JP2018509154A5 - - Google Patents
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- JP2018509154A5 JP2018509154A5 JP2017547425A JP2017547425A JP2018509154A5 JP 2018509154 A5 JP2018509154 A5 JP 2018509154A5 JP 2017547425 A JP2017547425 A JP 2017547425A JP 2017547425 A JP2017547425 A JP 2017547425A JP 2018509154 A5 JP2018509154 A5 JP 2018509154A5
- Authority
- JP
- Japan
- Prior art keywords
- vector
- nucleotide sequence
- mammal
- motomeko
- sequence encoding
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
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Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201562131661P | 2015-03-11 | 2015-03-11 | |
| US62/131,661 | 2015-03-11 | ||
| PCT/US2016/022072 WO2016145345A1 (en) | 2015-03-11 | 2016-03-11 | Rp2 and rpgr vectors for treating x-linked retinitis pigmentosa |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2020167984A Division JP2021019611A (ja) | 2015-03-11 | 2020-10-02 | Ｘ連鎖性網膜色素変性症の治療のためのｒｐ２及びｒｐｇｒベクター |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2018509154A JP2018509154A (ja) | 2018-04-05 |
| JP2018509154A5 true JP2018509154A5 (enExample) | 2019-04-18 |
| JP6935049B2 JP6935049B2 (ja) | 2021-09-15 |
Family
ID=56879752
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2017547425A Active JP6935049B2 (ja) | 2015-03-11 | 2016-03-11 | Ｘ連鎖性網膜色素変性症の治療のためのｒｐ２及びｒｐｇｒベクター |
| JP2020167984A Pending JP2021019611A (ja) | 2015-03-11 | 2020-10-02 | Ｘ連鎖性網膜色素変性症の治療のためのｒｐ２及びｒｐｇｒベクター |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2020167984A Pending JP2021019611A (ja) | 2015-03-11 | 2020-10-02 | Ｘ連鎖性網膜色素変性症の治療のためのｒｐ２及びｒｐｇｒベクター |
Country Status (6)
| Country | Link |
|---|---|
| US (2) | US10646588B2 (enExample) |
| EP (2) | EP3719134B1 (enExample) |
| JP (2) | JP6935049B2 (enExample) |
| AU (1) | AU2016228751B2 (enExample) |
| CA (1) | CA2979229A1 (enExample) |
| WO (1) | WO2016145345A1 (enExample) |
Families Citing this family (6)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US10646588B2 (en) | 2015-03-11 | 2020-05-12 | The United States Of America, As Represented By The Secretary, Department Of Health And Human Services | RP2 and RPGR vectors for treating X-linked retinitis pigmentosa |
| WO2019099696A1 (en) * | 2017-11-15 | 2019-05-23 | The Regents Of The University Of Michigan | Viral vectors comprising rdh12 coding regions and methods of treating retinal dystrophies |
| JOP20210054A1 (ar) * | 2018-09-21 | 2020-03-21 | Nightstarx Ltd | تركيبات وطرق لعلاج التهاب الشبكية الصباغي |
| US20220054655A1 (en) * | 2019-02-22 | 2022-02-24 | University Of Massachusetts | Oxr1 gene therapy |
| CA3152513A1 (en) * | 2019-08-30 | 2021-03-04 | Baylor College Of Medicine | System for regulating gene expression |
| WO2021178668A1 (en) * | 2020-03-04 | 2021-09-10 | University Of Massachusetts | Compositions and methods for modulating rpgr expression |
Family Cites Families (13)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP0950111A1 (en) | 1996-09-06 | 1999-10-20 | The Trustees Of The University Of Pennsylvania | Methods using cre-lox for production of recombinant adeno-associated viruses |
| AU2009209408B2 (en) | 2008-01-29 | 2015-06-11 | Beacon Therapeutics Limited | Recombinant virus production using mammalian cells in suspension |
| US20100081707A1 (en) * | 2008-02-21 | 2010-04-01 | Ali Robin R | Devices and methods for delivering polynucleotides into retinal cells of the macula and fovea |
| BR112013030209A2 (pt) | 2011-05-26 | 2017-06-13 | Univ Washington | métodos baseados em célula e gene para melhorar função cardíaca |
| JP6199965B2 (ja) * | 2012-07-11 | 2017-09-20 | ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア | Ｒｐｇｒｘ連鎖性網膜変性のａａｖ媒介型遺伝子治療 |
| JP6449175B2 (ja) * | 2013-02-15 | 2019-01-09 | ザ ユナイテッド ステイツ オブ アメリカ， アズ リプレゼンテッド バイ ザ セクレタリー， デパートメント オブ ヘルス アンド ヒューマン サービシーズ | 眼の遺伝子関連疾患の治療のための方法及び組成物 |
| CN105209619B (zh) * | 2013-03-11 | 2018-10-12 | 泰莱托恩基金会 | miR-204和miR-211及其用途 |
| US9534225B2 (en) * | 2014-04-15 | 2017-01-03 | Applied Genetic Technologies Corporation | Codon optimized nucleic acid encoding a retinitis pigmentosa gtpase regulator (RPGR) |
| WO2015168666A2 (en) * | 2014-05-02 | 2015-11-05 | Genzyme Corporation | Aav vectors for retinal and cns gene therapy |
| GB201412011D0 (en) * | 2014-07-04 | 2014-08-20 | Ucl Business Plc | Treatments |
| PT3191139T (pt) * | 2014-07-24 | 2020-11-05 | Massachusetts Eye & Ear Infirmary | Terapia do gene rpgr para retinite pigmentosa |
| MX2017011255A (es) * | 2015-03-03 | 2018-08-01 | Fond Telethon | Sistema de vector múltiple y sus usos. |
| US10646588B2 (en) * | 2015-03-11 | 2020-05-12 | The United States Of America, As Represented By The Secretary, Department Of Health And Human Services | RP2 and RPGR vectors for treating X-linked retinitis pigmentosa |
-
2016
- 2016-03-11 US US15/556,746 patent/US10646588B2/en active Active
- 2016-03-11 WO PCT/US2016/022072 patent/WO2016145345A1/en not_active Ceased
- 2016-03-11 JP JP2017547425A patent/JP6935049B2/ja active Active
- 2016-03-11 CA CA2979229A patent/CA2979229A1/en active Pending
- 2016-03-11 EP EP20176667.2A patent/EP3719134B1/en active Active
- 2016-03-11 AU AU2016228751A patent/AU2016228751B2/en active Active
- 2016-03-11 EP EP16762623.3A patent/EP3268481B1/en active Active
-
2020
- 2020-04-21 US US16/854,605 patent/US11617801B2/en active Active
- 2020-10-02 JP JP2020167984A patent/JP2021019611A/ja active Pending
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