JP2018535691A5 - - Google Patents

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JP2018535691A5
JP2018535691A5 JP2018529170A JP2018529170A JP2018535691A5 JP 2018535691 A5 JP2018535691 A5 JP 2018535691A5 JP 2018529170 A JP2018529170 A JP 2018529170A JP 2018529170 A JP2018529170 A JP 2018529170A JP 2018535691 A5 JP2018535691 A5 JP 2018535691A5
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serpina1 gene
exon
serpina1
gene
editing
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JP2018529170A
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JP6932698B2 (ja
JP2018535691A (ja
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Priority claimed from PCT/IB2016/001845 external-priority patent/WO2017093804A2/en
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JP2018529170A 2015-12-01 2016-12-01 アルファ1アンチトリプシン欠乏症の治療のための材料および方法 Active JP6932698B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2021133299A JP7240456B2 (ja) 2015-12-01 2021-08-18 アルファ1アンチトリプシン欠乏症の治療のための材料および方法

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201562261661P 2015-12-01 2015-12-01
US62/261,661 2015-12-01
US201662324056P 2016-04-18 2016-04-18
US62/324,056 2016-04-18
PCT/IB2016/001845 WO2017093804A2 (en) 2015-12-01 2016-12-01 Materials and methods for treatment of alpha-1 antitrypsin deficiency

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JP2021133299A Division JP7240456B2 (ja) 2015-12-01 2021-08-18 アルファ1アンチトリプシン欠乏症の治療のための材料および方法

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JP2018535691A JP2018535691A (ja) 2018-12-06
JP2018535691A5 true JP2018535691A5 (enExample) 2020-05-14
JP6932698B2 JP6932698B2 (ja) 2021-09-08

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JP2018529170A Active JP6932698B2 (ja) 2015-12-01 2016-12-01 アルファ1アンチトリプシン欠乏症の治療のための材料および方法
JP2021133299A Active JP7240456B2 (ja) 2015-12-01 2021-08-18 アルファ1アンチトリプシン欠乏症の治療のための材料および方法

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US (2) US11851653B2 (enExample)
EP (2) EP3967758A1 (enExample)
JP (2) JP6932698B2 (enExample)
CN (1) CN109715801B (enExample)
AU (1) AU2016364667A1 (enExample)
CA (1) CA3006618A1 (enExample)
WO (1) WO2017093804A2 (enExample)

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