JP2018502112A5 - - Google Patents

Download PDF

Info

Publication number
JP2018502112A5
JP2018502112A5 JP2017534822A JP2017534822A JP2018502112A5 JP 2018502112 A5 JP2018502112 A5 JP 2018502112A5 JP 2017534822 A JP2017534822 A JP 2017534822A JP 2017534822 A JP2017534822 A JP 2017534822A JP 2018502112 A5 JP2018502112 A5 JP 2018502112A5
Authority
JP
Japan
Prior art keywords
composition
subject
therapeutic agent
aav
item
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Granted
Application number
JP2017534822A
Other languages
English (en)
Japanese (ja)
Other versions
JP6782701B2 (ja
JP2018502112A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2015/068034 external-priority patent/WO2016109649A1/en
Publication of JP2018502112A publication Critical patent/JP2018502112A/ja
Publication of JP2018502112A5 publication Critical patent/JP2018502112A5/ja
Application granted granted Critical
Publication of JP6782701B2 publication Critical patent/JP6782701B2/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

Links

JP2017534822A 2014-12-30 2015-12-30 脳疾患を処置するための方法および組成物 Active JP6782701B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201462098085P 2014-12-30 2014-12-30
US62/098,085 2014-12-30
PCT/US2015/068034 WO2016109649A1 (en) 2014-12-30 2015-12-30 Methods and compositions for treating brain diseases

Publications (3)

Publication Number Publication Date
JP2018502112A JP2018502112A (ja) 2018-01-25
JP2018502112A5 true JP2018502112A5 (OSRAM) 2019-02-07
JP6782701B2 JP6782701B2 (ja) 2020-11-11

Family

ID=56285031

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2017534822A Active JP6782701B2 (ja) 2014-12-30 2015-12-30 脳疾患を処置するための方法および組成物

Country Status (12)

Country Link
US (1) US11612641B2 (OSRAM)
EP (1) EP3240577B1 (OSRAM)
JP (1) JP6782701B2 (OSRAM)
KR (1) KR102618947B1 (OSRAM)
CN (1) CN107405414A (OSRAM)
AU (1) AU2015374043B2 (OSRAM)
BR (1) BR112017013674A2 (OSRAM)
CA (1) CA2971687C (OSRAM)
ES (1) ES2962439T3 (OSRAM)
SG (1) SG11201704829QA (OSRAM)
WO (1) WO2016109649A1 (OSRAM)
ZA (1) ZA201704327B (OSRAM)

Families Citing this family (8)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN112410338A (zh) 2014-11-14 2021-02-26 沃雅戈治疗公司 调节性多核苷酸
IL292999A (en) 2014-11-14 2022-07-01 Voyager Therapeutics Inc Compositions and methods of treating amyotrophic lateral sclerosis (als)
EP3240577B1 (en) 2014-12-30 2023-07-05 University of Iowa Research Foundation Therapeutic agent that activates mtorc1 function for use in treating huntington's disease
SG11201809699XA (en) 2016-05-18 2018-12-28 Voyager Therapeutics Inc Modulatory polynucleotides
KR20220108216A (ko) 2016-05-18 2022-08-02 보이저 테라퓨틱스, 인크. 헌팅톤 질환을 치료하기 위한 조성물 및 방법
CL2016003282A1 (es) * 2016-12-21 2017-08-18 Univ Chile Virus aav/igf2, método de tratamiento genético y su uso en enfermedades relacionadas con mal plegamiento de proteínas tal como la enfermedad de huntington
WO2018132791A1 (en) 2017-01-16 2018-07-19 The Regents Of The University Of California Treatment of neurodegenerative conditions by disruption of rhes
JP2020518259A (ja) 2017-05-05 2020-06-25 ボイジャー セラピューティクス インコーポレイテッドVoyager Therapeutics,Inc. ハンチントン病治療組成物および方法

Family Cites Families (10)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20050255086A1 (en) 2002-08-05 2005-11-17 Davidson Beverly L Nucleic acid silencing of Huntington's Disease gene
US20050009112A1 (en) 2003-03-07 2005-01-13 Fred Hutchinson Cancer Research Center, Office Of Technology Transfer Methods for identifying Rheb effectors as lead compounds for drug development for diabetes and diseases associated with abnormal cell growth
JP2008539276A (ja) 2005-04-27 2008-11-13 ユニバーシティ オブ フロリダ リサーチ ファウンデーション,インコーポレイティド ヒト疾患に関連する変異体タンパク質の分解能を改善するための材料及び方法
KR101286870B1 (ko) * 2009-11-30 2013-07-16 (주)아모레퍼시픽 황기 추출물을 포함하는 대사 촉진 조성물
PH12014500912A1 (en) * 2011-10-28 2014-06-09 Novartis Ag Novel purine derivatives and their use in the treatment of disease
WO2013067125A1 (en) * 2011-11-01 2013-05-10 Children's Medical Center Corporation Co-activation of mtor and stat3 pathways to promote neuronal survival and regeneration
CN106924741A (zh) 2011-11-08 2017-07-07 因特利凯有限责任公司 使用多种药剂的治疗方案
WO2013116691A1 (en) * 2012-02-02 2013-08-08 The Washington University Methods for improving muscle strength
KR101626526B1 (ko) 2014-10-30 2016-06-02 경북대학교 산학협력단 hRheb를 유효성분으로 포함하는 허혈성 뇌질환의 예방 또는 치료용 조성물
EP3240577B1 (en) 2014-12-30 2023-07-05 University of Iowa Research Foundation Therapeutic agent that activates mtorc1 function for use in treating huntington's disease

Similar Documents

Publication Publication Date Title
JP2020514286A5 (OSRAM)
JP2014512171A5 (OSRAM)
JP2017513504A5 (OSRAM)
JP2021530548A (ja) 遺伝子治療製剤を生産するための系および方法
JP2018520646A5 (OSRAM)
Ozlu et al. Gene transfer therapy for neurodevelopmental disorders
JP2019513779A5 (OSRAM)
JP2019504003A5 (OSRAM)
JP2015520161A5 (OSRAM)
BR112017005892A2 (pt) variantes de vetor de vírus adeno-associado para edição de genoma de alta eficácia e métodos da mesma
RU2021134920A (ru) Композиции и способы деградации неправильно упакованных белков
PH12021552887A1 (en) Modified viral particles and uses thereof
JP2018537984A5 (OSRAM)
JP2020537637A5 (OSRAM)
JP2014526904A5 (OSRAM)
EA202091194A1 (ru) Вирусные векторы, содержащие области, кодирующие rdh12, и способы лечения дистрофий сетчатки
JP2018509154A5 (OSRAM)
FI3737423T3 (fi) Koostumuksia ja menetelmiä verkkokalvon häiriöiden hoitoon
ZA201704327B (en) Methods and compositions for treating brain diseases
JP2020527167A5 (OSRAM)
FI3873511T3 (fi) Ekspressiovektori kolesteroli-24-hydrolaasille amyotroofisen lateraaliskleroosin hoitoon
JP2023542950A (ja) α-シヌクレインの凝集を阻害するための組成物及び方法
Duan et al. Deaths in gene therapy of Duchenne muscular dystrophy and other diseases: underlying mechanisms and mitigating strategies
MX2022004799A (es) Composiciones y metodos para el tratamiento de los trastornos de almacenamiento de glucogeno.
Ketterl et al. Ofatumumab for refractory opsoclonus‐myoclonus syndrome following treatment of neuroblastoma