JP2014517694A5 - - Google Patents

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JP2014517694A5
JP2014517694A5 JP2014512189A JP2014512189A JP2014517694A5 JP 2014517694 A5 JP2014517694 A5 JP 2014517694A5 JP 2014512189 A JP2014512189 A JP 2014512189A JP 2014512189 A JP2014512189 A JP 2014512189A JP 2014517694 A5 JP2014517694 A5 JP 2014517694A5
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JP
Japan
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pharmaceutical composition
nucleic acid
acid sequence
vector
viral vector
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JP2014512189A
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English (en)
Japanese (ja)
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JP2014517694A (ja
JP6162104B2 (ja
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Priority claimed from PCT/US2012/039897 external-priority patent/WO2012162705A2/en
Publication of JP2014517694A publication Critical patent/JP2014517694A/ja
Publication of JP2014517694A5 publication Critical patent/JP2014517694A5/ja
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Publication of JP6162104B2 publication Critical patent/JP6162104B2/ja
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JP2014512189A 2011-05-26 2012-05-29 細胞及び遺伝子に基づく心臓機能改善方法 Active JP6162104B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201161490450P 2011-05-26 2011-05-26
US61/490,450 2011-05-26
PCT/US2012/039897 WO2012162705A2 (en) 2011-05-26 2012-05-29 Cell and gene based methods to improve cardiac function

Publications (3)

Publication Number Publication Date
JP2014517694A JP2014517694A (ja) 2014-07-24
JP2014517694A5 true JP2014517694A5 (https=) 2015-07-16
JP6162104B2 JP6162104B2 (ja) 2017-07-12

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ID=47218136

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JP2014512189A Active JP6162104B2 (ja) 2011-05-26 2012-05-29 細胞及び遺伝子に基づく心臓機能改善方法

Country Status (10)

Country Link
US (1) US9868937B2 (https=)
EP (1) EP2714709B1 (https=)
JP (1) JP6162104B2 (https=)
KR (1) KR20140035967A (https=)
CN (1) CN103946230B (https=)
AU (1) AU2012258525B2 (https=)
BR (1) BR112013030209A2 (https=)
CA (1) CA2837322C (https=)
RU (1) RU2608957C2 (https=)
WO (1) WO2012162705A2 (https=)

Families Citing this family (17)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
AU2012258525B2 (en) 2011-05-26 2017-02-23 University Of Washington Cell and gene based methods to improve cardiac function
EP2792742A1 (en) 2013-04-17 2014-10-22 Universitätsklinikum Hamburg-Eppendorf (UKE) Gene-therapy vectors for treating cardiomyopathy
WO2015153357A1 (en) * 2014-03-29 2015-10-08 Beat Biotherapeutics Corp. Compositions and methods for improving cardiac function
IL286316B2 (en) 2015-01-16 2023-03-01 Univ Washington New micro-dystrophins and related method of use
AU2016228751B2 (en) 2015-03-11 2022-01-13 The United States Of America, As Represented By The Secretary, Department Of Health And Human Services Rp2 vectors for treating x-linked retinitis pigmentosa
WO2017031238A2 (en) * 2015-08-18 2017-02-23 Boston Scientific Scimed Inc. Methods for producing cardiomyocyte cells
WO2018144770A1 (en) * 2017-02-04 2018-08-09 AnaBios Corporation System and methods for predicting drug-induced inotropic and pro-arrhythmia risk
CN108913655B (zh) * 2018-07-16 2022-07-15 浙江大学 基于多能干细胞技术建立“人源性”心肌肥大模型的方法
MY204234A (en) 2018-08-27 2024-08-16 Regeneron Pharma Use of raman spectroscopy in downstream purification
CA3111076A1 (en) 2018-08-30 2020-03-05 Tenaya Therapeutics, Inc. Cardiac cell reprogramming with myocardin and ascl1
US20200405824A1 (en) * 2019-06-26 2020-12-31 University Of Washington Use of ribonucleotide reductase alone or in combination with micro-dystrophin to treat duchenne muscular dystrophy striated muscle disease
CN110384800B (zh) * 2019-07-19 2021-06-08 广东省实验动物监测所 LncRNA XLOC_075168在制备促进血管新生的药物中的应用
MY209860A (en) 2020-02-13 2025-08-07 Tenaya Therapeutics Inc Gene therapy vectors for treating heart disease
WO2022216800A1 (en) * 2021-04-06 2022-10-13 University Of Washington Non-contractile cardiomyocytes for cardiac repair
WO2023108129A1 (en) * 2021-12-10 2023-06-15 Spacecraft Seven, Llc Troponin c (tnnc1) gene therapy using aav vector
WO2025207745A1 (en) * 2024-03-27 2025-10-02 The Board Of Trustees Of The Leland Stanford Junior University Methods of inducing dilated cardiomyopathy phenotype in cardiomyocytes and applications thereof
CN120758566B (zh) * 2025-09-10 2025-11-21 瓯江实验室 一种在心肌细胞中特异性过表达zer1的病毒载体的构建及在心衰治疗中的应用

Family Cites Families (14)

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Publication number Priority date Publication date Assignee Title
JPH02240440A (ja) 1989-03-14 1990-09-25 Shiigeru:Kk 慣性ダンパ
GB9022543D0 (en) 1990-10-17 1990-11-28 Wellcome Found Antibody production
US6151525A (en) * 1997-11-07 2000-11-21 Medtronic, Inc. Method and system for myocardial identifier repair
WO1999062940A2 (en) 1998-05-30 1999-12-09 Collateral Therapeutics, Inc. Methods of altering cardiac cell phenotype
WO2000015821A1 (en) * 1998-09-11 2000-03-23 The Regents Of The University Of California Recombinant adenovirus for tissue specific expression in heart
AU763049B2 (en) * 1998-12-28 2003-07-10 Arch Development Corporation Efficient and stable (in vivo) gene transfer to cardiomyocytes using recombinantadeno-associated virus vectors
AU2002230999A1 (en) 2000-12-21 2002-07-01 Medtronic, Inc. Electrically responsive promoter system
AU2003234520A1 (en) * 2002-05-08 2003-11-11 The Regents Of The University Of California Methods and compositions for correction of cardiac conduction disturbances
AU2003270544A1 (en) 2002-09-11 2004-04-30 University Of Florida Vigilant vector system
EP1654365A1 (en) 2003-08-11 2006-05-10 University Of South Florida Vigilant cells
SG148197A1 (en) 2003-11-21 2008-12-31 Asubio Pharma Co Ltd Method for proliferating cardiomyocytes
WO2005094485A2 (en) 2004-03-25 2005-10-13 Yun Yen Drug screening
DE102011018586A1 (de) 2011-04-26 2012-10-31 Oliver Müller Vektorsystem zur spezifischen Genexpression im Herzmuskel
AU2012258525B2 (en) 2011-05-26 2017-02-23 University Of Washington Cell and gene based methods to improve cardiac function

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