JP2021534201A5 - - Google Patents

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Publication number
JP2021534201A5
JP2021534201A5 JP2021509893A JP2021509893A JP2021534201A5 JP 2021534201 A5 JP2021534201 A5 JP 2021534201A5 JP 2021509893 A JP2021509893 A JP 2021509893A JP 2021509893 A JP2021509893 A JP 2021509893A JP 2021534201 A5 JP2021534201 A5 JP 2021534201A5
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JP
Japan
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nucleic acid
acid sequence
administered
approximately
pharmaceutical composition
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JP2021509893A
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English (en)
Japanese (ja)
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JP2021534201A (ja
JP7403852B2 (ja
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Priority claimed from CN201810948193.1A external-priority patent/CN110846392A/zh
Priority claimed from PCT/CN2018/103937 external-priority patent/WO2020000641A1/zh
Priority claimed from CN201811221305.XA external-priority patent/CN111073899B/zh
Priority claimed from CN201811230856.2A external-priority patent/CN111068071A/zh
Application filed filed Critical
Priority claimed from PCT/CN2019/101538 external-priority patent/WO2020038352A1/en
Publication of JP2021534201A publication Critical patent/JP2021534201A/ja
Publication of JP2021534201A5 publication Critical patent/JP2021534201A5/ja
Priority to JP2023205807A priority Critical patent/JP7690713B2/ja
Publication of JP7403852B2 publication Critical patent/JP7403852B2/ja
Application granted granted Critical
Active legal-status Critical Current
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JP2021509893A 2018-08-20 2019-08-20 レーベル遺伝性視神経症を治療するための組成物及び方法 Active JP7403852B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2023205807A JP7690713B2 (ja) 2018-08-20 2023-12-06 レーベル遺伝性視神経症を治療するための組成物及び方法

Applications Claiming Priority (15)

Application Number Priority Date Filing Date Title
CN201810948193.1A CN110846392A (zh) 2018-08-20 2018-08-20 一种重组腺相关病毒或含其的试剂盒及其应用
CN201810948193.1 2018-08-20
PCT/CN2018/103937 WO2020000641A1 (zh) 2018-06-29 2018-09-04 编码人nadh脱氢酶亚单位蛋白的核酸及其应用
CNPCT/CN2018/103937 2018-09-04
CN201811221305.XA CN111073899B (zh) 2018-10-19 2018-10-19 一种编码人nadh脱氢酶亚单位4蛋白的核酸及其应用
CN201811221305.X 2018-10-19
CN201811230856.2A CN111068071A (zh) 2018-10-22 2018-10-22 基因治疗Leber遗传学视神经病变
CN201811230856.2 2018-10-22
CNPCT/CN2018/113799 2018-11-02
PCT/CN2018/113799 WO2020082417A1 (zh) 2018-10-22 2018-11-02 基因治疗Leber遗传性视神经病变
PCT/CN2018/118662 WO2020077756A1 (zh) 2018-10-19 2018-11-30 Nd4蛋白的编码序列及其应用
CNPCT/CN2018/118662 2018-11-30
CNPCT/CN2019/070461 2019-01-04
PCT/CN2019/070461 WO2020037938A1 (zh) 2018-08-20 2019-01-04 一种重组腺相关病毒或含其的试剂盒及其应用
PCT/CN2019/101538 WO2020038352A1 (en) 2018-08-20 2019-08-20 Compositions and methods for treating leber's hereditary optic neuropathy

Related Child Applications (1)

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JP2023205807A Division JP7690713B2 (ja) 2018-08-20 2023-12-06 レーベル遺伝性視神経症を治療するための組成物及び方法

Publications (3)

Publication Number Publication Date
JP2021534201A JP2021534201A (ja) 2021-12-09
JP2021534201A5 true JP2021534201A5 (enExample) 2022-08-29
JP7403852B2 JP7403852B2 (ja) 2023-12-25

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JP2021509893A Active JP7403852B2 (ja) 2018-08-20 2019-08-20 レーベル遺伝性視神経症を治療するための組成物及び方法
JP2023205807A Active JP7690713B2 (ja) 2018-08-20 2023-12-06 レーベル遺伝性視神経症を治療するための組成物及び方法

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JP2023205807A Active JP7690713B2 (ja) 2018-08-20 2023-12-06 レーベル遺伝性視神経症を治療するための組成物及び方法

Country Status (9)

Country Link
US (2) US11352645B2 (enExample)
EP (1) EP3840785A4 (enExample)
JP (2) JP7403852B2 (enExample)
KR (1) KR20210068014A (enExample)
CN (1) CN112584874A (enExample)
AU (1) AU2019323434A1 (enExample)
CA (1) CA3109432A1 (enExample)
SG (1) SG11202101032VA (enExample)
WO (1) WO2020038352A1 (enExample)

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SG11202101032VA (en) 2018-08-20 2021-02-25 Wuhan Neurophth Biotechnology Ltd Company Compositions and methods for treating leber's hereditary optic neuropathy
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CN113025633B (zh) * 2019-12-09 2024-08-27 武汉纽福斯生物科技有限公司 编码人nadh脱氢酶亚单位1蛋白的核酸及其应用
AR126727A1 (es) * 2021-08-06 2023-11-08 Wuhan Neurophth Biotechnology Ltd Company Composición y método para tratar la neuropatía óptica hereditaria de leber causada por la mutación nd4
CN116789772A (zh) * 2022-03-18 2023-09-22 北京安龙生物医药有限公司 Aav5扩容衣壳突变体及其扩容检测方法
JP2026501611A (ja) * 2022-12-29 2026-01-16 エッジーン インコーポレイテッド レーベル遺伝性視神経症のミトコンドリア塩基変異矯正システム
CN118320132A (zh) * 2024-04-26 2024-07-12 首都医科大学附属北京友谊医院 重组腺相关病毒rAAV2/Rec2作为胰腺靶向性载体的应用

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WO2020010491A1 (zh) 2018-07-09 2020-01-16 武汉纽福斯生物科技有限公司 编码人nadh脱氢酶亚单位4蛋白的核酸及其应用
WO2020000641A1 (zh) 2018-06-29 2020-01-02 武汉纽福斯生物科技有限公司 编码人nadh脱氢酶亚单位蛋白的核酸及其应用
CN113528510A (zh) 2018-06-29 2021-10-22 武汉纽福斯生物科技有限公司 治疗遗传性视神经病变的组合物和方法
CN111068071A (zh) 2018-10-22 2020-04-28 武汉纽福斯生物科技有限公司 基因治疗Leber遗传学视神经病变
CN111073899B (zh) 2018-10-19 2021-01-01 武汉纽福斯生物科技有限公司 一种编码人nadh脱氢酶亚单位4蛋白的核酸及其应用
SG11202101032VA (en) 2018-08-20 2021-02-25 Wuhan Neurophth Biotechnology Ltd Company Compositions and methods for treating leber's hereditary optic neuropathy
CN113025633B (zh) 2019-12-09 2024-08-27 武汉纽福斯生物科技有限公司 编码人nadh脱氢酶亚单位1蛋白的核酸及其应用

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