JP2014523748A5 - - Google Patents

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JP2014523748A5
JP2014523748A5 JP2014522973A JP2014522973A JP2014523748A5 JP 2014523748 A5 JP2014523748 A5 JP 2014523748A5 JP 2014522973 A JP2014522973 A JP 2014522973A JP 2014522973 A JP2014522973 A JP 2014522973A JP 2014523748 A5 JP2014523748 A5 JP 2014523748A5
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JP
Japan
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composition
protein
stem cells
cell
cells
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JP2014522973A
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Japanese (ja)
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JP6072788B2 (ja
JP2014523748A (ja
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Priority claimed from PCT/US2012/048176 external-priority patent/WO2013016446A2/en
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Publication of JP2014523748A5 publication Critical patent/JP2014523748A5/ja
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JP2014522973A 2011-07-25 2012-07-25 嚢胞性線維症膜コンダクタンス制御因子（ｃｆｔｒ）遺伝子を改変するための方法および組成物 Expired - Fee Related JP6072788B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201161511434P 2011-07-25 2011-07-25
US61/511,434 2011-07-25
PCT/US2012/048176 WO2013016446A2 (en) 2011-07-25 2012-07-25 Methods and compositions for alteration of a cystic fibrosis transmembrane conductance regulator (cftr) gene

Publications (3)

Publication Number Publication Date
JP2014523748A JP2014523748A (ja) 2014-09-18
JP2014523748A5 true JP2014523748A5 (OSRAM) 2015-07-16
JP6072788B2 JP6072788B2 (ja) 2017-02-01

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ID=47601755

Family Applications (1)

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JP2014522973A Expired - Fee Related JP6072788B2 (ja) 2011-07-25 2012-07-25 嚢胞性線維症膜コンダクタンス制御因子（ｃｆｔｒ）遺伝子を改変するための方法および組成物

Country Status (6)

Country Link
US (2) US9161995B2 (OSRAM)
EP (1) EP2737063B1 (OSRAM)
JP (1) JP6072788B2 (OSRAM)
AU (1) AU2012286901B2 (OSRAM)
CA (1) CA2841541C (OSRAM)
WO (1) WO2013016446A2 (OSRAM)

Families Citing this family (13)

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JP2016522679A (ja) 2013-04-04 2016-08-04 プレジデント アンド フェローズ オブ ハーバード カレッジ ＣＲＩＳＰＲ／Ｃａｓ系を用いたゲノム編集の治療的使用
JP2016528890A (ja) 2013-07-09 2016-09-23 プレジデント アンド フェローズ オブ ハーバード カレッジ ＣＲＩＳＰＲ／Ｃａｓ系を用いるゲノム編集の治療用の使用
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