JP2015520161A5 - - Google Patents

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Publication number
JP2015520161A5
JP2015520161A5 JP2015512644A JP2015512644A JP2015520161A5 JP 2015520161 A5 JP2015520161 A5 JP 2015520161A5 JP 2015512644 A JP2015512644 A JP 2015512644A JP 2015512644 A JP2015512644 A JP 2015512644A JP 2015520161 A5 JP2015520161 A5 JP 2015520161A5
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JP
Japan
Prior art keywords
composition
mammal
nucleic acid
aav
vector
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JP2015512644A
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English (en)
Japanese (ja)
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JP6469000B2 (ja
JP2015520161A (ja
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Priority claimed from PCT/US2013/031725 external-priority patent/WO2013172964A1/en
Publication of JP2015520161A publication Critical patent/JP2015520161A/ja
Publication of JP2015520161A5 publication Critical patent/JP2015520161A5/ja
Application granted granted Critical
Publication of JP6469000B2 publication Critical patent/JP6469000B2/ja
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JP2015512644A 2012-05-18 2013-03-14 アミロイドの沈着を処置するための方法および組成物 Active JP6469000B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201261648801P 2012-05-18 2012-05-18
US61/648,801 2012-05-18
PCT/US2013/031725 WO2013172964A1 (en) 2012-05-18 2013-03-14 Methods and compositions for treating amyloid deposits

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2018207331A Division JP2019031564A (ja) 2012-05-18 2018-11-02 アミロイドの沈着を処置するための方法および組成物

Publications (3)

Publication Number Publication Date
JP2015520161A JP2015520161A (ja) 2015-07-16
JP2015520161A5 true JP2015520161A5 (enExample) 2016-05-12
JP6469000B2 JP6469000B2 (ja) 2019-02-13

Family

ID=49584137

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2015512644A Active JP6469000B2 (ja) 2012-05-18 2013-03-14 アミロイドの沈着を処置するための方法および組成物
JP2018207331A Pending JP2019031564A (ja) 2012-05-18 2018-11-02 アミロイドの沈着を処置するための方法および組成物

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2018207331A Pending JP2019031564A (ja) 2012-05-18 2018-11-02 アミロイドの沈着を処置するための方法および組成物

Country Status (12)

Country Link
US (1) US20150183850A1 (enExample)
EP (1) EP2850195B1 (enExample)
JP (2) JP6469000B2 (enExample)
CN (2) CN112574964A (enExample)
AU (1) AU2013263346B2 (enExample)
BR (1) BR112014028666B1 (enExample)
CA (1) CA2873890C (enExample)
ES (1) ES2786078T3 (enExample)
HK (1) HK1207109A1 (enExample)
IN (1) IN2014KN02672A (enExample)
RU (1) RU2673484C2 (enExample)
WO (1) WO2013172964A1 (enExample)

Families Citing this family (16)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CA2975583A1 (en) 2014-11-14 2016-05-19 Voyager Therapeutics, Inc. Modulatory polynucleotides
WO2016196507A1 (en) 2015-05-29 2016-12-08 University Of Iowa Research Foundation Methods of delivery of transgenes for treating brain diseases
US20180161395A1 (en) * 2015-06-12 2018-06-14 Inserm (Institut National De La Sante Et De La Recherche Medicale) Methods and pharmaceutical composition for the treatment of alzheimer's disease
JP7161401B2 (ja) * 2016-04-14 2022-10-26 公益財団法人神戸医療産業都市推進機構 アミロスフェロイド(aspd)様構造体及び医薬組成物
IL262784B2 (en) 2016-05-18 2023-10-01 Voyager Therapeutics Inc modulatory polynucleotides
NZ750291A (en) * 2016-08-03 2021-07-30 Univ South Florida Reelin compositions for treatment of neurological disorders
CN110121356A (zh) * 2016-09-02 2019-08-13 星火治疗股份有限公司 治疗cns疾病的方法和载体
EP3309550A1 (en) * 2016-10-12 2018-04-18 sphingotec GmbH Method for the detection of apolipoprotein e4
JP7361037B2 (ja) 2017-10-03 2023-10-13 プリベイル セラピューティクス,インコーポレーテッド ライソゾーム病の遺伝子治療
AU2018346102B2 (en) 2017-10-03 2023-05-11 Prevail Therapeutics, Inc. Gene therapies for lysosomal disorders
JP7616995B2 (ja) * 2018-11-28 2025-01-17 プリベイル セラピューティクス,インコーポレーテッド 神経変性疾患のための遺伝子治療
MX2022004524A (es) * 2019-10-16 2022-07-21 Univ Cornell Tratamiento génico para la enfermedad de alzheimer.
KR20230020946A (ko) * 2020-03-31 2023-02-13 누오-베타 파마슈티컬 테크놀로지 (상하이) 씨오., 엘티디. 중수소화 옥소페닐아르신 화합물 및 이의 용도
CN116670291A (zh) * 2020-11-25 2023-08-29 普利维尔治疗公司 用于神经退行性疾病的基因疗法
US20250297279A1 (en) * 2021-12-15 2025-09-25 Genans Biotechnology Co., Ltd Recombinant aav vectors and use thereof
CN116063405B (zh) * 2022-09-27 2025-08-29 广州译码基因科技有限公司 可提高AAV病毒包装能力的衣壳蛋白突变体MutC及其应用

Family Cites Families (10)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US5589154A (en) * 1994-11-22 1996-12-31 Rutgers, The State University Of New Jersey Methods for the prevention or treatment of vascular hemorrhaging and Alzheimer's disease
US6436996B1 (en) * 1997-09-30 2002-08-20 Duke University Modulation of nitric oxide production
US6855314B1 (en) 2000-03-22 2005-02-15 The United States Of America As Represented By The Department Of Health And Human Services AAV5 vector for transducing brain cells and lung cells
US6468524B1 (en) 2000-03-22 2002-10-22 The United States Of America, As Represented By The Secretary Of The Department Of Health And Human Services AAV4 vector and uses thereof
GB0322645D0 (en) * 2003-09-26 2003-10-29 Melacure Therapeutics Ab Use of antisecretory factor peptides
NZ555830A (en) * 2004-12-15 2009-01-31 Univ North Carolina Chimeric vectors
DK1879623T3 (da) * 2005-05-02 2012-12-17 Genzyme Corp Genterapi til rygmarvssygdomme
WO2008033375A2 (en) * 2006-09-14 2008-03-20 Medgenics Ltd. Long lasting drug formulations
HUE027278T2 (en) * 2007-05-16 2016-11-28 Brigham & Womens Hospital Inc Treatment of synucleinopathies
CA2833912C (en) * 2010-04-23 2021-09-21 University Of Massachusetts Aav-based treatment of cholesterol-related disorders

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