JP2019513395A5 - - Google Patents

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Publication number
JP2019513395A5
JP2019513395A5 JP2018554006A JP2018554006A JP2019513395A5 JP 2019513395 A5 JP2019513395 A5 JP 2019513395A5 JP 2018554006 A JP2018554006 A JP 2018554006A JP 2018554006 A JP2018554006 A JP 2018554006A JP 2019513395 A5 JP2019513395 A5 JP 2019513395A5
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JP
Japan
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seq
sequence
nucleic acid
effector
set forth
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JP2018554006A
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English (en)
Japanese (ja)
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JP2019513395A (ja
JP7236195B2 (ja
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Priority claimed from PCT/AU2017/050330 external-priority patent/WO2017177277A1/en
Publication of JP2019513395A publication Critical patent/JP2019513395A/ja
Publication of JP2019513395A5 publication Critical patent/JP2019513395A5/ja
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JP2018554006A 2016-04-14 2017-04-13 眼咽頭筋ジストロフィー(opmd)の処置のための試薬およびその使用 Active JP7236195B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201662322745P 2016-04-14 2016-04-14
US62/322,745 2016-04-14
PCT/AU2017/050330 WO2017177277A1 (en) 2016-04-14 2017-04-13 Reagents for treatment of oculopharyngeal muscular dystrophy (opmd) and use thereof

Publications (3)

Publication Number Publication Date
JP2019513395A JP2019513395A (ja) 2019-05-30
JP2019513395A5 true JP2019513395A5 (https=) 2020-04-23
JP7236195B2 JP7236195B2 (ja) 2023-03-09

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ID=60041243

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2018554006A Active JP7236195B2 (ja) 2016-04-14 2017-04-13 眼咽頭筋ジストロフィー(opmd)の処置のための試薬およびその使用

Country Status (14)

Country Link
US (1) US11234994B2 (https=)
EP (1) EP3443091A4 (https=)
JP (1) JP7236195B2 (https=)
KR (1) KR102353847B1 (https=)
CN (1) CN109219659B (https=)
AU (1) AU2017250017B2 (https=)
CA (1) CA3020754C (https=)
IL (1) IL262337B2 (https=)
MX (1) MX2018012545A (https=)
NZ (1) NZ747314A (https=)
RU (1) RU2755544C2 (https=)
SG (1) SG11201808981XA (https=)
WO (1) WO2017177277A1 (https=)
ZA (1) ZA201807589B (https=)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CA3020754C (en) 2016-04-14 2023-07-25 Benitec Biopharma Limited Reagents for treatment of oculopharyngeal muscular dystrophy (opmd) and use thereof
EP3555294A4 (en) * 2016-12-14 2020-08-26 Benitec Biopharma Limited REAGENTS FOR THE TREATMENT OF OCULOPHARYNGEAL MUSCLE DYSTROPHY (PDD) AND THEIR USE
CN112867511A (zh) * 2018-10-17 2021-05-28 贝尼泰克生物制药有限公司 用于治疗眼咽肌营养不良(opmd)的方法

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CA3020754C (en) 2016-04-14 2023-07-25 Benitec Biopharma Limited Reagents for treatment of oculopharyngeal muscular dystrophy (opmd) and use thereof

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