JP2021512601A5 - - Google Patents
Info
- Publication number
- JP2021512601A5 JP2021512601A5 JP2020541862A JP2020541862A JP2021512601A5 JP 2021512601 A5 JP2021512601 A5 JP 2021512601A5 JP 2020541862 A JP2020541862 A JP 2020541862A JP 2020541862 A JP2020541862 A JP 2020541862A JP 2021512601 A5 JP2021512601 A5 JP 2021512601A5
- Authority
- JP
- Japan
- Prior art keywords
- aav
- seq
- sequence
- capsid protein
- pharmaceutical composition
- Prior art date
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2022073374A JP7433360B2 (ja) | 2018-02-01 | 2022-04-27 | Ｐａｈ遺伝子移入のためのアデノ随伴ウイルス組成物及びそれらの使用方法 |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201862625150P | 2018-02-01 | 2018-02-01 | |
| US62/625,150 | 2018-02-01 | ||
| PCT/US2019/016351 WO2019152841A1 (en) | 2018-02-01 | 2019-02-01 | Adeno-associated virus compositions for pah gene transfer and methods of use thereof |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022073374A Division JP7433360B2 (ja) | 2018-02-01 | 2022-04-27 | Ｐａｈ遺伝子移入のためのアデノ随伴ウイルス組成物及びそれらの使用方法 |
Publications (4)
| Publication Number | Publication Date |
|---|---|
| JP2021512601A JP2021512601A (ja) | 2021-05-20 |
| JPWO2019152841A5 JPWO2019152841A5 (https=) | 2022-02-09 |
| JP2021512601A5 true JP2021512601A5 (https=) | 2022-02-09 |
| JP7066861B2 JP7066861B2 (ja) | 2022-05-13 |
Family
ID=67478560
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2020541862A Expired - Fee Related JP7066861B2 (ja) | 2018-02-01 | 2019-02-01 | Ｐａｈ遺伝子移入のためのアデノ随伴ウイルス組成物及びそれらの使用方法 |
| JP2022073374A Active JP7433360B2 (ja) | 2018-02-01 | 2022-04-27 | Ｐａｈ遺伝子移入のためのアデノ随伴ウイルス組成物及びそれらの使用方法 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022073374A Active JP7433360B2 (ja) | 2018-02-01 | 2022-04-27 | Ｐａｈ遺伝子移入のためのアデノ随伴ウイルス組成物及びそれらの使用方法 |
Country Status (14)
| Country | Link |
|---|---|
| EP (1) | EP3746113A4 (https=) |
| JP (2) | JP7066861B2 (https=) |
| KR (2) | KR102528641B1 (https=) |
| CN (1) | CN111886021A (https=) |
| AU (1) | AU2019215150A1 (https=) |
| BR (1) | BR112020015511A2 (https=) |
| CA (1) | CA3089824A1 (https=) |
| CL (1) | CL2020001992A1 (https=) |
| CO (1) | CO2020010783A2 (https=) |
| EA (1) | EA202091844A1 (https=) |
| IL (2) | IL295830A (https=) |
| MX (1) | MX2020008085A (https=) |
| PE (1) | PE20210341A1 (https=) |
| WO (1) | WO2019152841A1 (https=) |
Families Citing this family (9)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| PE20190401A1 (es) | 2016-07-26 | 2019-03-13 | Biomarin Pharm Inc | Novedosas proteinas de la capside del virus adenoasociado |
| BR112020022722A8 (pt) | 2018-05-09 | 2022-01-18 | Biomarin Pharm Inc | Genoma e seu uso, vetor, partícula, molécula de ácido nucleico isolada, ácido nucleico, composição, tratamento, método |
| TW202005978A (zh) | 2018-05-14 | 2020-02-01 | 美商拜奧馬林製藥公司 | 新穎肝靶向腺相關病毒載體 |
| EP3980447A4 (en) * | 2019-06-10 | 2023-07-26 | Homology Medicines, Inc. | ADENO-ASSOCIATED VIRUS COMPOSITIONS FOR ARSA GENE TRANSFER AND METHODS OF USE THEREOF |
| TW202140791A (zh) * | 2020-01-13 | 2021-11-01 | 美商霍蒙拉奇醫藥公司 | 治療苯酮尿症之方法 |
| IL294713A (en) * | 2020-01-16 | 2022-09-01 | Takeda Pharmaceuticals Co | Adeno associated virus based gene therapy for phenylketonuria |
| TW202208632A (zh) | 2020-05-27 | 2022-03-01 | 美商同源醫藥公司 | 用於恢復ｐａｈ基因功能的腺相關病毒組成物及其使用方法 |
| CN116656740A (zh) * | 2023-05-30 | 2023-08-29 | 浙江大学 | 一种腺相关病毒基因治疗载体及其在制备治疗苯丙酮尿症的药物中的应用 |
| CN119876192B (zh) * | 2024-07-02 | 2025-11-07 | 浙江大学滨江研究院 | 用于治疗苯丙酮尿症的多核苷酸 |
Family Cites Families (8)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US20030198620A1 (en) | 2002-04-16 | 2003-10-23 | Keiya Ozawa | Method of treating amino acid metabolic disorders using recombinant adeno-associated virus virions |
| AU2003237159A1 (en) * | 2002-04-30 | 2003-11-17 | University Of Florida | Treatment for phenylketonuria |
| WO2010124180A1 (en) * | 2009-04-23 | 2010-10-28 | Phasebio Pharmaceuticals, Inc. | Phenylalanine hydroxylase fusion protein and methods for treating phenylketonuria |
| US9839696B2 (en) * | 2010-04-30 | 2017-12-12 | City Of Hope | Recombinant adeno-associated vectors for targeted treatment |
| DK2675902T3 (da) * | 2011-02-17 | 2019-06-03 | Univ Pennsylvania | Sammensætninger og fremgangsmåder til at ændre vævsspecificitet og forbedre aav9-medieret genoverførsel |
| EA034103B1 (ru) * | 2013-10-22 | 2019-12-27 | Транслейт Био, Инк. | СПОСОБ ЛЕЧЕНИЯ ФЕНИЛКЕТОНУРИИ С ПРИМЕНЕНИЕМ мРНК |
| BR112017005892A2 (pt) * | 2014-09-24 | 2017-12-12 | Hope City | variantes de vetor de vírus adeno-associado para edição de genoma de alta eficácia e métodos da mesma |
| KR102738752B1 (ko) * | 2016-12-30 | 2024-12-06 | 더 트러스티스 오브 더 유니버시티 오브 펜실베니아 | 페닐케톤뇨증을 치료하기 위한 유전자 치료 |
-
2019
- 2019-02-01 KR KR1020207025137A patent/KR102528641B1/ko active Active
- 2019-02-01 BR BR112020015511-0A patent/BR112020015511A2/pt not_active IP Right Cessation
- 2019-02-01 PE PE2020001141A patent/PE20210341A1/es unknown
- 2019-02-01 EP EP19748290.4A patent/EP3746113A4/en active Pending
- 2019-02-01 CN CN201980019659.2A patent/CN111886021A/zh active Pending
- 2019-02-01 AU AU2019215150A patent/AU2019215150A1/en not_active Abandoned
- 2019-02-01 IL IL295830A patent/IL295830A/en unknown
- 2019-02-01 KR KR1020237014637A patent/KR20230065367A/ko not_active Ceased
- 2019-02-01 JP JP2020541862A patent/JP7066861B2/ja not_active Expired - Fee Related
- 2019-02-01 EA EA202091844A patent/EA202091844A1/ru unknown
- 2019-02-01 WO PCT/US2019/016351 patent/WO2019152841A1/en not_active Ceased
- 2019-02-01 MX MX2020008085A patent/MX2020008085A/es unknown
- 2019-02-01 CA CA3089824A patent/CA3089824A1/en active Pending
-
2020
- 2020-07-22 IL IL276215A patent/IL276215B2/en unknown
- 2020-07-30 CL CL2020001992A patent/CL2020001992A1/es unknown
- 2020-08-28 CO CONC2020/0010783A patent/CO2020010783A2/es unknown
-
2022
- 2022-04-27 JP JP2022073374A patent/JP7433360B2/ja active Active
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