HK1202434A1 - Virus vectors for highly efficient transgene delivery - Google Patents

Virus vectors for highly efficient transgene delivery

Info

Publication number
HK1202434A1
HK1202434A1 HK15103023.8A HK15103023A HK1202434A1 HK 1202434 A1 HK1202434 A1 HK 1202434A1 HK 15103023 A HK15103023 A HK 15103023A HK 1202434 A1 HK1202434 A1 HK 1202434A1
Authority
HK
Hong Kong
Prior art keywords
highly efficient
virus vectors
transgene delivery
efficient transgene
delivery
Prior art date
Application number
HK15103023.8A
Other languages
English (en)
Chinese (zh)
Inventor
Federico Mingozzi
Xavier Anguela
J Fraser Wright
Katherine A High
Original Assignee
Philadelphia Children Hospital
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Family has litigation
First worldwide family litigation filed litigation Critical https://patents.darts-ip.com/?family=48470322&utm_source=google_patent&utm_medium=platform_link&utm_campaign=public_patent_search&patent=HK1202434(A1) "Global patent litigation dataset” by Darts-ip is licensed under a Creative Commons Attribution 4.0 International License.
Application filed by Philadelphia Children Hospital filed Critical Philadelphia Children Hospital
Publication of HK1202434A1 publication Critical patent/HK1202434A1/xx

Links

Classifications

    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12NMICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N15/00Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor
    • C12N15/09Recombinant DNA-technology
    • C12N15/63Introduction of foreign genetic material using vectors; Vectors; Use of hosts therefor; Regulation of expression
    • C12N15/79Vectors or expression systems specially adapted for eukaryotic hosts
    • C12N15/85Vectors or expression systems specially adapted for eukaryotic hosts for animal cells
    • C12N15/86Viral vectors
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P7/00Drugs for disorders of the blood or the extracellular fluid
    • A61P7/04Antihaemorrhagics; Procoagulants; Haemostatic agents; Antifibrinolytic agents
    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12NMICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N9/00Enzymes; Proenzymes; Compositions thereof; Processes for preparing, activating, inhibiting, separating or purifying enzymes
    • C12N9/14Hydrolases (3)
    • C12N9/48Hydrolases (3) acting on peptide bonds (3.4)
    • C12N9/50Proteinases, e.g. Endopeptidases (3.4.21-3.4.25)
    • C12N9/64Proteinases, e.g. Endopeptidases (3.4.21-3.4.25) derived from animal tissue
    • C12N9/6421Proteinases, e.g. Endopeptidases (3.4.21-3.4.25) derived from animal tissue from mammals
    • C12N9/6424Serine endopeptidases (3.4.21)
    • C12N9/644Coagulation factor IXa (3.4.21.22)
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K38/00Medicinal preparations containing peptides
    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12NMICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N2750/00MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA ssDNA viruses
    • C12N2750/00011Details
    • C12N2750/14011Parvoviridae
    • C12N2750/14111Dependovirus, e.g. adenoassociated viruses
    • C12N2750/14123Virus like particles [VLP]
    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12NMICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N2750/00MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA ssDNA viruses
    • C12N2750/00011Details
    • C12N2750/14011Parvoviridae
    • C12N2750/14111Dependovirus, e.g. adenoassociated viruses
    • C12N2750/14141Use of virus, viral particle or viral elements as a vector
    • C12N2750/14143Use of virus, viral particle or viral elements as a vector viral genome or elements thereof as genetic vector
HK15103023.8A 2011-11-22 2015-03-25 Virus vectors for highly efficient transgene delivery HK1202434A1 (en)

Applications Claiming Priority (4)

Application Number Priority Date Filing Date Title
US201161562795P 2011-11-22 2011-11-22
US201261639025P 2012-04-26 2012-04-26
US201261682019P 2012-08-10 2012-08-10
PCT/US2012/066380 WO2013078400A1 (fr) 2011-11-22 2012-11-21 Vecteurs viraux pour administration de transgènes hautement efficace

Publications (1)

Publication Number Publication Date
HK1202434A1 true HK1202434A1 (en) 2015-10-02

Family

ID=48470322

Family Applications (1)

Application Number Title Priority Date Filing Date
HK15103023.8A HK1202434A1 (en) 2011-11-22 2015-03-25 Virus vectors for highly efficient transgene delivery

Country Status (7)

Country Link
US (1) US10640785B2 (fr)
EP (2) EP3539568A1 (fr)
JP (1) JP6348064B2 (fr)
AU (1) AU2012340567B2 (fr)
CA (1) CA2856137A1 (fr)
HK (1) HK1202434A1 (fr)
WO (1) WO2013078400A1 (fr)

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Also Published As

Publication number Publication date
US10640785B2 (en) 2020-05-05
JP6348064B2 (ja) 2018-06-27
WO2013078400A1 (fr) 2013-05-30
US20140336245A1 (en) 2014-11-13
JP2014534245A (ja) 2014-12-18
AU2012340567B2 (en) 2017-11-23
AU2012340567A1 (en) 2014-06-05
EP2782596A4 (fr) 2015-07-29
EP2782596A1 (fr) 2014-10-01
CA2856137A1 (fr) 2013-05-30
EP3539568A1 (fr) 2019-09-18

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