JP2017025008A5 - - Google Patents
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- Publication number
- JP2017025008A5 JP2017025008A5 JP2015142810A JP2015142810A JP2017025008A5 JP 2017025008 A5 JP2017025008 A5 JP 2017025008A5 JP 2015142810 A JP2015142810 A JP 2015142810A JP 2015142810 A JP2015142810 A JP 2015142810A JP 2017025008 A5 JP2017025008 A5 JP 2017025008A5
- Authority
- JP
- Japan
- Prior art keywords
- composition
- subject
- retinitis pigmentosa
- aav
- aav vector
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
- 239000000203 mixture Substances 0.000 claims 18
- 239000013607 AAV vector Substances 0.000 claims 7
- 208000007014 Retinitis pigmentosa Diseases 0.000 claims 7
- 108010005939 Ciliary Neurotrophic Factor Proteins 0.000 claims 6
- 102100031614 Ciliary neurotrophic factor Human genes 0.000 claims 6
- 210000004027 cell Anatomy 0.000 claims 4
- 230000007850 degeneration Effects 0.000 claims 4
- 238000002347 injection Methods 0.000 claims 4
- 239000007924 injection Substances 0.000 claims 4
- 108010076504 Protein Sorting Signals Proteins 0.000 claims 3
- 239000002773 nucleotide Substances 0.000 claims 3
- 125000003729 nucleotide group Chemical group 0.000 claims 3
- 241000702421 Dependoparvovirus Species 0.000 claims 2
- 210000000608 photoreceptor cell Anatomy 0.000 claims 2
- 230000028327 secretion Effects 0.000 claims 2
- 239000013598 vector Substances 0.000 claims 2
- 101000993364 Homo sapiens Ciliary neurotrophic factor Proteins 0.000 claims 1
- 101000634196 Homo sapiens Neurotrophin-3 Proteins 0.000 claims 1
- 108010025020 Nerve Growth Factor Proteins 0.000 claims 1
- 230000030833 cell death Effects 0.000 claims 1
- 239000008194 pharmaceutical composition Substances 0.000 claims 1
- 108091008695 photoreceptors Proteins 0.000 claims 1
- 230000002207 retinal effect Effects 0.000 claims 1
- 230000003248 secreting effect Effects 0.000 claims 1
- 230000004382 visual function Effects 0.000 claims 1
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2015142810A JP2017025008A (ja) | 2015-07-17 | 2015-07-17 | 網膜色素変性症の治療 |
Applications Claiming Priority (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2015142810A JP2017025008A (ja) | 2015-07-17 | 2015-07-17 | 網膜色素変性症の治療 |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2019209865A Division JP2020059719A (ja) | 2019-11-20 | 2019-11-20 | 網膜色素変性症の治療 |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2017025008A JP2017025008A (ja) | 2017-02-02 |
| JP2017025008A5 true JP2017025008A5 (enExample) | 2018-08-30 |
Family
ID=57945349
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2015142810A Pending JP2017025008A (ja) | 2015-07-17 | 2015-07-17 | 網膜色素変性症の治療 |
Country Status (1)
| Country | Link |
|---|---|
| JP (1) | JP2017025008A (enExample) |
-
2015
- 2015-07-17 JP JP2015142810A patent/JP2017025008A/ja active Pending
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