JP2022506219A - ジストロフィンエクソンスキッピングのための二重特異性アンチセンスオリゴヌクレオチド - Google Patents
ジストロフィンエクソンスキッピングのための二重特異性アンチセンスオリゴヌクレオチド Download PDFInfo
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Applications Claiming Priority (3)
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| EP18204170.7 | 2018-11-02 | ||
| EP18204170 | 2018-11-02 | ||
| PCT/EP2019/079714 WO2020089325A1 (en) | 2018-11-02 | 2019-10-30 | Bispecific antisense oligonucleotides for dystrophin exon skipping |
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| JP2022506219A true JP2022506219A (ja) | 2022-01-17 |
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| EP (1) | EP3874044A1 (es) |
| JP (1) | JP2022506219A (es) |
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| MX (1) | MX2021004822A (es) |
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| WO2022232478A1 (en) | 2021-04-30 | 2022-11-03 | Sarepta Therapeutics, Inc. | Treatment methods for muscular dystrophy |
| CN114540461A (zh) * | 2022-01-26 | 2022-05-27 | 深圳市儿童医院 | 一种plga微球-crispr免疫共沉淀法检测杜氏肌萎缩症的试剂盒 |
| WO2023178230A1 (en) | 2022-03-17 | 2023-09-21 | Sarepta Therapeutics, Inc. | Phosphorodiamidate morpholino oligomer conjugates |
| WO2023215781A1 (en) * | 2022-05-05 | 2023-11-09 | Biomarin Pharmaceutical Inc. | Method of treating duchenne muscular dystrophy |
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| EP1857548A1 (en) * | 2006-05-19 | 2007-11-21 | Academisch Ziekenhuis Leiden | Means and method for inducing exon-skipping |
| KR102113306B1 (ko) * | 2009-11-12 | 2020-05-21 | 더 유니버시티 오브 웨스턴 오스트레일리아 | 안티센스 분자 및 이를 이용한 질환 치료방법 |
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