JP2010500357A5 - - Google Patents

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Publication number
JP2010500357A5
JP2010500357A5 JP2009523836A JP2009523836A JP2010500357A5 JP 2010500357 A5 JP2010500357 A5 JP 2010500357A5 JP 2009523836 A JP2009523836 A JP 2009523836A JP 2009523836 A JP2009523836 A JP 2009523836A JP 2010500357 A5 JP2010500357 A5 JP 2010500357A5
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JP
Japan
Prior art keywords
interfering rna
small interfering
strand
medical system
viral vector
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2009523836A
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English (en)
Japanese (ja)
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JP2010500357A (ja
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Publication date
Priority claimed from US11/501,147 external-priority patent/US7732591B2/en
Application filed filed Critical
Publication of JP2010500357A publication Critical patent/JP2010500357A/ja
Publication of JP2010500357A5 publication Critical patent/JP2010500357A5/ja
Pending legal-status Critical Current

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JP2009523836A 2006-08-08 2007-08-08 頭蓋内のｓｉＲＮＡの運搬を通じたハンチントンの疾患治療用の組成物、デバイス及び方法 Pending JP2010500357A (ja)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US11/501,147 US7732591B2 (en) 2003-11-25 2006-08-08 Compositions, devices and methods for treatment of huntington's disease through intracranial delivery of sirna
PCT/US2007/017659 WO2008021149A2 (en) 2006-08-08 2007-08-08 Compositions, devices and methods for treatment of huntington's disease through intracranial delivery of sirna

Publications (2)

Publication Number Publication Date
JP2010500357A JP2010500357A (ja) 2010-01-07
JP2010500357A5 true JP2010500357A5 (enExample) 2010-10-07

Family

ID=39082586

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2009523836A Pending JP2010500357A (ja) 2006-08-08 2007-08-08 頭蓋内のｓｉＲＮＡの運搬を通じたハンチントンの疾患治療用の組成物、デバイス及び方法

Country Status (6)

Country Link
US (1) US7732591B2 (enExample)
EP (1) EP2056840B1 (enExample)
JP (1) JP2010500357A (enExample)
CN (1) CN101522202B (enExample)
CA (1) CA2660153C (enExample)
WO (1) WO2008021149A2 (enExample)

Families Citing this family (12)

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US8173614B2 (en) * 2007-01-03 2012-05-08 Medtronic, Inc. Therapeuting compositions comprising an RNAi agent and a neurotrophic factor and methods of use thereof
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JOP20190104A1 (ar) 2016-11-10 2019-05-07 Ionis Pharmaceuticals Inc مركبات وطرق لتقليل التعبير عن atxn3
CN112292177A (zh) * 2018-02-14 2021-01-29 神经电子学公司 使用靶向神经刺激治疗脑疾病的系统和方法
SG11202010215TA (en) 2018-05-09 2020-11-27 Ionis Pharmaceuticals Inc Compounds and methods for reducing atxn3 expression
CN114728018B (zh) * 2019-11-01 2024-07-19 阿尔尼拉姆医药品有限公司 亨廷顿(HTT)iRNA药剂组合物及其使用方法
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