JP2016521556A - Ｆｏｘｐ３発現を調節するための組成物及び方法 - Google Patents

Ｆｏｘｐ３発現を調節するための組成物及び方法 Download PDF

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JP2016521556A
JP2016521556A JP2016518041A JP2016518041A JP2016521556A JP 2016521556 A JP2016521556 A JP 2016521556A JP 2016518041 A JP2016518041 A JP 2016518041A JP 2016518041 A JP2016518041 A JP 2016518041A JP 2016521556 A JP2016521556 A JP 2016521556A
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oligonucleotide
stranded oligonucleotide
nucleotide
nucleotides
single stranded
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JP2016521556A5 (enExample
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ジェイムズ バーサム，
ジェイムズ バーサム，
マリアノ セヴェルニーニ，
マリアノ セヴェルニーニ，
ジェイムズ マクスウィゲン，
ジェイムズ マクスウィゲン，
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ラナ セラピューティクス インコーポレイテッド
ラナ セラピューティクス インコーポレイテッド
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JP2016518041A 2013-06-07 2014-06-06 Ｆｏｘｐ３発現を調節するための組成物及び方法 Pending JP2016521556A (ja)

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US201361832677P 2013-06-07 2013-06-07
US61/832,677 2013-06-07
PCT/US2014/041345 WO2014197826A1 (en) 2013-06-07 2014-06-06 Compositions and methods for modulating foxp3 expression

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JP2016521556A true JP2016521556A (ja) 2016-07-25
JP2016521556A5 JP2016521556A5 (enExample) 2017-07-20

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US (1) US20160122760A1 (enExample)
EP (1) EP3004354A4 (enExample)
JP (1) JP2016521556A (enExample)
KR (1) KR20160027968A (enExample)
AU (1) AU2014274730A1 (enExample)
CA (1) CA2914536A1 (enExample)
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Cited By (6)

* Cited by examiner, † Cited by third party
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JP2017509631A (ja) * 2014-03-13 2017-04-06 エフ・ホフマン−ラ・ロシュ・アクチェンゲゼルシャフト エストロゲン受容体突然変異体を調節する方法及び組成物
JP2022502062A (ja) * 2018-09-26 2022-01-11 オーム ライフテック インコーポレイテッド ２’ｆａｎａ修飾ｆｏｘｐ３アンチセンスオリゴヌクレオチドおよびその使用方法
JP2022507425A (ja) * 2018-11-14 2022-01-18 アイオニス・ファーマシューティカルズ・インコーポレイテッド Ｆｏｘｐ３発現のモジュレータ
JP2022518929A (ja) * 2019-01-29 2022-03-17 アイオーニス ファーマシューティカルズ， インコーポレーテッド Ａｐｐの発現を低減するための化合物及び方法
US11584932B2 (en) 2016-11-01 2023-02-21 The Research Foundation For The State University Of New York 5-halouracil-modified microRNAs and their use in the treatment of cancer
US12319913B2 (en) 2018-10-31 2025-06-03 The Research Foundation For The State University Of New York 5-halouracil-modified microRNAs and their use in the treatment of cancer

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EA201492120A1 (ru) 2012-05-16 2015-10-30 Рана Терапьютикс, Инк. Композиции и способы для модулирования экспрессии atp2a2
US10174315B2 (en) 2012-05-16 2019-01-08 The General Hospital Corporation Compositions and methods for modulating hemoglobin gene family expression
JP2015523854A (ja) 2012-05-16 2015-08-20 ラナ セラピューティクス インコーポレイテッド Ｓｍｎ遺伝子ファミリー発現を調節するための組成物及び方法
CN104540946A (zh) 2012-05-16 2015-04-22 Rana医疗有限公司 用于调节utrn表达的组合物和方法
US10837014B2 (en) 2012-05-16 2020-11-17 Translate Bio Ma, Inc. Compositions and methods for modulating SMN gene family expression
CN104583402A (zh) 2012-05-16 2015-04-29 Rana医疗有限公司 用于调节mecp2表达的组合物和方法
JP2016531570A (ja) 2013-08-16 2016-10-13 ラナ セラピューティクス インコーポレイテッド ユークロマチン領域を標的とするオリゴヌクレオチド
WO2017181026A1 (en) * 2016-04-15 2017-10-19 Translate Bio Ma, Inc. Selective modulation of foxp3 expression
WO2017184082A1 (en) * 2016-04-22 2017-10-26 Nanyang Technological University A lymphocyte permeating chimeric oligonucleotide, methods and uses thereof
WO2018031871A1 (en) * 2016-08-12 2018-02-15 Translate Bio Ma, Inc. Ex vivo modulation of foxp3 expression
US20180193270A1 (en) 2016-11-29 2018-07-12 PureTech Health LLC Exosomes for delivery of therapeutic agents
WO2019094404A1 (en) * 2017-11-07 2019-05-16 Temple University-Of The Commonwealth System Of Higher Education Compositions and methods for improved t cells
CN111378622B (zh) * 2018-12-29 2022-12-02 华东师范大学 核酸编码的car-t细胞及其制备方法和应用
US20220213478A1 (en) * 2019-04-18 2022-07-07 Proqr Therapeutics Ii B.V. Antisense oligonucleotides for the treatment of usher syndrome
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