JP2022519596A5 - - Google Patents
Info
- Publication number
- JP2022519596A5 JP2022519596A5 JP2021545401A JP2021545401A JP2022519596A5 JP 2022519596 A5 JP2022519596 A5 JP 2022519596A5 JP 2021545401 A JP2021545401 A JP 2021545401A JP 2021545401 A JP2021545401 A JP 2021545401A JP 2022519596 A5 JP2022519596 A5 JP 2022519596A5
- Authority
- JP
- Japan
- Prior art keywords
- nucleic acid
- sequence
- acid molecule
- cln3
- molecule according
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2025090921A JP2025138648A (ja) | 2019-02-04 | 2025-05-30 | Ｃｌｎ３ポリヌクレオチドのアデノ随伴ウイルス送達 |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962800911P | 2019-02-04 | 2019-02-04 | |
| US62/800,911 | 2019-02-04 | ||
| PCT/US2020/016542 WO2020163300A1 (en) | 2019-02-04 | 2020-02-04 | Adeno-associated virus delivery of cln3 polynucleotide |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025090921A Division JP2025138648A (ja) | 2019-02-04 | 2025-05-30 | Ｃｌｎ３ポリヌクレオチドのアデノ随伴ウイルス送達 |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2022519596A JP2022519596A (ja) | 2022-03-24 |
| JP2022519596A5 true JP2022519596A5 (https=) | 2023-02-10 |
| JP7691367B2 JP7691367B2 (ja) | 2025-06-11 |
Family
ID=69771089
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021545401A Active JP7691367B2 (ja) | 2019-02-04 | 2020-02-04 | Ｃｌｎ３ポリヌクレオチドのアデノ随伴ウイルス送達 |
| JP2025090921A Pending JP2025138648A (ja) | 2019-02-04 | 2025-05-30 | Ｃｌｎ３ポリヌクレオチドのアデノ随伴ウイルス送達 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025090921A Pending JP2025138648A (ja) | 2019-02-04 | 2025-05-30 | Ｃｌｎ３ポリヌクレオチドのアデノ随伴ウイルス送達 |
Country Status (16)
| Country | Link |
|---|---|
| US (2) | US12404523B2 (https=) |
| EP (1) | EP3921430A1 (https=) |
| JP (2) | JP7691367B2 (https=) |
| KR (1) | KR20210124300A (https=) |
| CN (1) | CN113646436A (https=) |
| AR (1) | AR118005A1 (https=) |
| AU (1) | AU2020217708B2 (https=) |
| BR (1) | BR112021015285A2 (https=) |
| CA (1) | CA3129077A1 (https=) |
| CL (1) | CL2021002049A1 (https=) |
| EA (1) | EA202192160A1 (https=) |
| IL (1) | IL285328A (https=) |
| MX (1) | MX2021009401A (https=) |
| SG (1) | SG11202107986YA (https=) |
| TW (1) | TW202045530A (https=) |
| WO (1) | WO2020163300A1 (https=) |
Families Citing this family (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| AU2013296425B2 (en) | 2012-08-01 | 2018-06-07 | Nationwide Children's Hospital | Intrathecal delivery of recombinant adeno-associated virus 9 |
| WO2022170038A1 (en) * | 2021-02-05 | 2022-08-11 | Amicus Therapeutics, Inc. | Adeno-associated virus delivery of cln3 polynucleotide |
| JP2025524569A (ja) * | 2022-07-06 | 2025-07-30 | リサーチ インスティチュート アット ネイションワイド チルドレンズ ホスピタル | Ｃｌｎ１ポリヌクレオチドのアデノ随伴ウイルス送達 |
Family Cites Families (25)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US5173414A (en) | 1990-10-30 | 1992-12-22 | Applied Immune Sciences, Inc. | Production of recombinant adeno-associated virus vectors |
| PT728214E (pt) | 1993-11-09 | 2004-11-30 | Ohio Med College | Linhas celulares estaveis capazes de expressar o gene de replicacao do virus adeno-associado |
| WO1995013365A1 (en) | 1993-11-09 | 1995-05-18 | Targeted Genetics Corporation | Generation of high titers of recombinant aav vectors |
| US5658785A (en) | 1994-06-06 | 1997-08-19 | Children's Hospital, Inc. | Adeno-associated virus materials and methods |
| US5856152A (en) | 1994-10-28 | 1999-01-05 | The Trustees Of The University Of Pennsylvania | Hybrid adenovirus-AAV vector and methods of use therefor |
| CA2207927A1 (en) | 1994-12-06 | 1996-06-13 | Targeted Genetics Corporation | Packaging cell lines for generation of high titers of recombinant aav vectors |
| FR2737730B1 (fr) | 1995-08-10 | 1997-09-05 | Pasteur Merieux Serums Vacc | Procede de purification de virus par chromatographie |
| WO1997008298A1 (en) | 1995-08-30 | 1997-03-06 | Genzyme Corporation | Chromatographic purification of adenovirus and aav |
| US6632670B1 (en) | 1995-09-08 | 2003-10-14 | Genzyme Corporation | AAV vectors for gene therapy |
| US5910434A (en) | 1995-12-15 | 1999-06-08 | Systemix, Inc. | Method for obtaining retroviral packaging cell lines producing high transducing efficiency retroviral supernatant |
| JP2001500497A (ja) | 1996-09-06 | 2001-01-16 | トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア | 組換えアデノ随伴ウイルスに指図される遺伝子治療の方法 |
| DK1009808T3 (da) | 1997-09-05 | 2013-01-21 | Genzyme Corp | Fremgangsmåder til generering af hjælper-frie præparater af rekombinante aav-vektorer med høj titer |
| US6566118B1 (en) | 1997-09-05 | 2003-05-20 | Targeted Genetics Corporation | Methods for generating high titer helper-free preparations of released recombinant AAV vectors |
| US6258595B1 (en) | 1999-03-18 | 2001-07-10 | The Trustees Of The University Of Pennsylvania | Compositions and methods for helper-free production of recombinant adeno-associated viruses |
| US7056502B2 (en) | 2000-04-28 | 2006-06-06 | The Trustees Of The University Of Pennsylvania | Recombinant aav vectors with AAV5 capsids and AAV5 vectors pseudotyped in heterologous capsids |
| US9233131B2 (en) | 2003-06-30 | 2016-01-12 | The Regents Of The University Of California | Mutant adeno-associated virus virions and methods of use thereof |
| US9441244B2 (en) | 2003-06-30 | 2016-09-13 | The Regents Of The University Of California | Mutant adeno-associated virus virions and methods of use thereof |
| US9434928B2 (en) | 2011-11-23 | 2016-09-06 | Nationwide Children's Hospital, Inc. | Recombinant adeno-associated virus delivery of alpha-sarcoglycan polynucleotides |
| DE102012007232B4 (de) | 2012-04-07 | 2014-03-13 | Susanne Weller | Verfahren zur Herstellung von rotierenden elektrischen Maschinen |
| AU2013296425B2 (en) | 2012-08-01 | 2018-06-07 | Nationwide Children's Hospital | Intrathecal delivery of recombinant adeno-associated virus 9 |
| JP2015092462A (ja) | 2013-09-30 | 2015-05-14 | Tdk株式会社 | 正極及びそれを用いたリチウムイオン二次電池 |
| WO2015141521A1 (ja) | 2014-03-21 | 2015-09-24 | 株式会社日立国際電気 | 基板処理装置、半導体装置の製造方法及び記録媒体 |
| JP6197169B2 (ja) | 2014-09-29 | 2017-09-20 | 東芝メモリ株式会社 | 半導体装置の製造方法 |
| WO2016100575A1 (en) * | 2014-12-16 | 2016-06-23 | Board Of Regents Of The University Of Nebraska | Gene therapy for juvenile batten disease |
| JP7106534B2 (ja) * | 2016-11-17 | 2022-07-26 | ネイションワイド チルドレンズ ホスピタル， インコーポレイテッド | メチル－ｃｐｇ結合タンパク質２をコードする組換えアデノ随伴ウイルスの髄腔内送達 |
-
2020
- 2020-02-04 CA CA3129077A patent/CA3129077A1/en active Pending
- 2020-02-04 BR BR112021015285-7A patent/BR112021015285A2/pt unknown
- 2020-02-04 EA EA202192160A patent/EA202192160A1/ru unknown
- 2020-02-04 KR KR1020217027483A patent/KR20210124300A/ko active Pending
- 2020-02-04 EP EP20709850.0A patent/EP3921430A1/en active Pending
- 2020-02-04 US US17/427,010 patent/US12404523B2/en active Active
- 2020-02-04 WO PCT/US2020/016542 patent/WO2020163300A1/en not_active Ceased
- 2020-02-04 MX MX2021009401A patent/MX2021009401A/es unknown
- 2020-02-04 TW TW109103419A patent/TW202045530A/zh unknown
- 2020-02-04 JP JP2021545401A patent/JP7691367B2/ja active Active
- 2020-02-04 CN CN202080014802.1A patent/CN113646436A/zh active Pending
- 2020-02-04 AU AU2020217708A patent/AU2020217708B2/en active Active
- 2020-02-04 AR ARP200100305A patent/AR118005A1/es unknown
- 2020-02-04 SG SG11202107986YA patent/SG11202107986YA/en unknown
-
2021
- 2021-08-03 IL IL285328A patent/IL285328A/en unknown
- 2021-08-03 CL CL2021002049A patent/CL2021002049A1/es unknown
-
2025
- 2025-05-30 JP JP2025090921A patent/JP2025138648A/ja active Pending
- 2025-08-04 US US19/289,974 patent/US20260062713A1/en active Pending
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