JP2021531276A5 - - Google Patents

Info

Publication number
JP2021531276A5
JP2021531276A5 JP2021502545A JP2021502545A JP2021531276A5 JP 2021531276 A5 JP2021531276 A5 JP 2021531276A5 JP 2021502545 A JP2021502545 A JP 2021502545A JP 2021502545 A JP2021502545 A JP 2021502545A JP 2021531276 A5 JP2021531276 A5 JP 2021531276A5
Authority
JP
Japan
Prior art keywords
human
idua
expression vector
immunosuppressive therapy
subject
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2021502545A
Other languages
English (en)
Japanese (ja)
Other versions
JP2021531276A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2019/042205 external-priority patent/WO2020018665A1/en
Publication of JP2021531276A publication Critical patent/JP2021531276A/ja
Publication of JP2021531276A5 publication Critical patent/JP2021531276A5/ja
Priority to JP2024040767A priority Critical patent/JP2024095680A/ja
Pending legal-status Critical Current

Links

JP2021502545A 2018-07-18 2019-07-17 完全ヒトグリコシル化ヒトα−L−イズロニダーゼ(IDUA)を用いたムコ多糖症I型の治療 Pending JP2021531276A (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2024040767A JP2024095680A (ja) 2018-07-18 2024-03-15 完全ヒトグリコシル化ヒトα-L-イズロニダーゼ(IDUA)を用いたムコ多糖症I型の治療

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201862699923P 2018-07-18 2018-07-18
US62/699,923 2018-07-18
PCT/US2019/042205 WO2020018665A1 (en) 2018-07-18 2019-07-17 Treatment of mucopolysaccharidosis i with fully-human glycosylated human alpha-l-iduronidase (idus)

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2024040767A Division JP2024095680A (ja) 2018-07-18 2024-03-15 完全ヒトグリコシル化ヒトα-L-イズロニダーゼ(IDUA)を用いたムコ多糖症I型の治療

Publications (2)

Publication Number Publication Date
JP2021531276A JP2021531276A (ja) 2021-11-18
JP2021531276A5 true JP2021531276A5 (https=) 2022-07-26

Family

ID=69164759

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2021502545A Pending JP2021531276A (ja) 2018-07-18 2019-07-17 完全ヒトグリコシル化ヒトα−L−イズロニダーゼ(IDUA)を用いたムコ多糖症I型の治療
JP2024040767A Pending JP2024095680A (ja) 2018-07-18 2024-03-15 完全ヒトグリコシル化ヒトα-L-イズロニダーゼ(IDUA)を用いたムコ多糖症I型の治療

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2024040767A Pending JP2024095680A (ja) 2018-07-18 2024-03-15 完全ヒトグリコシル化ヒトα-L-イズロニダーゼ(IDUA)を用いたムコ多糖症I型の治療

Country Status (10)

Country Link
US (1) US20210275647A1 (https=)
EP (1) EP3823590A4 (https=)
JP (2) JP2021531276A (https=)
KR (1) KR20210034037A (https=)
AU (1) AU2019306236A1 (https=)
BR (1) BR112021000830A2 (https=)
CA (1) CA3106651A1 (https=)
IL (1) IL280198B2 (https=)
SG (1) SG11202100423YA (https=)
WO (1) WO2020018665A1 (https=)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CA3068328A1 (en) 2017-07-06 2019-01-10 The Trustees Of The University Of Pennsylvania Aav9-mediated gene therapy for treating mucopolysaccharidosis type i
KR102883778B1 (ko) 2017-09-22 2025-11-12 더 트러스티스 오브 더 유니버시티 오브 펜실베니아 Ii형 점액다당류증의 치료를 위한 유전자 요법
US20190114858A1 (en) * 2017-10-16 2019-04-18 Raritan Americas, Inc. System for controlling access to an equipment rack and intelligent power distribution unit and control unit used therein

Family Cites Families (9)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
AU2001269923A1 (en) * 2000-06-19 2002-01-02 Genzyme Corporation Combination enzyme replacement, gene therapy and small molecule therapy for lysosomal storage diseases
DE60329724D1 (de) * 2002-06-07 2009-11-26 Waratah Pharmaceuticals Inc Methoden und Kompositionen um Diabetes zu behandeln
JP5385143B2 (ja) * 2006-09-21 2014-01-08 ザ スクリプス リサーチ インスティチュート 真正細菌における選択的に硫酸化された蛋白質の遺伝的にプログラムされた発現
EP3230438B1 (en) * 2014-12-12 2024-12-04 University of Copenhagen N-glycosylation
HK1256341A1 (zh) * 2015-05-15 2019-09-20 明尼苏达大学董事会 用於治疗性递送到中枢神经系统的腺相关物
CA3012195A1 (en) * 2016-02-03 2017-08-10 The Trustees Of The University Of Pennsylvania Gene therapy for treating mucopolysaccharidosis type i
EP3411484B1 (en) * 2016-02-05 2023-10-04 Emory University Injection of single-stranded or self-complementary adeno-associated virus 9 into the cerebrospinal fluid
JP2020500928A (ja) * 2016-11-15 2020-01-16 リジェネクスバイオ インコーポレイテッド Mpsiおよびmpsiiならびに他の神経障害において神経機能を改善するための方法
KR20250022877A (ko) * 2017-01-31 2025-02-17 리젠엑스바이오 인크. 완전히-인간 글리코실화된 인간 알파-l-이두로니다아제(idua)를 이용한 뮤코다당증 1형의 치료

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