-03-06 | The Board Of Trustees Of The Leland Stanford Junior University | Minigene expression cassette |
| US9198984B2 (en) | 2006-04-28 | 2015-12-01 | The Trustees Of The University Of Pennsylvania | Scalable production method for AAV |
| ES2785223T3 (es) | 2006-06-21 | 2020-10-06 | Uniqure Ip Bv | Células de insecto para la producción de vectores de AAV |
| CA2713338C (en) | 2008-01-29 | 2021-10-26 | Applied Genetic Technologies Corporation | Recombinant virus production using mammalian cells in suspension |
| PT3024497T (pt) * | 2013-07-26 | 2021-08-23 | Univ Iowa Res Found | Métodos e composições para o tratamento de doenças cerebrais |
| US11078464B2 (en) | 2013-08-30 | 2021-08-03 | Amgen Inc. | High titer recombinant AAV vector production in adherent and suspension cells |
| CN104815338A (zh) * | 2015-05-01 | 2015-08-05 | 许瑞安 | 一种携带kal基因重组腺相关病毒载体的基因治疗药物 |
| AU2017254652B2 (en) | 2016-04-21 | 2022-12-01 | Virovek, Inc. | AAV production in insect cells, methods and compositions therefor |
| MX2019007110A (es) * | 2016-12-14 | 2019-12-05 | Benitec Biopharma Ltd | Reactivos para el tratamiento de la distrofia muscular oculofaringea (opmd) y uso de estos. |
| EP3575398A4 (en) * | 2017-01-30 | 2020-11-11 | Nippon Medical School Foundation | ADENO-ASSOCIATED VIRUS (AAV) CAPSIDE PROTEIN MUTANT |
| KR102612563B1 (ko) | 2017-08-31 | 2023-12-11 | 베니텍 아이피 홀딩스 아이엔씨. | 변형된 포스포리파제 도메인을 갖는 아데노-연관 바이러스 (aav) |
-
2020
- 2020-02-28 US US17/434,666 patent/US20220098614A1/en active Pending
- 2020-02-28 WO PCT/AU2020/050182 patent/WO2020172720A1/en not_active Ceased
- 2020-02-28 CN CN202511142034.9A patent/CN121160804A/zh active Pending
- 2020-02-28 KR KR1020217031046A patent/KR102959609B1/ko active Active
- 2020-02-28 BR BR112021017054A patent/BR112021017054A2/pt unknown
- 2020-02-28 EP EP20762817.3A patent/EP3931317A4/en active Pending
- 2020-02-28 CA CA3130221A patent/CA3130221A1/en active Pending
- 2020-02-28 SG SG11202108469XA patent/SG11202108469XA/en unknown
- 2020-02-28 MX MX2021010412A patent/MX2021010412A/es unknown
- 2020-02-28 AU AU2020229886A patent/AU2020229886B2/en active Active
- 2020-02-28 CN CN202080017400.7A patent/CN113631706A/zh active Pending
- 2020-02-28 JP JP2021549908A patent/JP2022522166A/ja active Pending
-
2021
- 2021-08-24 IL IL285841A patent/IL285841A/en unknown
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