JP2022522166A5 - - Google Patents
Info
- Publication number
- JP2022522166A5 JP2022522166A5 JP2021549908A JP2021549908A JP2022522166A5 JP 2022522166 A5 JP2022522166 A5 JP 2022522166A5 JP 2021549908 A JP2021549908 A JP 2021549908A JP 2021549908 A JP2021549908 A JP 2021549908A JP 2022522166 A5 JP2022522166 A5 JP 2022522166A5
- Authority
- JP
- Japan
- Prior art keywords
- sequence
- effector
- seq
- sequence described
- shmir
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962812187P | 2019-02-28 | 2019-02-28 | |
| US62/812,187 | 2019-02-28 | ||
| PCT/AU2020/050182 WO2020172720A1 (en) | 2019-02-28 | 2020-02-28 | Compositions and methods for treating oculopharyngeal muscular dystrophy (opmd) |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2022522166A JP2022522166A (ja) | 2022-04-14 |
| JP2022522166A5 true JP2022522166A5 (enExample) | 2023-03-03 |
Family
ID=72238736
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021549908A Pending JP2022522166A (ja) | 2019-02-28 | 2020-02-28 | 眼咽頭型筋ジストロフィー（ｏｐｍｄ）を治療するための組成物及び方法 |
Country Status (11)
| Country | Link |
|---|---|
| US (1) | US20220098614A1 (enExample) |
| EP (1) | EP3931317A4 (enExample) |
| JP (1) | JP2022522166A (enExample) |
| CN (2) | CN113631706A (enExample) |
| AU (1) | AU2020229886B2 (enExample) |
| BR (1) | BR112021017054A2 (enExample) |
| CA (1) | CA3130221A1 (enExample) |
| IL (1) | IL285841A (enExample) |
| MX (1) | MX2021010412A (enExample) |
| SG (1) | SG11202108469XA (enExample) |
| WO (1) | WO2020172720A1 (enExample) |
Families Citing this family (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| JP2022508835A (ja) * | 2018-10-17 | 2022-01-19 | ベニテック バイオファーマ リミテッド | 眼咽頭筋ジストロフィー（ｏｐｍｄ）を治療するための方法 |
| AU2024310011A1 (en) * | 2023-06-28 | 2026-02-05 | Benitec IP Holdings Inc. | Device and methods for administering a therapeutic composition to the pharyngeal muscle |
| WO2026011009A1 (en) * | 2024-07-02 | 2026-01-08 | Kate Therapeutics, Inc. | Compositions and methods for muscle disorders |
Family Cites Families (21)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US4745051A (en) | 1983-05-27 | 1988-05-17 | The Texas A&M University System | Method for producing a recombinant baculovirus expression vector |
| US6632670B1 (en) | 1995-09-08 | 2003-10-14 | Genzyme Corporation | AAV vectors for gene therapy |
| US7208315B2 (en) | 2000-01-05 | 2007-04-24 | Fred Hutchinson Cancer Research Center | Compositions and methods for efficient AAV vector production |
| EP1390490B1 (en) | 2001-05-24 | 2009-04-15 | Genzyme Corporation | Muscle-specific expression vectors |
| WO2003042361A2 (en) | 2001-11-09 | 2003-05-22 | Government Of The United States Of America, Department Of Health And Human Services | Production of adeno-associated virus in insect cells |
| US6723551B2 (en) | 2001-11-09 | 2004-04-20 | The United States Of America As Represented By The Department Of Health And Human Services | Production of adeno-associated virus in insect cells |
| AU2003212708A1 (en) | 2002-03-05 | 2003-09-16 | Stichting Voor De Technische Wetenschappen | Baculovirus expression system |
| US20060166363A1 (en) | 2004-01-27 | 2006-07-27 | Sergei Zolotukhin | Modified baculovirus expression system for production of pseudotyped rAAV vector |
| US8008468B2 (en) | 2005-02-16 | 2011-08-30 | Benitec, Inc. | RNAi expression constructs with liver-specific enhancer/promoter |
| EP2311966A3 (en) | 2005-10-20 | 2012-09-05 | Amsterdam Molecular Therapeutics (AMT) B.V. | Improved AAV vectors produced in insect cells |
| WO2007120533A2 (en) | 2006-03-30 | 2007-10-25 | The Board Of Trustees Of The Leland Stanford Junior University | Minigene expression cassette |
| EP2018421B1 (en) | 2006-04-28 | 2012-12-19 | The Trustees of the University of Pennsylvania | Scalable production method for aav |
| CN103849629B (zh) | 2006-06-21 | 2017-06-09 | 尤尼克尔Ip股份有限公司 | 具有经修饰的用于在昆虫细胞中产生aav的aav‑rep78翻译起始密码子的载体 |
| ES2751999T3 (es) | 2008-01-29 | 2020-04-02 | Applied Genetic Tech Corporation | Producción recombinante de virus adeno-asociados usando células BHK en suspensión |
| EP3024497B1 (en) * | 2013-07-26 | 2021-01-13 | University of Iowa Research Foundation | Methods and compositions for treating brain diseases |
| WO2015031686A1 (en) | 2013-08-30 | 2015-03-05 | Amgen Inc. | High titer recombinant aav vector production in adherent and suspension cells |
| CN104815338A (zh) * | 2015-05-01 | 2015-08-05 | 许瑞安 | 一种携带kal基因重组腺相关病毒载体的基因治疗药物 |
| JP7496667B2 (ja) | 2016-04-21 | 2024-06-07 | ビロベク，インコーポレイテッド | 昆虫細胞中でのａａｖ生成、方法およびその組成物 |
| JP7233149B2 (ja) * | 2016-12-14 | 2023-03-06 | ベニテック アイピー ホールディングス インコーポレーテッド | 眼咽頭型筋ジストロフィー（ｏｐｍｄ）を治療するための試薬及びその使用 |
| EP3575398A4 (en) * | 2017-01-30 | 2020-11-11 | Nippon Medical School Foundation | ADENO-ASSOCIATED VIRUS (AAV) CAPSIDE PROTEIN MUTANT |
| BR112020003976A8 (pt) | 2017-08-31 | 2023-03-28 | Benitec Biopharma Ltd | Vírus adeno-associado (aav) com domínio fosfolipase modificado |
-
2020
- 2020-02-28 CN CN202080017400.7A patent/CN113631706A/zh active Pending
- 2020-02-28 SG SG11202108469XA patent/SG11202108469XA/en unknown
- 2020-02-28 AU AU2020229886A patent/AU2020229886B2/en active Active
- 2020-02-28 EP EP20762817.3A patent/EP3931317A4/en active Pending
- 2020-02-28 CA CA3130221A patent/CA3130221A1/en active Pending
- 2020-02-28 US US17/434,666 patent/US20220098614A1/en active Pending
- 2020-02-28 JP JP2021549908A patent/JP2022522166A/ja active Pending
- 2020-02-28 MX MX2021010412A patent/MX2021010412A/es unknown
- 2020-02-28 BR BR112021017054A patent/BR112021017054A2/pt unknown
- 2020-02-28 CN CN202511142034.9A patent/CN121160804A/zh active Pending
- 2020-02-28 WO PCT/AU2020/050182 patent/WO2020172720A1/en not_active Ceased
-
2021
- 2021-08-24 IL IL285841A patent/IL285841A/en unknown
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